Diamond-Blackfan Anemia

Showing 1 - 16 of 16

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Adrenoleukodystrophy Trial in Denver, Valhalla, Salt Lake City (Human

Completed
  • Mucopolysaccharidosis I
  • +15 more
  • Human Placental Derived Stem Cell
  • Denver, Colorado
  • +2 more
Oct 24, 2022

Familial Investigations of Childhood Cancer Predisposition

Recruiting
  • Acute Leukemia
  • +45 more
    • Memphis, Tennessee
      St. Jude Children's Research Hospital
    May 11, 2022

    Sickle Cell Anemia, Beta-thalassemia Major, Diamond-blackfan Anemia Trial in Pittsburgh (CD3/CD19 depleted leukocytes, CD45RA

    Recruiting
    • Sickle Cell Anemia
    • +2 more
    • CD3/CD19 depleted leukocytes
    • +6 more
    • Pittsburgh, Pennsylvania
      Children's Hospital of Pittsburgh of UPMC
    May 4, 2022

    Multi-Center Study of Iron Overload: Pilot Study

    Completed
    • Sickle Cell Disease
    • +2 more
      • Oakland, California
      • +2 more
      Sep 22, 2020

      Multi-Center Study of Iron Overload: Survey Study (MCSIO)

      Completed
      • Sickle Cell Disease
      • +2 more
        • Oakland, California
        • +7 more
        Sep 22, 2020

        Bone Marrow Failure Syndrome, Severe Aplastic Anemia, Severe Congenital Neutropenia Trial in New York (CD34 Stem Cell Selection

        Active, not recruiting
        • Bone Marrow Failure Syndrome
        • +15 more
        • CD34 Stem Cell Selection Therapy
        • New York, New York
          Morgan Stanley Children's Hospital, New York-Presbyterian, Colum
        Jun 17, 2020

        Hurler Syndrome, Fanconi Anemia, Glanzmann Thrombasthenia Trial in Atlanta (Abatacept)

        Completed
        • Hurler Syndrome
        • +14 more
        • Atlanta, Georgia
          Children's Healthcare of Atlanta
        Dec 20, 2019

        Accelerated Phase Chronic Myelogenous Leukemia, Adult Acute Lymphoblastic Leukemia in Remission, Adult Acute Myeloid Leukemia in

        Completed
        • Accelerated Phase Chronic Myelogenous Leukemia
        • +77 more
        • fludarabine phosphate
        • +8 more
        • Buffalo, New York
          Roswell Park Cancer Institute
        Sep 16, 2019

        Sickle Cell Disease, Thalassemia, Diamond-Blackfan Anemia Trial in Birmingham, Minneapolis (Bone marrow transplantation,

        Completed
        • Sickle Cell Disease
        • +2 more
        • Bone marrow transplantation
        • Mesenchymal Stromal Cells
        • Birmingham, Alabama
        • +1 more
        Jul 9, 2018

        Diamond-Blackfan Anemia, Kostmann's Neutropenia, Shwachman-Diamond Syndrome Trial in Minneapolis (procedure, drug, biological)

        Completed
        • Diamond-Blackfan Anemia
        • +2 more
        • Stem cell transplant
        • +4 more
        • Minneapolis, Minnesota
          University of Minnesota Medical Center
        Dec 3, 2017

        Chronic Myeloproliferative Disorders, Diamond-blackfan Anemia, Fanconi Anemia Trial in Minneapolis (anti-thymocyte globulin,

        Terminated
        • Chronic Myeloproliferative Disorders
        • +8 more
        • anti-thymocyte globulin
        • +9 more
        • Minneapolis, Minnesota
          University of Minnesota Cancer Center
        Nov 27, 2017

        Congenital Amegakaryocytic Thrombocytopenia, Diamond-blackfan Anemia, Leukemia Trial in San Francisco, Madison (biological,

        Completed
        • Congenital Amegakaryocytic Thrombocytopenia
        • +4 more
        • alemtuzumab
        • +9 more
        • San Francisco, California
        • +1 more
        Aug 30, 2017

        Anemia, Aplastic, Amegakaryocytic Thrombocytopenia, Diamond-Blackfan Anemia Trial in Memphis (Allogeneic stem cell transplant)

        Completed
        • Anemia, Aplastic
        • +3 more
        • Allogeneic stem cell transplant
        • Memphis, Tennessee
          St. Jude Children's Research Hospital
        Apr 24, 2017

        Stem Cell Transplantation, Bone Marrow Transplantation, Peripheral Blood Stem Cell Transplantation Trial (Cyclophosphamide Dose

        Terminated
        • Stem Cell Transplantation
        • +12 more
        • Cyclophosphamide Dose Level 1
        • +3 more
        • (no location specified)
        Jan 12, 2017

        Hemoglobinopathies, MDS, Other Inherited or Acquired Anaemia Trial in Australia (deferasirox)

        Completed
        • Hemoglobinopathies
        • +6 more
        • Adelaide, Australia
        • +3 more
        Feb 20, 2017

        Congenital Amegakaryocytic Thrombocytopenia, Diamond-blackfan Anemia, Fanconi Anemia Trial in San Francisco (biological, drug,

        Completed
        • Congenital Amegakaryocytic Thrombocytopenia
        • +5 more
        • anti-thymocyte globulin
        • +6 more
        • San Francisco, California
          UCSF Comprehensive Cancer Center
        Nov 8, 2012