miglustat
Showing 1 - 12 of 12
Glycogen Storage Disease Type II Infantile Onset Trial in Gainesville (Cipaglucosidase alfa (ATB200), Miglustat (AT2221))
Recruiting
- Glycogen Storage Disease Type II Infantile Onset
- Cipaglucosidase alfa
- Miglustat
-
Gainesville, FloridaUniversity of Florida Clinical Research Center
Jan 18, 2023
GM2 Gangliosidosis, Supportive Care Trial in Kashan, Mashhad, Tehran (Miglustat)
Recruiting
- GM2 Gangliosidosis
- Supportive Care
- Miglustat
-
Kashan, Isfahan, Iran, Islamic Republic of
- +2 more
Oct 23, 2022
Pompe Disease Trial in New York, Fairfax (biological, drug, other)
Not yet recruiting
- Pompe Disease
- Cipaglucosidase alfa
- +3 more
-
New York, New York
- +1 more
Nov 2, 2023
GM1 Gangliosidoses, GM2 Gangliosidoses, Tay-Sachs Disease Trial in Minneapolis (miglustat, Ketogenic Diet)
Terminated
- GM1 Gangliosidoses
- +3 more
- miglustat
- Ketogenic Diet
-
Minneapolis, MinnesotaUniversity of Minnesota
Mar 18, 2021
Gaucher Disease Trial in Taipei (Miglustat, ERT)
Unknown status
- Gaucher Disease
- Miglustat
- ERT
-
Taipei, TaiwanNational Taiwan University Hospital
Mar 28, 2019
Gaucher Disease Type 1 Trial in Worldwide (Miglustat)
Completed
- Gaucher Disease Type 1
- Miglustat
-
San Francisco, California
- +19 more
Oct 24, 2018
Gangliosidoses GM2 Trial in Toronto (miglustat)
Completed
- Gangliosidoses GM2
- miglustat
-
Toronto, Ontario, CanadaThe Hospital for Sick Children
May 18, 2016
Cystic Fibrosis Trial in Brussels (miglustat, )
Completed
- Cystic Fibrosis
- miglustat
- placebo
-
Brussels, BelgiumUniversite Catholique de Louvain
Mar 5, 2014
Cystic Fibrosis Trial in Brussels (Miglustat, Placebo)
Completed
- Cystic Fibrosis
- Miglustat
- Placebo
-
Brussels, BelgiumCliniques Universitaires St Luc (Université Catholique de Louvai
Aug 9, 2011
Niemann-Pick Type C Disease Trial in New York (miglustat)
Completed
- Niemann-Pick Type C Disease
- miglustat
-
New York, New YorkColumbia University Medical Center
Mar 24, 2010
Cystic Fibrosis Trial in Barcelona (miglustat, )
Terminated
- Cystic Fibrosis
- miglustat
- placebo
-
Barcelona, SpainCorporacio Parc Tauli / Parc Tauli Hospital
Feb 11, 2010