Mucopolysaccharidosis II

Showing 1 - 25 of 32

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Mucopolysaccharidosis II Trial in Cincinnati (DNL310)

Enrolling by invitation
  • Mucopolysaccharidosis II
  • Cincinnati, Ohio
    Cincinnati Children's Hospital Medical Center
Oct 10, 2023

MPS (RaDiCo Cohort) (RaDiCo-MPS)

Recruiting
  • Mucopolysaccharidosis I
  • +7 more
    • Angers, France
    • +22 more
    Sep 12, 2023

    (LTFU) of Subjects Who Received SB-318, SB-913, or SB-FIX

    Active, not recruiting
    • Hemophilia B
    • +2 more
    • SB-318
    • +2 more
    • Oakland, California
    • +4 more
    Jan 30, 2023

    Mucopolysaccharidosis II Trial in Salt Lake City, Fairfax (Genetic HMI-203)

    Recruiting
    • Mucopolysaccharidosis II
    • Genetic HMI-203
    • Oakland, California
    • +5 more
    Jan 26, 2023

    Baby Detect : Genomic Newborn Screening

    Recruiting
    • Congenital Adrenal Hyperplasia
    • +126 more
      • Liege, Wallonia, Belgium
        CRMN, Hôpital La Citadelle
      Jan 24, 2023

      Mucopolysaccharidosis II Trial in Oakland, Chapel Hill (DNL310, Idursulfase)

      Recruiting
      • Mucopolysaccharidosis II
      • Oakland, California
      • +11 more
      Jan 9, 2023

      Mucopolysaccharidosis II Trial (Autologous CD34+ HSCs transduced ex vivo with CD11B LV encoding human IDS tagged with ApoEII)

      Not yet recruiting
      • Mucopolysaccharidosis II
      • Autologous CD34+ HSCs transduced ex vivo with CD11B LV encoding human IDS tagged with ApoEII
      • (no location specified)
      Dec 16, 2022

      Mucopolysaccharidosis II Trial in Worldwide (JR-141, Idursulfase, JR-141 or Idursulfase)

      Recruiting
      • Mucopolysaccharidosis II
      • Oakland, California
      • +8 more
      Dec 2, 2022

      Mucopolysaccharidosis II Trial in Japan (JR-141)

      Active, not recruiting
      • Mucopolysaccharidosis II
      • Fukui, Japan
      • +19 more
      Nov 30, 2022

      Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis IV A Trial in San Francisco (There is no intervention)

      Recruiting
      • Mucopolysaccharidosis I
      • +7 more
      • There is no intervention
      • San Francisco, California
        University of California San Francisco
      Nov 9, 2022

      Mucopolysaccharidosis II Trial in Netherlands, United States (DNL310)

      Recruiting
      • Mucopolysaccharidosis II
      • Oakland, California
      • +4 more
      Nov 14, 2022

      Mucopolysaccharidosis II Trial in Japan (JR-141)

      Completed
      • Mucopolysaccharidosis II
      • Fukui, Japan
      • +18 more
      Nov 10, 2022

      Mucopolysaccharidosis II Trial in Japan (JR-141)

      Completed
      • Mucopolysaccharidosis II
      • Gifu, Japan
      • +7 more
      Nov 10, 2022

      Mucopolysaccharidosis II Trial in Porto Alegre, São Paulo (JR-141)

      Completed
      • Mucopolysaccharidosis II
      • Porto Alegre, Brazil
      • +1 more
      Nov 10, 2022

      Mucopolysaccharidosis II Trial in Oakland (JR-141)

      Not yet recruiting
      • Mucopolysaccharidosis II
      • Oakland, California
        UCSF Benioff Children's Hospital Oakland
      Oct 21, 2022

      Adrenoleukodystrophy, Batten Disease, Mucopolysaccharidosis II Trial in Durham (DUOC-01)

      Recruiting
      • Adrenoleukodystrophy
      • +11 more
      • DUOC-01
      • Durham, North Carolina
        Duke University Medical Center
      Oct 24, 2022

      Mucopolysaccharidosis II, MPS II Trial in United States (SB-913)

      Terminated
      • Mucopolysaccharidosis II
      • MPS II
      • SB-913
      • Oakland, California
      • +4 more
      Oct 21, 2022

      Mucopolysaccharidosis Type II Observational

      Withdrawn
      • Mucopolysaccharidosis II
      • Observational
      • Oakland, California
      • +2 more
      Oct 6, 2022

      Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis VI Trial in Torrance (Adalimumab Injection [Humira],

      Recruiting
      • Mucopolysaccharidosis I
      • +2 more
      • Adalimumab Injection [Humira]
      • Saline Solution for Injection
      • Torrance, California
        The Lundquist Institute at Harbor-UCLA Medical Center
      Aug 9, 2022

      Mucopolysaccharidosis II, Hunter Syndrome Trial in Pusan, Seoul (GC1123)

      Not yet recruiting
      • Mucopolysaccharidosis II
      • Hunter Syndrome
      • GC1123
      • Pusan, Korea, Republic of
      • +2 more
      Jun 16, 2022

      MPS II Immunophenotyping

      Recruiting
      • MPS II
      • +2 more
        • Durham, North Carolina
          Duke University
        Jun 3, 2022

        ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn

        Enrolling by invitation
        • Acid Sphingomyelinase Deficiency
        • +13 more
        • Confirmatory Testing
        • Bronx, New York
        • +9 more
        May 9, 2022

        Mucopolysaccharidosis Type II Natural History

        Completed
        • Mucopolysaccharidosis II
          • Pittsburgh, Pennsylvania
          • +2 more
          Apr 22, 2022

          Long-term Follow-Up for RGX-121

          Enrolling by invitation
          • Mucopolysaccharidosis II
          • Long-term Follow-Up
          • Pittsburgh, Pennsylvania
            Children's Hospital of Pittsburgh - UPMC: Program for Neurodevel
          Aug 9, 2021

          Mucopolysaccharidosis II Trial in Worldwide (Iduronate-2-sulfatase enzyme replacement therapy, iduronate-2-sulfatase enzyme

          Completed
          • Mucopolysaccharidosis II
          • Iduronate-2-sulfatase enzyme replacement therapy
          • +2 more
          • Oakland, California
          • +8 more
          May 30, 2021