Mucopolysaccharidoses
Showing 1 - 25 of 164
Iris Cameras in Mucopolysaccharidoses
Not yet recruiting
- Mucopolysaccharidoses
- Imaging
-
Manchester, United KingdomManchester University NHS Foundation Trust
Aug 30, 2022
Cardiovascular Structure and Function in Mucopolysaccharidoses
Recruiting
- Mucopolysaccharidoses
- +3 more
- Carotid ultrasonography
- +2 more
-
Orange, CaliforniaChildren's Hospital of Orange County
Jul 18, 2022
Set for Head, Neck and Respiratory Disease in
Completed
- Mucopolysaccharidosis Type II
-
Manchester, Lancashire, United KingdomManchester University NHS Foundation Trust
Aug 31, 2023
Mucopolysaccharidosis III-A Trial in Hamburg (JR-441)
Recruiting
- Mucopolysaccharidosis III-A
-
Hamburg, GermanyUniversitätsklinikum Hamburg-Eppendorf
Oct 18, 2023
Long Term Follow-Up for RGX-111
Enrolling by invitation
- Mucopolysaccharidosis I
- No Intervention
-
Orange, California
- +2 more
Oct 25, 2023
Participants With Sanfilippo Syndrome Type IIIC
Not yet recruiting
- Sanfilippo Syndrome Type C
-
Bron, FranceHospices Civils De Lyon
Apr 20, 2023
Hunter Syndrome Trial in Lexington
Recruiting
- Hunter Syndrome
-
Lexington, MassachusettsShire
Nov 7, 2022
Mucopolysaccharidosis I Trial in Wuhan (Laronidase)
Recruiting
- Mucopolysaccharidosis I
-
Wuhan, ChinaInvestigational Site Number :1560001
Jan 15, 2023
Mucopolysaccharidosis IH/S, Mucopolysaccharidosis IS Trial in Minneapolis (Autologous Plasmablasts (B cells))
Not yet recruiting
- Mucopolysaccharidosis IH/S
- Mucopolysaccharidosis IS
- Autologous Plasmablasts (B cells)
-
Minneapolis, MinnesotaUniversity of Minnesota
Jan 20, 2023
MPS II Immunophenotyping
Recruiting
- MPS II
- +2 more
-
Durham, North CarolinaDuke University
Jun 3, 2022
Adrenoleukodystrophy, Batten Disease, Mucopolysaccharidosis II Trial in Durham (DUOC-01)
Recruiting
- Adrenoleukodystrophy
- +11 more
- DUOC-01
-
Durham, North CarolinaDuke University Medical Center
Oct 24, 2022
Before and After Hematopoietic Cell Transplantation in
Enrolling by invitation
- Hematopoietic Cell Transplantation
- Mucopolysaccharidosis Type I
- Laronidase therapy and a stem cell transplant
-
Minneapolis, MinnesotaUniversity of Minnesota Masonic Cancer Center
Nov 22, 2022
Mucopolysaccharidosis II Trial in Cincinnati (DNL310)
Enrolling by invitation
- Mucopolysaccharidosis II
-
Cincinnati, OhioCincinnati Children's Hospital Medical Center
Oct 10, 2023
Mucopolysaccharidosis II Trial in Oakland (JR-141)
Not yet recruiting
- Mucopolysaccharidosis II
-
Oakland, CaliforniaUCSF Benioff Children's Hospital Oakland
Oct 21, 2022
MPS I Trial in Oakland (SB-318)
Terminated
- MPS I
- SB-318
-
Oakland, CaliforniaUCSF Benioff Children's Hospital Oakland
Jan 6, 2023
Mucopolysaccharidosis Type II Observational
Withdrawn
- Mucopolysaccharidosis II
- Observational
-
Oakland, California
- +2 more
Oct 6, 2022
Mucopolysaccharidosis Type IH (MPS IH, Hurler Syndrome), Mucopolysaccharidosis Type IH, MPS IH, Hurler Syndrome Trial
Withdrawn
- Mucopolysaccharidosis Type IH (MPS IH, Hurler Syndrome)
- +2 more
- Autologous Plasmablasts
- (no location specified)
Oct 5, 2022
MPS I, MPS1-S, MPS1-HS Trial in Porto Alegre, London, Salford (SIG-005 (hIDUA Producing Spheres))
Withdrawn
- MPS I
- +2 more
- SIG-005 (hIDUA Producing Spheres)
-
Porto Alegre, Brazil
- +2 more
Dec 16, 2022
Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis IV A Trial in San Francisco (There is no intervention)
Recruiting
- Mucopolysaccharidosis I
- +7 more
- There is no intervention
-
San Francisco, CaliforniaUniversity of California San Francisco
Nov 9, 2022
Mucopolysaccharidosis Type I (MPS I), Hurler Syndrome, Hurler-Scheie Syndrome Trial in Orange, Philadelphia, Porto Alegre
Active, not recruiting
- Mucopolysaccharidosis Type I (MPS I)
- +2 more
- RGX-111
-
Orange, California
- +3 more
Jan 9, 2023
Mucopolysaccharidosis (MPS), Hunter Syndrome Trial (ELAPRASE, Rituximab, Methotrexate)
Not yet recruiting
- Mucopolysaccharidosis (MPS)
- Hunter Syndrome
- ELAPRASE
- +3 more
- (no location specified)
Aug 8, 2022
Mucopolysaccharidosis II Trial (Autologous CD34+ HSCs transduced ex vivo with CD11B LV encoding human IDS tagged with ApoEII)
Not yet recruiting
- Mucopolysaccharidosis II
- Autologous CD34+ HSCs transduced ex vivo with CD11B LV encoding human IDS tagged with ApoEII
- (no location specified)
Dec 16, 2022
Study of Patients With MPS IIIA Treated With ABO-102
Enrolling by invitation
- Mucopolysaccharidosis III-A
- ABO-102
-
Columbus, Ohio
- +2 more
Nov 8, 2022