AAV Vectors
Showing 1 - 25 of 208
Seroprevalence and Seroconversion of Antibodies to
Recruiting
- Hemophilia A
- Blood sample collection
-
Madison, WisconsinCovance Inc
Sep 16, 2022
Study in Subjects Who Received vMCO-I Administered Via
Enrolling by invitation
- Retinitis Pigmentosa
- +2 more
- Gene Therapy product:vMCO-I
-
Cuttack, Odisha, IndiaJPM Rotary Club of Cuttack Eye Hospital and Research Institute
Jun 26, 2023
Parkinson's Disease Trial run by the National Institute of Neurological Disorders and Stroke (NINDS) (Convection enhanced
Completed
- Parkinson's Disease
- Convection enhanced delivery/AAV2-GDNF
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 26, 2023
Alpha 1-Antitrypsin Deficiency Trial in Gainesville, Worcester (rAAV2-CB-hAAT Gene Vector)
Completed
- Alpha 1-Antitrypsin Deficiency
- rAAV2-CB-hAAT Gene Vector
-
Gainesville, Florida
- +1 more
Apr 8, 2020
Liver Biopsy In Haemophilia Gene Therapy
Not yet recruiting
- Hemophilia B, Severe
- Hemophilia A, Severe
- (no location specified)
Mar 23, 2021
Retinitis Pigmentosa, Retinitis, Retinal Diseases Trial in Puerto Rico, United States (Gene Therapy Product-vMCO-010, Sham
Active, not recruiting
- Retinitis Pigmentosa
- +6 more
- Gene Therapy Product-vMCO-010
- Sham Injection
-
Beverly Hills, California
- +6 more
Jul 13, 2022
Hypertriglyceridemia, Familial Trial in Nanjing (GC304)
Not yet recruiting
- Hypertriglyceridemia, Familial
- GC304
-
Nanjing, ChinaAffiliated Jinling Hospital, Medical School, Nanjing University
May 5, 2023
Squamous Cell Head Neck Cancer, Radiation Induced Xerostomia, Salivary Hypofunction Trial run by the (AAV2hAQP1)
Recruiting
- Squamous Cell Head and Neck Cancer
- +2 more
- AAV2hAQP1
-
Bethesda, MarylandNational Institutes of Health Clinical Center, 9000 Rockville Pi
May 3, 2022
Non-syndromic Retinitis Pigmentosa Trial in Pittsburgh, Paris, London (Gene therapy: GS030-DP AND Medical device: GS030-MD)
Recruiting
- Non-syndromic Retinitis Pigmentosa
- Gene therapy: GS030-DP AND Medical device: GS030-MD
-
Pittsburgh, Pennsylvania
- +2 more
Jul 25, 2022
Hemophilia B Trial in Washington (SB-FIX)
Terminated
- Hemophilia B
- SB-FIX
-
Washington, District of ColumbiaGeorgetown University Medical Center
Mar 8, 2022
Pompe Disease (Late-onset) Trial (No Intervention)
Not yet recruiting
- Pompe Disease (Late-onset)
- No Intervention
- (no location specified)
Nov 21, 2023
Pompe Disease Trial in Gainesville (genetic, drug, other)
Completed
- Pompe Disease
- Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase
- +7 more
-
Gainesville, FloridaClinical and Translational Research Building (CTRB), University
Mar 24, 2022
MPS I Trial in Oakland (SB-318)
Terminated
- MPS I
- SB-318
-
Oakland, CaliforniaUCSF Benioff Children's Hospital Oakland
Jan 6, 2023
Leber Hereditary Optic Neuropathy Trial in Worldwide (GS010, Placebo)
Active, not recruiting
- Leber Hereditary Optic Neuropathy
- GS010
- Placebo
-
Pasadena, California
- +12 more
Aug 2, 2022
Liver Biopsy Following Gene Therapy For Hemophilia
Not yet recruiting
- Hemophilia A
- Hemophilia B
- Liver Biopsy
-
Memphis, TennesseeSt. Jude Children's Research Hospital
Jun 27, 2023
Leber Hereditary Optic Neuropathy Trial in Worldwide (GS010, Sham)
Completed
- Leber Hereditary Optic Neuropathy
- GS010
- Sham
-
Pasadena, California
- +6 more
Jul 25, 2022
Anti-Neutrophil Cytoplasmic Antibody-Associated Vasculitis, End Stage Renal Disease Trial in France (Discontinuation (or not
Recruiting
- Anti-Neutrophil Cytoplasmic Antibody-Associated Vasculitis
- End Stage Renal Disease
- Discontinuation (or not initiation) of Immunosuppressive Therapy
- Maintenance (or initiation) of immunosuppressive treatment: Imurel®, Mabthera®,Cellcept®, Cortancyl®
-
Amiens, France
- +54 more
Jan 6, 2023
Antineutrophil Cytoplasmic Antibody-associated Vasculitis Trial (Avacopan, Placebo, Standard of Care)
Not yet recruiting
- Antineutrophil Cytoplasmic Antibody-associated Vasculitis
- Avacopan
- +2 more
- (no location specified)
Oct 6, 2023
Avacostar - (PASS)
Not yet recruiting
- ANCA-associated Vasculitis
- (no location specified)
Jun 12, 2023
Bietti's Crystalline Dystrophy Trial in Beijing (ZVS101e)
Recruiting
- Bietti's Crystalline Dystrophy
-
Beijing, Beijing, ChinaPeking University Third Hospital
Feb 2, 2023
Parkinson Disease Trial in United States (AAV-GAD)
Enrolling by invitation
- Parkinson Disease
- AAV-GAD
-
West Bloomfield, Michigan
- +4 more
Jun 7, 2023
Subclinical Cytomegalovirus Reactivation in Acute
Recruiting
- ANCA Associated Vasculitis
-
Birmingham, West Midlands, United KingdomUniversity Hospitals Birmingham
Jan 15, 2023
Age-Related Macular Degeneration Trial in Toronto (NG101 AAV gene therapy)
Not yet recruiting
- Age-Related Macular Degeneration
- NG101 AAV gene therapy
-
Toronto, Ontario, CanadaVitreous Retina Macula Specialists of Toronto
Aug 2, 2023