Mannosidosis

Showing 1 - 3 of 3

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Bone Marrow Failure Syndrome, Thalassemia, Sickle Cell Disease Trial in Gainesville (Thiotepa--single daily dose,

Recruiting
  • Bone Marrow Failure Syndrome
  • +15 more
  • Thiotepa--single daily dose
  • Thiotepa--escalated dose
  • Gainesville, Florida
    UF Health Shands Children's Hospital
Jul 8, 2021

Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Mannosidosis Trial in Minneapolis (Stem Cell Transplant, Busulfan,

Completed
  • Mucopolysaccharidosis I
  • +3 more
  • Stem Cell Transplant
  • Busulfan, Cyclophosphamide, ATG
  • Minneapolis, Minnesota
    Masonic Cancer Center, University of Minnesota
Dec 3, 2017

Pulmonary Complications in Pediatric Storage Disorders

Unknown status
  • I Cell Disease
  • +11 more
    • Minneapolis, Minnesota
      Fairview University Medical Center
    Jun 23, 2005