Beta-Thalassemia

Showing 1 - 25 of 60

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Beta-Thalassemia Trial (CS-101 injection)

Not yet recruiting
  • Beta-Thalassemia
  • CS-101 injection
  • (no location specified)
Sep 27, 2023

Beta-Thalassemia Trial in Nanning (CS-101)

Recruiting
  • Beta-Thalassemia
  • CS-101
  • Nanning, China
    The First Affiliated Hospital of Guangxi Medical University
Sep 9, 2023

Beta-Thalassemia, Thalassemia, Genetic Diseases, Inborn Trial in Nashville (CTX001)

Recruiting
  • Beta-Thalassemia
  • +4 more
  • CTX001
  • Nashville, Tennessee
  • +5 more
Feb 2, 2023

MDS (MDS), Beta-thalassemia, Myeloproliferative Tumor(MPN)-Associated Myelofibrosis Trial in Worldwide (Luspatercept)

Recruiting
  • Myelodysplastic Syndromes (MDS)
  • +2 more
  • Los Angeles, California
  • +203 more
Jan 30, 2023

The Prevelence of HBB c.93-21 G-A in ß Thalassemia Patients

Recruiting
  • Beta-Thalassemia
  • ARMS PCR
  • Assiut, Egypt
    Faculty of Medicine Assiut University
Jan 30, 2023

Beta-thalassemia Trial in Nanning (Luspatercept, Placebo)

Recruiting
  • Beta-thalassemia
  • Nanning, China
  • +1 more
Jan 13, 2023

A Single-Site Tissue Repository Providing Annotated Biospecimens

Recruiting
  • Age-Related Macular Degeneration
  • +46 more
  • Specimen sample
  • Waltham, Massachusetts
    Sanguine Biosciences
Nov 22, 2022

Beta-Thalassemia, Thalassemia, Genetic Diseases, Inborn Trial in Worldwide (CTX001)

Active, not recruiting
  • Beta-Thalassemia
  • +4 more
  • CTX001
  • Stanford, California
  • +11 more
Nov 30, 2022

A Long-term Follow-up Study in Subjects Who Received CTX001

Enrolling by invitation
  • Beta-Thalassemia
  • +6 more
  • CTX001
  • New York, New York
  • +12 more
Nov 18, 2022

Beta-Thalassemia Trial in China (BRL-101)

Recruiting
  • Beta-Thalassemia
  • Guangzhou, Guangdong, China
  • +3 more
Nov 7, 2022

Beta-Thalassemia Trial in Bulgaria, Israel, United States (VIT-2763 60 mg QD, VIT-2763 60 mg BID, VIT-2763 120 mg BID)

Withdrawn
  • Beta-Thalassemia
  • VIT-2763 60 mg QD
  • +3 more
  • Whittier, California
  • +6 more
Nov 7, 2022

Sickle Cell Disease, Sickle Cell Trait, Beta-Thalassemia Trial (High performance liquid chromatography, Automated sickling test,

Not yet recruiting
  • Sickle Cell Disease
  • +4 more
  • High performance liquid chromatography
  • +5 more
  • (no location specified)
Aug 17, 2022

Minimisation Measures for REBLOZYL Among Healthcare

Active, not recruiting
  • Myelodysplastic Syndromes
  • Beta-thalassemia
    • City, State, Austria
      Local Institution
    Aug 4, 2022

    Beta-Thalassemia, Thalassemia, Hematologic Diseases Trial (CTX001)

    Not yet recruiting
    • Beta-Thalassemia
    • +6 more
    • CTX001
    • (no location specified)
    Jul 26, 2022

    Cognitive Function, Fatigue and Health Related Quality of Life

    Recruiting
    • Cognitive Change
    • +3 more
      • Giza, Egypt
        Abo El-Rish Pediatric Hospital
      Jul 20, 2022

      The Prevelence of IVS 1-6 [HBB:c.92 +6 T-C] Gene Mutation in

      Not yet recruiting
      • Beta-Thalassemia
      • ARMS
      • (no location specified)
      May 10, 2022

      Beta-Thalassemia Trial in Worldwide (LentiGlobin BB305 Drug Product)

      Active, not recruiting
      • Beta-Thalassemia
      • LentiGlobin BB305 Drug Product
      • Oakland, California
      • +8 more
      Feb 4, 2022

      Erythrocyte Transfusion, Beta-Thalassemia Trial in Worldwide (Luspatercept, Placebo)

      Completed
      • Erythrocyte Transfusion
      • Beta-Thalassemia
      • Los Angeles, California
      • +72 more
      Jan 21, 2022

      Beta-Thalassemia Trial in Ferrara, Firenze, Pisa (Sirolimus 0.5 mg)

      Recruiting
      • Beta-Thalassemia
      • Sirolimus 0.5 mg
      • Ferrara, FE, Italy
      • +3 more
      Nov 11, 2021

      Beta-Thalassemia Trial in Worldwide (LJPC-401)

      Terminated
      • Beta-Thalassemia
      • Oakland, California
      • +21 more
      Jul 28, 2021

      Iron Status in BTM With Blood Transfusion

      Not yet recruiting
      • Beta-Thalassemia
        • (no location specified)
        Jul 13, 2021

        Transfusional Iron Overload, Beta-Thalassemia Trial in Worldwide (SPD602)

        Terminated
        • Transfusional Iron Overload
        • Beta-Thalassemia
        • Boston, Massachusetts
        • +8 more
        Jun 10, 2021

        Beta-thalassemia, Iron Overload Trial in Los Angeles, Oakland, Chicago (Deferasirox)

        Completed
        • Beta-thalassemia
        • Iron Overload
        • Los Angeles, California
        • +2 more
        Jun 8, 2021

        Transfusional Iron Overload, Beta-thalassemia Trial in Worldwide (SPD602 (FBS0701, SSP-004184))

        Completed
        • Transfusional Iron Overload
        • Beta-thalassemia
        • SPD602 (FBS0701, SSP-004184)
        • Oakland, California
        • +8 more
        May 30, 2021

        Transfusional Iron Overload, Iron Overload, Iron Chelation Trial (SPD602, Deferasirox)

        Withdrawn
        • Transfusional Iron Overload
        • +6 more
        • (no location specified)
        Jun 1, 2021