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thalassemia

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Thalassemia, Beta Trial in Karachi (Hydroxyurea and Thalidomide)

Completed
  • Thalassemia, Beta
  • Hydroxyurea and Thalidomide
  • Karachi, Sindh, Pakistan
    Children's Hospital Karachi
Nov 23, 2023

Bone Denisty Change in Children With Beta Thalassemia Major

Not yet recruiting
  • Evaluate Bone Denisty Changes in Children With Beta Thalassemia Major
  • Dexa scan
  • (no location specified)
Sep 29, 2023

Beta-Thalassemia Trial (CS-101 injection)

Not yet recruiting
  • Beta-Thalassemia
  • CS-101 injection
  • (no location specified)
Sep 27, 2023

Transfusion-dependent Beta-Thalassemia Trial in Peshawar (Thalidomide)

Completed
  • Transfusion-dependent Beta-Thalassemia
  • Peshawar, Khyber Pakhtunkhwa, Pakistan
    Blood Care Clinic
Nov 19, 2023

Thalassemia, Beta, Thalassemia Major Trial in Tianjin (VGB-Ex01)

Not yet recruiting
  • Thalassemia, Beta
  • Thalassemia Major
  • VGB-Ex01
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
Sep 11, 2023

Luspatercept in Korean Myelodysplastic Syndrome or ß-thalassemia

Not yet recruiting
  • Myelodysplastic Syndrome
  • Beta Thalassemia
  • Seoul, Korea, Republic of
    Bristol-Myers Squibb YH
Oct 3, 2023

Transfusion-dependent Beta-thalassemia After Gene Therapy

Recruiting
  • Transfusion-dependent Beta-Thalassemia
  • Gene Therapy
  • Gene therapy
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
Aug 6, 2023

Beta-Thalassemia Trial in Nanning (CS-101)

Recruiting
  • Beta-Thalassemia
  • CS-101
  • Nanning, China
    The First Affiliated Hospital of Guangxi Medical University
Sep 9, 2023

"Iron Overload and Endocrinological Diseases"

Recruiting
  • Iron Overload
  • +4 more
    • Modena, Italy
      Unit of Endocrinology of Azienza Ospedaliero-Universitaria di Mo
    Nov 13, 2023

    Pumilio1 Expression, Sickle Cell Anemia, ß-thalassemia

    Not yet recruiting
    • Sickle Cell Disease, Beta Thalassemia Intermedia
    • RNA Binding Protein Pumilio1 (PUM1) Expression by reverse transcriptase quantatative PCR
    • (no location specified)
    May 30, 2023

    Patients With Thalassemia Minor and Breast Cancer

    Completed
    • Breast Cancer
    • +2 more
      • Fatih, Istanbul, Turkey
        Istanbul Faculty of Medicine
      Jul 21, 2023

      ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)

      Recruiting
      • β-thalassemia
      • β-globin restored autologous hematopoietic stem cells
      • Shenzhen, Guangdong, China
        Shenzhen University General Hospital
      May 8, 2023

      a-thalassemia Trial in Nanning (a-globin restored autologous hematopoietic stem cells)

      Recruiting
      • α-thalassemia
      • α-globin restored autologous hematopoietic stem cells
      • Nanning, Guangxi, China
        PLA Joint Logistic Support Force No. 923 Hospital
      May 6, 2023

      Thalassemia Major Trial (n-acetylcystine)

      Not yet recruiting
      • Thalassemia Major
      • (no location specified)
      Mar 9, 2023

      Transfusion-dependent Beta-Thalassemia Trial in Tianjin (KL003 cell injection Drug Product)

      Not yet recruiting
      • Transfusion-dependent Beta-Thalassemia
      • KL003 cell injection Drug Product
      • Tianjin, Tianjin, China
        Regenerative Medicine Center
      May 8, 2023

      ß-thalassemia Trial (BD211)

      Not yet recruiting
      • β-thalassemia
      • BD211
      • (no location specified)
      Mar 15, 2023

      ß-thalassemia Trial in Shanghai (BD211)

      Not yet recruiting
      • β-thalassemia
      • BD211
      • Shanghai, China
        Shanghai Ruijin Hospital
      Mar 16, 2023

      Alpha-Thalassemia, Alpha Thalassemia Major, Alpha Thalassemia Minor Trial in San Francisco

      Recruiting
      • Alpha-Thalassemia
      • +2 more
        • San Francisco, California
          University of California San Francisco
        Oct 7, 2022

        ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)

        Recruiting
        • β-thalassemia
        • β-globin restored autologous hematopoietic stem cells
        • Shenzhen, Guangdong, China
          Shenzhen Children's Hospital
        Feb 24, 2023

        Screening for Alpha Thalassemia in Healthy Volunteers

        Recruiting
        • Alpha Thalassemia
          • Bethesda, Maryland
            National Institutes of Health Clinical Center
          Jan 26, 2023

          Transfusion-dependent Thalassemia Trial in Dhaka (Thalidomide Capsules, Placebo)

          Recruiting
          • Transfusion-dependent Thalassemia
          • Thalidomide Capsules
          • Placebo
          • Dhaka, Bangladesh
            Bangabandhu Sheikh Mujib Medical University
          Oct 18, 2023

          Alpha Thalassemia Major, Hemoglobinopathy; With Thalassemia, Hemoglobinopathies Trial in San Francisco (in utero hematopoietic

          Enrolling by invitation
          • Alpha Thalassemia Major
          • +8 more
          • in utero hematopoietic stem cell transplantation
          • San Francisco, California
            University of California
          Oct 28, 2022

          Beta Thalassemia Major Anemia Trial (SP-420)

          Not yet recruiting
          • Beta Thalassemia Major Anemia
          • (no location specified)
          Jan 20, 2023

          Transfusion-dependent a-Thalassemia Trial (GMCN-508A Drug Product)

          Not yet recruiting
          • Transfusion-dependent α-Thalassemia
          • GMCN-508A Drug Product
          • (no location specified)
          Feb 24, 2023

          The Prevelence of HBB c.93-21 G-A in ß Thalassemia Patients

          Recruiting
          • Beta-Thalassemia
          • ARMS PCR
          • Assiut, Egypt
            Faculty of Medicine Assiut University
          Jan 30, 2023