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miglustat

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STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Glycogen Storage Disease Type II Infantile Onset Trial in Gainesville (Cipaglucosidase alfa (ATB200), Miglustat (AT2221))

Recruiting
  • Glycogen Storage Disease Type II Infantile Onset
  • Cipaglucosidase alfa
  • Miglustat
  • Gainesville, Florida
    University of Florida Clinical Research Center
Jan 18, 2023

GM2 Gangliosidosis, Supportive Care Trial in Kashan, Mashhad, Tehran (Miglustat)

Recruiting
  • GM2 Gangliosidosis
  • Supportive Care
  • Miglustat
  • Kashan, Isfahan, Iran, Islamic Republic of
  • +2 more
Oct 23, 2022

Pompe Disease Trial in New York, Fairfax (biological, drug, other)

Not yet recruiting
  • Pompe Disease
  • Cipaglucosidase alfa
  • +3 more
  • New York, New York
  • +1 more
Nov 2, 2023

GM1 Gangliosidoses, GM2 Gangliosidoses, Tay-Sachs Disease Trial in Minneapolis (miglustat, Ketogenic Diet)

Terminated
  • GM1 Gangliosidoses
  • +3 more
  • miglustat
  • Ketogenic Diet
  • Minneapolis, Minnesota
    University of Minnesota
Mar 18, 2021

Gaucher Disease Trial in Taipei (Miglustat, ERT)

Unknown status
  • Gaucher Disease
  • Taipei, Taiwan
    National Taiwan University Hospital
Mar 28, 2019

Gaucher Disease Type 1 Trial in Worldwide (Miglustat)

Completed
  • Gaucher Disease Type 1
  • Miglustat
  • San Francisco, California
  • +19 more
Oct 24, 2018

Pompe Disease Undergoing Immune Modulation Therapies

Completed
  • Pompe Disease
  • Gainesville, Florida
    University of Florida
Dec 6, 2017

Gangliosidoses GM2 Trial in Toronto (miglustat)

Completed
  • Gangliosidoses GM2
  • miglustat
  • Toronto, Ontario, Canada
    The Hospital for Sick Children
May 18, 2016

Cystic Fibrosis Trial in Brussels (miglustat, )

Completed
  • Cystic Fibrosis
  • miglustat
  • placebo
  • Brussels, Belgium
    Universite Catholique de Louvain
Mar 5, 2014

Cystic Fibrosis Trial in Brussels (Miglustat, Placebo)

Completed
  • Cystic Fibrosis
  • Miglustat
  • Placebo
  • Brussels, Belgium
    Cliniques Universitaires St Luc (Université Catholique de Louvai
Aug 9, 2011

Niemann-Pick Type C Disease Trial in New York (miglustat)

Completed
  • Niemann-Pick Type C Disease
  • miglustat
  • New York, New York
    Columbia University Medical Center
Mar 24, 2010

Cystic Fibrosis Trial in Barcelona (miglustat, )

Terminated
  • Cystic Fibrosis
  • miglustat
  • placebo
  • Barcelona, Spain
    Corporacio Parc Tauli / Parc Tauli Hospital
Feb 11, 2010