Mucopolysaccharidosis VI Clinical Trials
STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS
LAST UPDATED
L
Recruiting
- Mucopolysaccharidosis I
- +2 more
- Adalimumab Injection [Humira]
- Saline Solution for Injection
- Torrance, CaliforniaThe Lundquist Institute at Harbor-UCLA Medical Center
2021-11-30
Nov 30, 2021N
Active, not recruiting
- Mucopolysaccharidosis I
- +15 more
- Human Placental Derived Stem Cell
- Denver, Colorado
- +2 more
2021-10-29
Oct 29, 2021H
Recruiting
- Mucopolysaccharidosis IV A
- +8 more
- Losartan
- Placebo
- Porto Alegre, Rio Grande Do Sul, BrazilHospital de Clinicas de Porto Alegre
2020-10-02
Oct 2, 2020I
L
Terminated
- Mucopolysaccharidosis I
- +2 more
- Somatropin (DNA origin)
- Minneapolis, MinnesotaUniversity of Minnesota
2018-08-06
Aug 6, 2018M
Completed
- Mucopolysaccharidosis I
- +3 more
- Stem Cell Transplant
- Busulfan, Cyclophosphamide, ATG
- Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
2017-12-03
Dec 3, 2017C
Completed
- Mucopolysaccharidosis IV A
- Mucopolysaccharidosis VI
- Enzyme testing
- Minneapolis, Minnesota
- +1 more
2015-07-31
Jul 31, 2015N
Terminated
- Mucopolysaccharidoses
- +4 more
- Dried blood spot test for MPS
- New Brunswick, New Jersey
- +1 more
2013-05-23
May 23, 2013B
Completed
- Mucopolysaccharidosis VI
- Maroteaux-Lamy Syndrome
- Los Angeles, California
- +3 more
2011-07-19
Jul 19, 2011B
Completed
- Mucopolysaccharidosis VI
- N-acetylgalactosamine 4-sulfatase
- Placebo/rhASB
- Novato, CaliforniaBioMarin Pharmaceutical Inc.
2010-01-26
Jan 26, 2010B
Completed
- Mucopolysaccharidosis VI
- Placebo
- N-acetylgalactosamine 4-sulfatase
- Novato, CaliforniaBioMarin Pharmaceutical Inc.
2009-12-18
Dec 18, 2009B
Completed
- Mucopolysaccharidosis VI
- N-acetylgalactosamine 4-sulfatase
- Novato, CaliforniaBioMarin Pharmaceutical Inc.
2009-08-24
Aug 24, 2009B
Completed
- Mucopolysaccharidosis VI
- N-acetylgalactosamine 4-sulfatase
- Novato, CaliforniaBioMarin Pharmaceutical Inc.
2006-11-02
Nov 2, 2006F
Unknown status
- I Cell Disease
- +11 more
- Minneapolis, MinnesotaFairview University Medical Center
2005-06-23
Jun 23, 2005