Mucopolysaccharidosis VI

Showing 1 - 18 of 18

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

MPS (RaDiCo Cohort) (RaDiCo-MPS)

Recruiting
  • Mucopolysaccharidosis I
  • +7 more
    • Angers, France
    • +22 more
    Sep 12, 2023

    Baby Detect : Genomic Newborn Screening

    Recruiting
    • Congenital Adrenal Hyperplasia
    • +126 more
      • Liege, Wallonia, Belgium
        CRMN, Hôpital La Citadelle
      Jan 24, 2023

      Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis IV A Trial in San Francisco (There is no intervention)

      Recruiting
      • Mucopolysaccharidosis I
      • +7 more
      • There is no intervention
      • San Francisco, California
        University of California San Francisco
      Nov 9, 2022

      Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Adrenoleukodystrophy Trial in Denver, Valhalla, Salt Lake City (Human

      Completed
      • Mucopolysaccharidosis I
      • +15 more
      • Human Placental Derived Stem Cell
      • Denver, Colorado
      • +2 more
      Oct 24, 2022

      Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis VI Trial in Torrance (Adalimumab Injection [Humira],

      Recruiting
      • Mucopolysaccharidosis I
      • +2 more
      • Adalimumab Injection [Humira]
      • Saline Solution for Injection
      • Torrance, California
        The Lundquist Institute at Harbor-UCLA Medical Center
      Aug 9, 2022

      ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn

      Enrolling by invitation
      • Acid Sphingomyelinase Deficiency
      • +13 more
      • Confirmatory Testing
      • Bronx, New York
      • +9 more
      May 9, 2022

      Mucopolysaccharidosis IV A, Mucopolysaccharidosis VI, Mucopolysaccharidoses Trial in Porto Alegre (Losartan, Placebo)

      Recruiting
      • Mucopolysaccharidosis IV A
      • +8 more
      • Porto Alegre, Rio Grande Do Sul, Brazil
        Hospital de Clinicas de Porto Alegre
      Oct 2, 2020

      Mucopolysaccharidosis VI Trial in Worldwide (Odiparcil, Placebo)

      Completed
      • Mucopolysaccharidosis VI
      • Bron, France
      • +3 more
      Oct 31, 2019

      Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis VI Trial in Minneapolis (Somatropin (DNA origin))

      Terminated
      • Mucopolysaccharidosis I
      • +2 more
      • Somatropin (DNA origin)
      • Minneapolis, Minnesota
        University of Minnesota
      Aug 6, 2018

      Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Mannosidosis Trial in Minneapolis (Stem Cell Transplant, Busulfan,

      Completed
      • Mucopolysaccharidosis I
      • +3 more
      • Stem Cell Transplant
      • Busulfan, Cyclophosphamide, ATG
      • Minneapolis, Minnesota
        Masonic Cancer Center, University of Minnesota
      Dec 3, 2017

      Mucopolysaccharidosis Disorders in Patients Presenting With

      Completed
      • Mucopolysaccharidosis IV A
      • Mucopolysaccharidosis VI
      • Enzyme testing
      • Minneapolis, Minnesota
      • +1 more
      Jul 31, 2015

      Detect Unrecognized Mucopolysaccharidosis in Children Visiting

      Terminated
      • Mucopolysaccharidoses
      • +4 more
      • Dried blood spot test for MPS
      • New Brunswick, New Jersey
      • +1 more
      May 23, 2013

      Mucopolysaccharidosis VI, Maroteaux-Lamy Syndrome Trial in France, Portugal, United States (Naglazyme)

      Completed
      • Mucopolysaccharidosis VI
      • Maroteaux-Lamy Syndrome
      • Los Angeles, California
      • +3 more
      Jul 19, 2011

      Mucopolysaccharidosis VI Trial in Novato (N-acetylgalactosamine 4-sulfatase, Placebo/rhASB)

      Completed
      • Mucopolysaccharidosis VI
      • N-acetylgalactosamine 4-sulfatase
      • Placebo/rhASB
      • Novato, California
        BioMarin Pharmaceutical Inc.
      Jan 26, 2010

      Mucopolysaccharidosis VI Trial in Novato (Placebo, N-acetylgalactosamine 4-sulfatase)

      Completed
      • Mucopolysaccharidosis VI
      • Placebo
      • N-acetylgalactosamine 4-sulfatase
      • Novato, California
        BioMarin Pharmaceutical Inc.
      Dec 18, 2009

      Mucopolysaccharidosis VI Trial in Novato (N-acetylgalactosamine 4-sulfatase)

      Completed
      • Mucopolysaccharidosis VI
      • N-acetylgalactosamine 4-sulfatase
      • Novato, California
        BioMarin Pharmaceutical Inc.
      Aug 24, 2009

      Mucopolysaccharidosis VI Trial in Novato (N-acetylgalactosamine 4-sulfatase)

      Completed
      • Mucopolysaccharidosis VI
      • N-acetylgalactosamine 4-sulfatase
      • Novato, California
        BioMarin Pharmaceutical Inc.
      Nov 2, 2006

      Pulmonary Complications in Pediatric Storage Disorders

      Unknown status
      • I Cell Disease
      • +11 more
        • Minneapolis, Minnesota
          Fairview University Medical Center
        Jun 23, 2005