Muscular Dystrophy, Duchenne

Showing 1 - 25 of 37

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Development of Non-Invasive Prenatal Diagnosis for Single Gene

Not yet recruiting
  • Invasive PreNatal Diagnosis in a Context of Family History of Single-gene Disorders, Including
  • +14 more
  • Blood sample
  • Paris, France
    Hôpital Cochin, Maternité Port-Royal, service de Gynécologie obs
Nov 24, 2023

Duchenne Muscular Dystrophy With Small Mutations

Recruiting
  • Muscular Dystrophy, Duchenne
  • MUSCLE MAGNETIC RESONANCE IMAGING (MRI)
  • Rome, Italy
    Claudia Brogna
Apr 17, 2023

Muscular Dystrophies, Muscular Dystrophy, Duchenne, Muscular Disorders, Atrophic Trial in Little Rock, Sacramento, Atlanta

Recruiting
  • Muscular Dystrophies
  • +7 more
  • CAP-1002
  • Placebo
  • Little Rock, Arkansas
  • +9 more
Jan 9, 2023

Muscular Dystrophy, Duchenne Trial in United States (SRP-9001)

Enrolling by invitation
  • Muscular Dystrophy, Duchenne
  • SRP-9001
  • Palo Alto, California
  • +4 more
Sep 28, 2022

Muscular Dystrophy, Duchenne Trial in Worldwide

Active, not recruiting
  • Muscular Dystrophy, Duchenne
    • Linz, Austria
    • +70 more
    Aug 16, 2022

    Muscular Dystrophy, Duchenne Trial in Westmead, Parkville (PF-06939926)

    Recruiting
    • Muscular Dystrophy, Duchenne
    • PF-06939926
    • Westmead, New South Wales, Australia
    • +1 more
    Aug 15, 2022

    Muscular Dystrophy, Duchenne, Muscular Dystrophies, Muscular Disorders, Atrophic Trial in Worldwide (Ataluren, PLACEBO)

    Active, not recruiting
    • Muscular Dystrophy, Duchenne
    • +8 more
    • Phoenix, Arizona
    • +71 more
    Mar 30, 2022

    Physical Activity Level and Participation in Duchenne Muscular

    Recruiting
    • Muscular Dystrophy, Duchenne
      • Ankara, Sıhhiye, Turkey
        Hacettepe University
      Mar 14, 2022

      Muscular Dystrophy, Duchenne Trial in United States (Spironolactone, Prednisolone)

      Terminated
      • Muscular Dystrophy, Duchenne
      • Iowa City, Iowa
      • +3 more
      Jan 19, 2022

      Regular Physical Exercise in Duchenne Muscular Dystrophy

      Active, not recruiting
      • Muscular Dystrophy, Duchenne
      • Physical Exercise
      • Bergen, Norway
        Department of Physiotherapy. Haukeland University Hospital
      Dec 28, 2021

      Muscular Dystrophy, Duchenne Trial in Canada, United States (SRP-5051)

      Terminated
      • Muscular Dystrophy, Duchenne
      • Hartford, Connecticut
      • +7 more
      Nov 19, 2021

      Muscular Dystrophy, Duchenne Trial in Gdansk (Metoprolol Succinate, Placebo)

      Recruiting
      • Muscular Dystrophy, Duchenne
      • Metoprolol Succinate
      • Placebo
      • Gdańsk, Pomorskie, Poland
        University Clinical Centre in Gdańsk, Clinic of Paediatric Cardi
      Sep 23, 2021

      Double Push Acoustic Radiation Force Ultrasound for Monitoring

      Completed
      • Muscular Dystrophy, Duchenne
        • Chapel Hill, North Carolina
          The University of North Carolina at Chapel Hill Hospitals
        Jul 29, 2021

        Muscular Dystrophy, Duchenne Trial in Gyeonggi-do (BLS-M22, Placebo)

        Completed
        • Muscular Dystrophy, Duchenne
        • BLS-M22
        • Placebo
        • Gyeonggi-do, Yongin-si, Korea, Republic of
          BioLeaders Co., Ltd.
        Apr 21, 2021

        Muscular Dystrophy, Duchenne Trial in Worldwide (MNK-1411, Placebo)

        Terminated
        • Muscular Dystrophy, Duchenne
        • Gulf Breeze, Florida
        • +15 more
        Feb 19, 2021

        Muscular Dystrophy, Duchenne, Upper Extremity, Respiratory Functions Trial in Antalya (Trunk-oriented exercise program,

        Completed
        • Muscular Dystrophy, Duchenne
        • +2 more
        • Trunk-oriented exercise program
        • Conventional exercise program
        • Antalya, Turkey
          Gokce Yagmur Gunes Gencer
        Dec 15, 2020

        Muscular Dystrophy, Duchenne, DMD Trial (viltolarsen)

        Approved for marketing
        • Muscular Dystrophy, Duchenne
        • DMD
        • (no location specified)
        Aug 14, 2020

        Muscular Dystrophy, Duchenne, Muscular Dystrophies, Muscular Disorders, Atrophic Trial in Worldwide (Ataluren)

        Terminated
        • Muscular Dystrophy, Duchenne
        • +8 more
        • Los Angeles, California
        • +57 more
        Aug 10, 2020

        Muscular Dystrophy, Duchenne, Muscular Dystrophies, Muscular Disorders, Atrophic Trial in Worldwide (Ataluren, Placebo)

        Completed
        • Muscular Dystrophy, Duchenne
        • +8 more
        • Los Angeles, California
        • +54 more
        Jul 17, 2020

        Muscular Dystrophies, Muscular Dystrophy, Duchenne, Muscular Disorders, Atrophic Trial in United States (CAP-1002, Placebo)

        Completed
        • Muscular Dystrophies
        • +7 more
        • CAP-1002
        • Placebo
        • Sacramento, California
        • +6 more
        Jun 3, 2020

        Muscular Dystrophy, Duchenne Trial in United States (Eteplirsen)

        Completed
        • Muscular Dystrophy, Duchenne
        • Los Angeles, California
        • +8 more
        Mar 26, 2020

        Muscular Dystrophies, Muscular Dystrophy, Duchenne, Muscular Dystrophy, Becker Trial in Bosisio Parini, Costa Masnaga (Assistive

        Completed
        • Muscular Dystrophies
        • +3 more
        • Assistive device (Armon Ayura) test
        • Assistive device (Jaeco Wrex) test
        • Bosisio Parini, LC, Italy
        • +1 more
        Dec 9, 2019

        Duchenne Muscular Dystrophy, Muscular Dystrophies, Muscular Dystrophy, Duchenne Trial in Erlangen (Multispectral Optoacoustic

        Completed
        • Duchenne Muscular Dystrophy
        • +2 more
        • Multispectral Optoacoustic Tomography
        • Erlangen, Bavaria, Germany
          Department of Pediatrics and Adolescent Medicine, University Hos
        Dec 5, 2019

        Muscular Dystrophy, Duchenne Trial in Worldwide (Tadalafil, Placebo)

        Terminated
        • Muscular Dystrophy, Duchenne
        • Los Angeles, California
        • +61 more
        Sep 25, 2019

        Muscular Dystrophy, Duchenne Trial in Worldwide (Rimeporide)

        Completed
        • Muscular Dystrophy, Duchenne
        • Paris, Ile De France, France
        • +3 more
        May 6, 2019