Mucopolysaccharidosis IV A
Showing 1 - 8 of 8
Baby Detect : Genomic Newborn Screening
Recruiting
- Congenital Adrenal Hyperplasia
- +126 more
-
Liege, Wallonia, BelgiumCRMN, Hôpital La Citadelle
Jan 24, 2023
Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis IV A Trial in San Francisco (There is no intervention)
Recruiting
- Mucopolysaccharidosis I
- +7 more
- There is no intervention
-
San Francisco, CaliforniaUniversity of California San Francisco
Nov 9, 2022
ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn
Enrolling by invitation
- Acid Sphingomyelinase Deficiency
- +13 more
- Confirmatory Testing
-
Bronx, New York
- +9 more
May 9, 2022
Natural History of Atypical Morquio A Disease
Active, not recruiting
- Mucopolysaccharidosis IV A
- Elosulfase Alfa 1 MG/ML Intravenous Solution [VIMIZIM]
-
Bordeaux, Aquitaine, FranceRheumatology department - Bordeaux University Hospital
Feb 15, 2022
Mucopolysaccharidosis IV A, Morquio A Syndrome, MPS IVA Trial in Worldwide (BMN 110 - Weekly, BMN 110 - Every Other Week)
Completed
- Mucopolysaccharidosis IV A
- +2 more
- BMN 110 - Weekly
- BMN 110 - Every Other Week
-
Phoenix, Arizona
- +42 more
Jul 19, 2021
Mucopolysaccharidosis IV A, Mucopolysaccharidosis VI, Mucopolysaccharidoses Trial in Porto Alegre (Losartan, Placebo)
Recruiting
- Mucopolysaccharidosis IV A
- +8 more
- Losartan
- Placebo
-
Porto Alegre, Rio Grande Do Sul, BrazilHospital de Clinicas de Porto Alegre
Oct 2, 2020
Psychological Concomitants of Morquio A Syndrome - Longitudinal
Completed
- Morquio A Syndrome
- Mucopolysaccharidosis IV A
-
Decatur, GeorgiaEmory University
Apr 9, 2018
Mucopolysaccharidosis Disorders in Patients Presenting With
Completed
- Mucopolysaccharidosis IV A
- Mucopolysaccharidosis VI
- Enzyme testing
-
Minneapolis, Minnesota
- +1 more
Jul 31, 2015