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mucopolysaccharidosis

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STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Mucopolysaccharidosis III-A Trial in Hamburg (JR-441)

Recruiting
  • Mucopolysaccharidosis III-A
  • Hamburg, Germany
    Universitätsklinikum Hamburg-Eppendorf
Oct 18, 2023

Set for Head, Neck and Respiratory Disease in

Completed
  • Mucopolysaccharidosis Type II
    • Manchester, Lancashire, United Kingdom
      Manchester University NHS Foundation Trust
    Aug 31, 2023

    MPS (RaDiCo Cohort) (RaDiCo-MPS)

    Recruiting
    • Mucopolysaccharidosis I
    • +7 more
      • Angers, France
      • +22 more
      Sep 12, 2023

      Mucopolysaccharidosis IH/S, Mucopolysaccharidosis IS Trial in Minneapolis (Autologous Plasmablasts (B cells))

      Not yet recruiting
      • Mucopolysaccharidosis IH/S
      • Mucopolysaccharidosis IS
      • Autologous Plasmablasts (B cells)
      • Minneapolis, Minnesota
        University of Minnesota
      Jan 20, 2023

      Mucopolysaccharidosis II Trial in Cincinnati (DNL310)

      Enrolling by invitation
      • Mucopolysaccharidosis II
      • Cincinnati, Ohio
        Cincinnati Children's Hospital Medical Center
      Oct 10, 2023

      Before and After Hematopoietic Cell Transplantation in

      Enrolling by invitation
      • Hematopoietic Cell Transplantation
      • Mucopolysaccharidosis Type I
      • Laronidase therapy and a stem cell transplant
      • Minneapolis, Minnesota
        University of Minnesota Masonic Cancer Center
      Nov 22, 2022

      Mucopolysaccharidosis II Trial in Porto Alegre, São Paulo (JR-141)

      Completed
      • Mucopolysaccharidosis II
      • Porto Alegre, Brazil
      • +1 more
      Nov 10, 2022

      Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis VI Trial in Torrance (Adalimumab Injection [Humira],

      Recruiting
      • Mucopolysaccharidosis I
      • +2 more
      • Adalimumab Injection [Humira]
      • Saline Solution for Injection
      • Torrance, California
        The Lundquist Institute at Harbor-UCLA Medical Center
      Aug 9, 2022

      Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis IV A Trial in San Francisco (There is no intervention)

      Recruiting
      • Mucopolysaccharidosis I
      • +7 more
      • There is no intervention
      • San Francisco, California
        University of California San Francisco
      Nov 9, 2022

      Mucopolysaccharidosis II Trial in Japan (JR-141)

      Completed
      • Mucopolysaccharidosis II
      • Gifu, Japan
      • +7 more
      Nov 10, 2022

      Mucopolysaccharidosis II Trial in Oakland (JR-141)

      Not yet recruiting
      • Mucopolysaccharidosis II
      • Oakland, California
        UCSF Benioff Children's Hospital Oakland
      Oct 21, 2022

      Mucopolysaccharidosis Type II Observational

      Withdrawn
      • Mucopolysaccharidosis II
      • Observational
      • Oakland, California
      • +2 more
      Oct 6, 2022

      Mucopolysaccharidosis I Trial in Brazil, Japan, United States (JR-171)

      Completed
      • Mucopolysaccharidosis I
      • Oakland, California
      • +5 more
      Aug 16, 2022

      Mucopolysaccharidosis II Trial in Worldwide (JR-141, Idursulfase, JR-141 or Idursulfase)

      Recruiting
      • Mucopolysaccharidosis II
      • Oakland, California
      • +8 more
      Dec 2, 2022

      Mucopolysaccharidosis Type IIIB, MPS III B Trial in Worldwide (AX 250)

      Active, not recruiting
      • Mucopolysaccharidosis Type IIIB
      • MPS III B
      • AX 250
      • Oakland, California
      • +7 more
      Jan 16, 2023

      Mucopolysaccharidosis I Trial in Wuhan (Laronidase)

      Recruiting
      • Mucopolysaccharidosis I
      • Wuhan, China
        Investigational Site Number :1560001
      Jan 15, 2023

      MPS VII, Mucopolysaccharidosis VII, Sly Syndrome Trial (Mepsevii)

      Available
      • MPS VII
      • +2 more
      • (no location specified)
      Nov 22, 2022

      Mucopolysaccharidosis II Trial in Oakland, Chapel Hill (DNL310, Idursulfase)

      Recruiting
      • Mucopolysaccharidosis II
      • Oakland, California
      • +11 more
      Jan 9, 2023

      Long Term Follow-Up for RGX-111

      Enrolling by invitation
      • Mucopolysaccharidosis I
      • No Intervention
      • Orange, California
      • +2 more
      Oct 25, 2023

      Mucopolysaccharidosis Type II Natural History

      Completed
      • Mucopolysaccharidosis II
        • Pittsburgh, Pennsylvania
        • +2 more
        Apr 22, 2022

        Mucopolysaccharidosis (MPS), Hunter Syndrome Trial (ELAPRASE, Rituximab, Methotrexate)

        Not yet recruiting
        • Mucopolysaccharidosis (MPS)
        • Hunter Syndrome
        • (no location specified)
        Aug 8, 2022

        Participants With Sanfilippo Syndrome Type IIIC

        Not yet recruiting
        • Sanfilippo Syndrome Type C
          • Bron, France
            Hospices Civils De Lyon
          Apr 20, 2023

          (LTFU) of Subjects Who Received SB-318, SB-913, or SB-FIX

          Active, not recruiting
          • Hemophilia B
          • +2 more
          • SB-318
          • +2 more
          • Oakland, California
          • +4 more
          Jan 30, 2023

          Mucopolysaccharidosis II Trial in Japan (JR-141)

          Active, not recruiting
          • Mucopolysaccharidosis II
          • Fukui, Japan
          • +19 more
          Nov 30, 2022

          Mucopolysaccharidosis Type 3 B Trial in Worldwide (rAAV9.CMV.hNAGLU)

          Terminated
          • Mucopolysaccharidosis Type 3 B
          • rAAV9.CMV.hNAGLU
          • Columbus, Ohio
          • +3 more
          Apr 29, 2022