F508del
Showing 1 - 25 of 4,260
Orkambi Treatment in 2 to 5 Year Old Children With CF
Completed
- Cystic Fibrosis
-
Philadelphia, PennsylvaniaChildren's Hospital of Philadelphia
Dec 1, 2021
Cystic Fibrosis Trial in United States (Tezacaftor/Ivacaftor, Ivacaftor, Tezacaftor/Ivacaftor matching )
Lumacaftor/Ivacaftor on F508del Homozygous Cystic Fibrosis
Completed
- Cystic Fibrosis
- Lumacaftor, Ivacaftor Drug Combination
- (no location specified)
Feb 2, 2021
Cystic Fibrosis Trial in Worldwide (VX-121/TEZ/D-IVA, ELX/TEZ/IVA, IVA)
Active, not recruiting
- Cystic Fibrosis
- VX-121/TEZ/D-IVA
- +5 more
-
Birmingham, Alabama
- +169 more
Dec 22, 2022
Lumacaftor/Ivacaftor in Cystic Fibrosis Homozygote for F508del
Recruiting
- Cystic Fibrosis in Children
-
Düsseldorf, Germany
- +1 more
Nov 9, 2020
Cystic Fibrosis Trial in Worldwide (VX-371 + HS, Hypertonic saline, Placebo)
Completed
- Cystic Fibrosis
- VX-371 + HS
- +4 more
-
Little Rock, Arkansas
- +39 more
Jul 8, 2021
Cystic Fibrosis Trial in Worldwide (TEZ/IVA, IVA)
Active, not recruiting
- Cystic Fibrosis
-
Birmingham, Alabama
- +54 more
Oct 28, 2022