Clincosm LogoSign in Get a demo

Methylmalonic Acidemia

Showing 1 - 13 of 13
STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS
LAST UPDATED

A Non-Interventional Post-Authorization Study of Carbaglu for

Enrolling by invitation
  • Hyperammonemia
  • +2 more
  • carglumic acid
  • Indianapolis, Indiana
    Riley Children's Hospital
Apr 24, 2023

Methylmalonic Acidemia Trial in Birmingham (mRNA-3705)

Recruiting
  • Methylmalonic Acidemia
  • Toronto, Ontario, Canada
  • +1 more
Dec 20, 2022

Methylmalonic Acidemia, Propionic Acidemia Trial in United States (HST5040, Placebo)

Recruiting
  • Methylmalonic Acidemia
  • Propionic Acidemia
  • San Diego, California
  • +10 more
Sep 6, 2022

Methylmalonic Acidemia Trial in United States (hLB-001)

Recruiting
  • Methylmalonic Acidemia
  • hLB-001
  • Atlanta, Georgia
  • +3 more
Aug 16, 2022

Patients Who Received hLB-001 Gene Therapy

Recruiting
  • Methylmalonic Acidemia
  • Nashville, Tennessee
  • +1 more
Aug 17, 2022

Carbaglu® for Treatment of MMA and PA in Adults and Pediatrics

Recruiting
  • Hyperammonemia
  • +2 more
  • Carglumic Acid
  • Washington, District of Columbia
  • +1 more
Jun 30, 2022

Methylmalonic Acidemia, Propionic Acidemia Trial in San Francisco, Remote (Registry)

Recruiting
  • Methylmalonic Acidemia
  • Propionic Acidemia
  • Registry
  • San Francisco, California
  • +2 more
Jun 27, 2022

Healthy Volunteers, Propionic Acidemia, Methylmalonic Acidemia Trial in Topeka, Pittsburgh, Austin (BBP-671, Placebo)

Recruiting
  • Healthy Volunteers
  • +3 more
  • Topeka, Indiana
  • +2 more
Apr 8, 2022

"The MaP Study": Mapping the Patient Journey in MMA and PA

Completed
  • Methylmalonic Acidemia
  • Propionic Acidemia
    • Stanford, California
    • +16 more
    Jul 29, 2021

    Organic Acidemia CARBAGLU®: A Mixed Methods Approach

    Unknown status
    • Methylmalonic Acidemia
    • Propionic Acidemia
    • Carglumic Acid
    • Bordeaux, France
    • +20 more
    Jan 8, 2020

    Propionic Acidemia, Methylmalonic Acidemia Trial in Riyadh (Carglumic Acid)

    Completed
    • Propionic Acidemia
    • Methylmalonic Acidemia
    • Carglumic Acid
    • Riyadh, Saudi Arabia
    • +1 more
    Apr 24, 2019

    Urea Cycle Disorders, Inborn, Inborn Errors of Metabolism, Propionic Acidemia Trial (N-carbamylglutamate)

    Withdrawn
    • Urea Cycle Disorders, Inborn
    • +4 more
    • (no location specified)
    May 28, 2014

    Combined Malonic and Methylmalonic Aciduria: Gene Identification

    Unknown status
    • Malonic Aciduria
    • Methylmalonic Acidemia
      • Montreal, Quebec, Canada
        McGill University Health Center
      Feb 7, 2011