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ataluren

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STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Nonsene Mutation Duchenne Muscular Dystrophy Trial in Atlanta (Ataluren)

Recruiting
  • Nonsene Mutation Duchenne Muscular Dystrophy
  • Ataluren
  • Atlanta, Georgia
    Rare Disease Research, LLC
Jan 27, 2023

Duchenne Muscular Dystrophy Trial in Los Angeles (Ataluren)

Completed
  • Duchenne Muscular Dystrophy
  • Ataluren
  • Los Angeles, California
    University of California, Los Angeles (UCLA)
Mar 9, 2022

Epilepsy Trial in New York (ataluren, Placebo)

Completed
  • Epilepsy
  • ataluren
  • Placebo
  • New York, New York
    New York University School of Medicine
Sep 7, 2021

Duchenne Muscular Dystrophy Trial in Canada, United States (Ataluren)

Enrolling by invitation
  • Duchenne Muscular Dystrophy
  • Ataluren
  • Phoenix, Arizona
  • +32 more
Jan 31, 2023

Duchenne Muscular Dystrophy Trial in United States (Ataluren)

Completed
  • Duchenne Muscular Dystrophy
  • Ataluren
  • Phoenix, Arizona
  • +8 more
Mar 10, 2022

Duchenne Muscular Dystrophy Trial in Cincinnati, Philadelphia, Salt Lake City (Ataluren)

Terminated
  • Duchenne Muscular Dystrophy
  • Ataluren
  • Cincinnati, Ohio
  • +2 more
Oct 2, 2020

Duchenne Muscular Dystrophy Trial in United States (Ataluren)

Completed
  • Duchenne Muscular Dystrophy
  • Ataluren
  • Gulf Breeze, Florida
  • +5 more
Aug 12, 2020

Duchenne Muscular Dystrophy, Becker Muscular Dystrophy, Dystrophinopathy Trial in Worldwide (Ataluren)

Completed
  • Duchenne Muscular Dystrophy
  • +2 more
  • Ataluren
  • Parkville, Melbourne, Australia
  • +20 more
Nov 3, 2020

Muscular Dystrophy, Duchenne, Muscular Dystrophies, Muscular Disorders, Atrophic Trial in Worldwide (Ataluren, PLACEBO)

Active, not recruiting
  • Muscular Dystrophy, Duchenne
  • +8 more
  • Ataluren
  • PLACEBO
  • Phoenix, Arizona
  • +71 more
Mar 30, 2022

Duchenne Muscular Dystrophy, Becker Muscular Dystrophy Trial in United Kingdom, United States (Ataluren, Chronic Corticosteroid

Terminated
  • Duchenne Muscular Dystrophy
  • Becker Muscular Dystrophy
  • Ataluren
  • Chronic Corticosteroid Therapy
  • Davis, California
  • +5 more
Jul 27, 2020

Cystic Fibrosis Trial in Jerusalem (Ataluren)

Completed
  • Cystic Fibrosis
  • Ataluren
  • Jerusalem, Israel
    Hadassah University Hospital - Mount Scopus
Jun 10, 2020

Amino Acid Metabolism, Inborn Errors Trial in Worldwide (Ataluren)

Terminated
  • Amino Acid Metabolism, Inborn Errors
  • Ataluren
  • Antwerp, Belgium
  • +8 more
Jun 22, 2020

Cystic Fibrosis Trial in Birmingham (Ataluren)

Completed
  • Cystic Fibrosis
  • Ataluren
  • Birmingham, Alabama
    University of Alabama at Birmingham
Mar 25, 2020

Cystic Fibrosis Trial in Worldwide (Ataluren)

Completed
  • Cystic Fibrosis
  • Ataluren
  • Birmingham, Alabama
  • +30 more
Oct 16, 2020

Hemophilia A, Hemophilia B Trial in Worldwide (Ataluren)

Terminated
  • Hemophilia A
  • Hemophilia B
  • Ataluren
  • Peoria, Illinois
  • +12 more
May 28, 2020

Cystic Fibrosis Trial in Brussels, Leuven, Paris (Ataluren)

Completed
  • Cystic Fibrosis
  • Ataluren
  • Brussels, Belgium
  • +2 more
Feb 21, 2020

Cystic Fibrosis Trial in Worldwide (Ataluren)

Terminated
  • Cystic Fibrosis
  • Ataluren
  • Birmingham, Alabama
  • +16 more
Mar 11, 2020

Aniridia Trial (Ataluren)

Withdrawn
  • Aniridia
  • Ataluren
  • (no location specified)
Oct 3, 2019

Muscular Dystrophy, Duchenne, Muscular Dystrophies, Muscular Disorders, Atrophic Trial in Worldwide (Ataluren)

Terminated
  • Muscular Dystrophy, Duchenne
  • +8 more
  • Ataluren
  • Los Angeles, California
  • +57 more
Aug 10, 2020

Muscular Dystrophy, Duchenne, Muscular Dystrophies, Muscular Disorders, Atrophic Trial in Worldwide (Ataluren, Placebo)

Completed
  • Muscular Dystrophy, Duchenne
  • +8 more
  • Ataluren
  • Placebo
  • Los Angeles, California
  • +54 more
Jul 17, 2020

Cystic Fibrosis Trial in Worldwide (Ataluren, Placebo)

Completed
  • Cystic Fibrosis
  • Ataluren
  • Placebo
  • Birmingham, Alabama
  • +37 more
May 4, 2020

Duchenne Muscular Dystrophy, Becker Muscular Dystrophy Trial in Worldwide (Ataluren)

Terminated
  • Duchenne Muscular Dystrophy
  • Becker Muscular Dystrophy
  • Ataluren
  • Sacramento, California
  • +36 more
Jun 26, 2020

Duchenne Muscular Dystrophy, Becker Muscular Dystrophy Trial in Worldwide (Ataluren, Placebo)

Completed
  • Duchenne Muscular Dystrophy
  • Becker Muscular Dystrophy
  • Ataluren
  • Placebo
  • Sacramento, California
  • +36 more
Mar 26, 2020

Cystic Fibrosis Trial in Worldwide (Ataluren)

Terminated
  • Cystic Fibrosis
  • Ataluren
  • Birmingham, Alabama
  • +69 more
Apr 14, 2020

Healthy Trial in Quebec (Ataluren, Rifampin)

Completed
  • Healthy
  • Quebec, Canada
    Inventiv
Dec 20, 2017