Mucopolysaccharidosis IV A

Showing 1 - 8 of 8

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Baby Detect : Genomic Newborn Screening

Recruiting
  • Congenital Adrenal Hyperplasia
  • +126 more
    • Liege, Wallonia, Belgium
      CRMN, Hôpital La Citadelle
    Jan 24, 2023

    Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis IV A Trial in San Francisco (There is no intervention)

    Recruiting
    • Mucopolysaccharidosis I
    • +7 more
    • There is no intervention
    • San Francisco, California
      University of California San Francisco
    Nov 9, 2022

    ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn

    Enrolling by invitation
    • Acid Sphingomyelinase Deficiency
    • +13 more
    • Confirmatory Testing
    • Bronx, New York
    • +9 more
    May 9, 2022

    Natural History of Atypical Morquio A Disease

    Active, not recruiting
    • Mucopolysaccharidosis IV A
    • Elosulfase Alfa 1 MG/ML Intravenous Solution [VIMIZIM]
    • Bordeaux, Aquitaine, France
      Rheumatology department - Bordeaux University Hospital
    Feb 15, 2022

    Mucopolysaccharidosis IV A, Morquio A Syndrome, MPS IVA Trial in Worldwide (BMN 110 - Weekly, BMN 110 - Every Other Week)

    Completed
    • Mucopolysaccharidosis IV A
    • +2 more
    • BMN 110 - Weekly
    • BMN 110 - Every Other Week
    • Phoenix, Arizona
    • +42 more
    Jul 19, 2021

    Mucopolysaccharidosis IV A, Mucopolysaccharidosis VI, Mucopolysaccharidoses Trial in Porto Alegre (Losartan, Placebo)

    Recruiting
    • Mucopolysaccharidosis IV A
    • +8 more
    • Porto Alegre, Rio Grande Do Sul, Brazil
      Hospital de Clinicas de Porto Alegre
    Oct 2, 2020

    Psychological Concomitants of Morquio A Syndrome - Longitudinal

    Completed
    • Morquio A Syndrome
    • Mucopolysaccharidosis IV A
      • Decatur, Georgia
        Emory University
      Apr 9, 2018

      Mucopolysaccharidosis Disorders in Patients Presenting With

      Completed
      • Mucopolysaccharidosis IV A
      • Mucopolysaccharidosis VI
      • Enzyme testing
      • Minneapolis, Minnesota
      • +1 more
      Jul 31, 2015