Muscular Dystrophy, Duchenne
Showing 1 - 25 of 37
Development of Non-Invasive Prenatal Diagnosis for Single Gene
Not yet recruiting
- Invasive PreNatal Diagnosis in a Context of Family History of Single-gene Disorders, Including
- +14 more
- Blood sample
-
Paris, FranceHôpital Cochin, Maternité Port-Royal, service de Gynécologie obs
Nov 24, 2023
Duchenne Muscular Dystrophy With Small Mutations
Recruiting
- Muscular Dystrophy, Duchenne
- MUSCLE MAGNETIC RESONANCE IMAGING (MRI)
-
Rome, ItalyClaudia Brogna
Apr 17, 2023
Muscular Dystrophies, Muscular Dystrophy, Duchenne, Muscular Disorders, Atrophic Trial in Little Rock, Sacramento, Atlanta
Recruiting
- Muscular Dystrophies
- +7 more
- CAP-1002
- Placebo
-
Little Rock, Arkansas
- +9 more
Jan 9, 2023
Muscular Dystrophy, Duchenne Trial in United States (SRP-9001)
Enrolling by invitation
- Muscular Dystrophy, Duchenne
- SRP-9001
-
Palo Alto, California
- +4 more
Sep 28, 2022
Muscular Dystrophy, Duchenne Trial in Worldwide
Active, not recruiting
- Muscular Dystrophy, Duchenne
-
Linz, Austria
- +70 more
Aug 16, 2022
Muscular Dystrophy, Duchenne Trial in Westmead, Parkville (PF-06939926)
Recruiting
- Muscular Dystrophy, Duchenne
- PF-06939926
-
Westmead, New South Wales, Australia
- +1 more
Aug 15, 2022
Muscular Dystrophy, Duchenne, Muscular Dystrophies, Muscular Disorders, Atrophic Trial in Worldwide (Ataluren, PLACEBO)
Active, not recruiting
- Muscular Dystrophy, Duchenne
- +8 more
- Ataluren
- PLACEBO
-
Phoenix, Arizona
- +71 more
Mar 30, 2022
Physical Activity Level and Participation in Duchenne Muscular
Recruiting
- Muscular Dystrophy, Duchenne
-
Ankara, Sıhhiye, TurkeyHacettepe University
Mar 14, 2022
Muscular Dystrophy, Duchenne Trial in United States (Spironolactone, Prednisolone)
Terminated
- Muscular Dystrophy, Duchenne
-
Iowa City, Iowa
- +3 more
Jan 19, 2022
Regular Physical Exercise in Duchenne Muscular Dystrophy
Active, not recruiting
- Muscular Dystrophy, Duchenne
- Physical Exercise
-
Bergen, NorwayDepartment of Physiotherapy. Haukeland University Hospital
Dec 28, 2021
Muscular Dystrophy, Duchenne Trial in Gdansk (Metoprolol Succinate, Placebo)
Recruiting
- Muscular Dystrophy, Duchenne
- Metoprolol Succinate
- Placebo
-
Gdańsk, Pomorskie, PolandUniversity Clinical Centre in Gdańsk, Clinic of Paediatric Cardi
Sep 23, 2021
Double Push Acoustic Radiation Force Ultrasound for Monitoring
Completed
- Muscular Dystrophy, Duchenne
-
Chapel Hill, North CarolinaThe University of North Carolina at Chapel Hill Hospitals
Jul 29, 2021
Muscular Dystrophy, Duchenne Trial in Gyeonggi-do (BLS-M22, Placebo)
Completed
- Muscular Dystrophy, Duchenne
- BLS-M22
- Placebo
-
Gyeonggi-do, Yongin-si, Korea, Republic ofBioLeaders Co., Ltd.
Apr 21, 2021
Muscular Dystrophy, Duchenne Trial in Worldwide (MNK-1411, Placebo)
Muscular Dystrophy, Duchenne, Upper Extremity, Respiratory Functions Trial in Antalya (Trunk-oriented exercise program,
Completed
- Muscular Dystrophy, Duchenne
- +2 more
- Trunk-oriented exercise program
- Conventional exercise program
-
Antalya, TurkeyGokce Yagmur Gunes Gencer
Dec 15, 2020
Muscular Dystrophy, Duchenne, DMD Trial (viltolarsen)
Approved for marketing
- Muscular Dystrophy, Duchenne
- DMD
- (no location specified)
Aug 14, 2020
Muscular Dystrophy, Duchenne, Muscular Dystrophies, Muscular Disorders, Atrophic Trial in Worldwide (Ataluren)
Terminated
- Muscular Dystrophy, Duchenne
- +8 more
-
Los Angeles, California
- +57 more
Aug 10, 2020
Muscular Dystrophy, Duchenne, Muscular Dystrophies, Muscular Disorders, Atrophic Trial in Worldwide (Ataluren, Placebo)
Completed
- Muscular Dystrophy, Duchenne
- +8 more
- Ataluren
- Placebo
-
Los Angeles, California
- +54 more
Jul 17, 2020
Muscular Dystrophies, Muscular Dystrophy, Duchenne, Muscular Disorders, Atrophic Trial in United States (CAP-1002, Placebo)
Completed
- Muscular Dystrophies
- +7 more
- CAP-1002
- Placebo
-
Sacramento, California
- +6 more
Jun 3, 2020
Muscular Dystrophy, Duchenne Trial in United States (Eteplirsen)
Completed
- Muscular Dystrophy, Duchenne
-
Los Angeles, California
- +8 more
Mar 26, 2020
Muscular Dystrophies, Muscular Dystrophy, Duchenne, Muscular Dystrophy, Becker Trial in Bosisio Parini, Costa Masnaga (Assistive
Completed
- Muscular Dystrophies
- +3 more
- Assistive device (Armon Ayura) test
- Assistive device (Jaeco Wrex) test
-
Bosisio Parini, LC, Italy
- +1 more
Dec 9, 2019
Duchenne Muscular Dystrophy, Muscular Dystrophies, Muscular Dystrophy, Duchenne Trial in Erlangen (Multispectral Optoacoustic
Completed
- Duchenne Muscular Dystrophy
- +2 more
- Multispectral Optoacoustic Tomography
-
Erlangen, Bavaria, GermanyDepartment of Pediatrics and Adolescent Medicine, University Hos
Dec 5, 2019
Muscular Dystrophy, Duchenne Trial in Worldwide (Tadalafil, Placebo)
Terminated
- Muscular Dystrophy, Duchenne
- Tadalafil
- Placebo
-
Los Angeles, California
- +61 more
Sep 25, 2019
Muscular Dystrophy, Duchenne Trial in Worldwide (Rimeporide)
Completed
- Muscular Dystrophy, Duchenne
-
Paris, Ile De France, France
- +3 more
May 6, 2019