spinal muscular atrophy
Showing 1 - 25 of 117
Cystinosis, Cystinosis, Nephropathic, Spinal Muscular Atrophy Trial in Germany (molecular-based screening)
Completed
- Cystinosis
- +2 more
- molecular-based screening
-
Rosenheim, Bavaria, Germany
- +3 more
Aug 30, 2023
Outcomes of SMA in the West Midlands During 2017-2022
Not yet recruiting
- Spinal Muscular Atrophy
- (no location specified)
Aug 15, 2023
Motor Function and Activity of Daily Life in Spinal Muscular
Not yet recruiting
- Spinal Muscular Atrophy
-
Taipei, TaiwanNational Taiwan University Hospital
Jul 5, 2023
Development ofMultidisciplinary Network for Clinical and
Not yet recruiting
- Spinal Muscular Atrophy
- (no location specified)
May 10, 2023
Spinal Muscular Atrophy Trial in Beijing, Shenyang, Suzhou (GC101)
Recruiting
- Spinal Muscular Atrophy
- GC101
-
Beijing, China
- +3 more
Apr 22, 2023
Personalized Medicine for SMA: a Translational Project
Recruiting
- Spinal Muscular Atrophy
-
Rome, Italy
- +1 more
Mar 9, 2023
MAP THE SMA:Machine-learning Based Algorithm to Predict
Not yet recruiting
- Spinal Muscular Atrophy
- disease modifying treatments
- (no location specified)
Mar 14, 2023
SMN Circular RNAs as Potential Biomarkers for Therapeutic
Recruiting
- Spinal Muscular Atrophy
-
Rome, Italy/rome, Italyethics committee of IRCCS Fondazione Policlinico Gemelli
Mar 10, 2023
Long Term Trajectories of SMA Patients Receiving or Not
Recruiting
- Spinal Muscular Atrophy
-
Genova, Italy
- +4 more
Mar 2, 2023
SMN Circular RNAs as Potential New Targets and Biomarkers for
Recruiting
- Spinal Muscular Atrophy
-
Rome, ItalyPoliclinico gemelli
Feb 27, 2023
Non Invasive Ventilation, Spinal Muscular Atrophy, Respiratory Bacterial Infection Trial in Amiens (non invasive ventilation
Recruiting
- Non Invasive Ventilation
- +2 more
- non invasive ventilation samples
- +2 more
-
Amiens, Picardie, FranceCentre Hospitalier Universitaire d'Amiens
Jan 26, 2023
Spinal Muscular Atrophy Trial (OAV101)
Recruiting
- Spinal Muscular Atrophy
- OAV101
-
Montreal, Quebec, Canada
- +1 more
Jan 31, 2023
Spinal Muscular Atrophy Trial in Worldwide (Risdiplam)
Active, not recruiting
- Spinal Muscular Atrophy
-
Palo Alto, California
- +23 more
Jan 19, 2023
Spinal Muscular Atrophy Trial in Worldwide (OAV101)
Active, not recruiting
- Spinal Muscular Atrophy
- OAV101
-
Boston, Massachusetts
- +12 more
Jan 17, 2023
Impairments of Neuro-muscular Communication in Motor-Neuron
Recruiting
- ALS (Amyotrophic Lateral Sclerosis)
- +2 more
- 128 electrode electroencephalography (EEG), Bipolar surface electromyography (sEMG), High-density electromyography (HD-EMG)
-
Dublin, Leinster, IrelandAcademic Unit of Neurology, Trinity College Dublin, The Universi
Dec 21, 2022
Ultrasound-assisted or Landmark-based Intrathecal Administration
Not yet recruiting
- Anesthesia, Spinal
- +3 more
- Interlaminar ultrasound-assisted intrathecal administration of nusinersen
- Landmark-based intrathecal administration of nusinersen
-
Roma, RM, ItalyFondazione Policlinico Gemelli
Dec 12, 2022
Spinal Muscular Atrophy Trial (Rehabilitation Intervention)
Not yet recruiting
- Spinal Muscular Atrophy
- Rehabilitation Intervention
- (no location specified)
Nov 25, 2022
Neurologic Diseases, Hemiparesis, Quadriplegia Trial in Wilmington, Philadelphia (Neurosleeve)
Recruiting
- Neurologic Diseases
- +13 more
- Neurosleeve
-
Wilmington, Delaware
- +1 more
Dec 2, 2022
Muscular Dystrophies, Spinal Muscular Atrophy, Duchenne Muscular Dystrophy Trial in Saint Paul (Abilitech Assist)
Recruiting
- Muscular Dystrophies
- +6 more
- Abilitech Assist
-
Saint Paul, MinnesotaGillette Children's
Dec 1, 2022
Spinal Muscular Atrophy Trial in Utrecht (Inspiratory and expiratory muscle training at a therapeutic intensity, Inspiratory and
Active, not recruiting
- Spinal Muscular Atrophy
- Inspiratory and expiratory muscle training at a therapeutic intensity
- Inspiratory and expiratory muscle training at a non-therapeutic intensity
-
Utrecht, NetherlandsUniversity Medical Center Utrecht
Nov 29, 2022
Spinal Muscular Atrophy, Spinal Muscular Atrophy Type 3, Spinal Muscular Atrophy Type II Trial in Worldwide (Apitegromab)
Not yet recruiting
- Spinal Muscular Atrophy
- +9 more
-
Phoenix, Arizona
- +26 more
Nov 15, 2022