eye diseases, hereditary

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STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Leber Congenital Amaurosis 10, Inherited Retinal Dystrophies, Eye Diseases, Hereditary Trial in United States (EDIT-101)

Active, not recruiting
  • Leber Congenital Amaurosis 10
  • +6 more
  • Miami, Florida
  • +4 more
Dec 2, 2022

Natural History of PRPF31 Mutation-Associated Retinal Dystrophy

Recruiting
  • Retinitis Pigmentosa
  • +4 more
    • San Francisco, California
    • +4 more
    Oct 5, 2022

    Retinitis Pigmentosa, Usher Syndrome Type 2, Deaf Blind Trial in Worldwide (Ultevursen, Sham-procedure)

    Recruiting
    • Retinitis Pigmentosa
    • +7 more
    • San Diego, California
    • +14 more
    Jul 29, 2022

    Natural History Study of CEP290-Related Retinal Degeneration

    Completed
    • Blindness
    • +7 more
      • Miami, Florida
      • +6 more
      May 18, 2022

      Retinitis Pigmentosa, Usher Syndrome Type 2, Deaf Blind Trial in Canada, France, United States (QR-421a, Sham-procedure (dose

      Completed
      • Retinitis Pigmentosa
      • +7 more
      • QR-421a
      • Sham-procedure (dose cohort 1&2 only)
      • Boston, Massachusetts
      • +6 more
      Apr 19, 2022