Sickle Cell Disease
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Drive Decision-AIDS for Gene Therapy for Rare Diseases (GENETX)
Not yet recruiting
- Sickle Cell Disease
- Interview
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Memphis, TennesseeSt. Jude Children's Research Hospital
Mar 30, 2023
Sickle Cell Disease, Hydroxyurea Failure, Hydroxyurea Intolerance Trial in Nashville (CTX001)
Recruiting
- Sickle Cell Disease
- +4 more
- CTX001
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Philadelphia, Pennsylvania
- +3 more
Jan 24, 2023
Sickle Cell Disease Trial in Memphis ([13N]NH3, Lexiscan, Positron emission tomography)
Not yet recruiting
- Sickle Cell Disease
- [13N]NH3
- +2 more
-
Memphis, TennesseeSt. Jude Children's Research Hospital
Jan 11, 2023
Sickle Cell Disease Trial in Memphis (Plerixafor)
Recruiting
- Sickle Cell Disease
-
Memphis, TennesseeSt. Jude Children's Research Hospital
Jan 11, 2023
Sickle Cell Disease Trial in Italy, United States (OTQ923, HIX763, OTQ923 or HIX763)
Recruiting
- Sickle Cell Disease
- OTQ923
-
Los Angeles, California
- +4 more
Jan 9, 2023
Sickle Cell Disease Trial in United States (Oxbryta® (voxelotor) 500mg Tablets)
Recruiting
- Sickle Cell Disease
- Oxbryta® (voxelotor) 500mg Tablets
-
Palo Alto, California
- +9 more
Dec 15, 2022
Sickle Cell Disease, Vaso-occlusive Crisis Trial in Memphis (Virtual Reality Therapy)
Recruiting
- Sickle Cell Disease
- Vaso-occlusive Crisis
- Virtual Reality Therapy
-
Memphis, Tennessee
- +1 more
Nov 17, 2022
A Long-term Follow-up Study in Subjects Who Received CTX001
Enrolling by invitation
- Beta-Thalassemia
- +6 more
- CTX001
-
New York, New York
- +12 more
Nov 18, 2022
Sickle Cell Disease Trial in United States
Recruiting
- Sickle Cell Disease
-
Peoria, Illinois
- +5 more
Nov 15, 2022
Sickle Cell Disease, Genetic Disease, Hematologic Diseases Trial in United States (Electronic Health Record (EHR) Embedded
Completed
- Sickle Cell Disease
- +3 more
- Electronic Health Record (EHR) Embedded Individualized Pain Plan (IPP)
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Oakland, California
- +7 more
Oct 26, 2022
Sickle Cell Disease Trial in Worldwide (Etavopivat Tablets, Placebo Tablets)
Recruiting
- Sickle Cell Disease
- Etavopivat Tablets Low dose
- +3 more
-
Birmingham, Alabama
- +77 more
Oct 11, 2022
Sickle Cell Disease Trial in United States (InCharge Health mobile application, HU Toolbox mobile application)
Completed
- Sickle Cell Disease
- InCharge Health mobile application
- HU Toolbox mobile application
-
Augusta, Georgia
- +6 more
Sep 26, 2022
Exploring Adherence Monitoring in Sickle Cell Disease
Active, not recruiting
- Sickle Cell Disease
-
Memphis, TennesseeSt. Jude Children's Research Hospital
Aug 19, 2022
The Predictive Capacity of Machine Learning Models for
Recruiting
- Sickle Cell Disease
- Kidney Diseases, Chronic
- Biospecimen/DNA collection and analysis
-
Chicago, Illinois
- +2 more
Jul 14, 2022
Predictors and Outcomes in Patients With Sickle Cell Disease
Recruiting
- Sickle Cell Disease
-
Memphis, Tennessee
- +1 more
Jul 8, 2022
Sickle Cell Disease Trial in Memphis (hydroxyurea, azathioprine, alemtuzumab, thioptepa, low dose total body irradiation and
Recruiting
- Sickle Cell Disease
- hydroxyurea, azathioprine, alemtuzumab, thioptepa, low dose total body irradiation and sirolimus
- hydroxyurea, azathioprine, alemtuzumab, thiotepa, plerixafor, low dose total body irradiation, cyclophosphamide and sirolimus
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Memphis, TennesseeSt. Jude Children's Research Hospital
May 5, 2022
Sickle Cell Disease and Genomic and Gene Therapy Needs of
Recruiting
- Sickle Cell Disease
-
Memphis, TennesseeSt. Jude Children's Research Hospital
Apr 4, 2022
Sickle Cell Disease, Thalassemia Trial in Memphis (Hydroxyurea, Hydroxyurea Oral Capsule)
Terminated
- Sickle Cell Disease
- Thalassemia
- Hydroxyurea
- Hydroxyurea Oral Capsule
-
Memphis, TennesseeSt. Jude Children's Research Hospital
Feb 18, 2022
Sickle Cell Disease Trial in United States (procedure, drug, radiation)
Recruiting
- Sickle Cell Disease
- Haploidentical Bone Marrow Transplantation
- +7 more
-
Birmingham, Alabama
- +31 more
Dec 30, 2021