Mannosidosis
Showing 1 - 3 of 3
Bone Marrow Failure Syndrome, Thalassemia, Sickle Cell Disease Trial in Gainesville (Thiotepa--single daily dose,
Recruiting
- Bone Marrow Failure Syndrome
- +15 more
- Thiotepa--single daily dose
- Thiotepa--escalated dose
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Gainesville, FloridaUF Health Shands Children's Hospital
Jul 8, 2021
Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Mannosidosis Trial in Minneapolis (Stem Cell Transplant, Busulfan,
Completed
- Mucopolysaccharidosis I
- +3 more
- Stem Cell Transplant
- Busulfan, Cyclophosphamide, ATG
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Dec 3, 2017
Pulmonary Complications in Pediatric Storage Disorders
Unknown status
- I Cell Disease
- +11 more
-
Minneapolis, MinnesotaFairview University Medical Center
Jun 23, 2005