Genetic Diseases, Inborn

Showing 26 - 32 of 32

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Lipid Metabolism, Inborn Errors, Hyperlipidemias, Metabolic Diseases Trial in Amsterdam (mipomersen, Placebo)

Completed
  • Lipid Metabolism, Inborn Errors
  • +13 more
  • Amsterdam, Netherlands
    (unnamed)
Sep 9, 2016

Lipid Metabolism, Inborn Errors, Hypercholesterolemia, Autosomal Dominant, Hyperlipidemias Trial in United States (mipomersen

Completed
  • Lipid Metabolism, Inborn Errors
  • +13 more
  • mipomersen sodium
  • Chicago, Illinois
  • +4 more
Aug 1, 2016

Lipid Metabolism, Inborn Errors, Hypercholesterolemia, Autosomal Dominant, Hyperlipidemias Trial in Worldwide (Mipomersen

Completed
  • Lipid Metabolism, Inborn Errors
  • +13 more
  • Mipomersen Sodium
  • Mission Viejo, California
  • +32 more
Aug 1, 2016

Lipid Metabolism, Inborn Errors, Hypercholesterolemia, Autosomal Dominant, Hyperlipidemias Trial in Worldwide (mipomersen,

Completed
  • Lipid Metabolism, Inborn Errors
  • +13 more
  • Charlotte, North Carolina
  • +9 more
Aug 1, 2016

Pre-Implantation Embryo Recovery, Genetic Diseases, Inborn Trial in Istanbul (Uterine Lavage Group)

Unknown status
  • Pre-Implantation Embryo Recovery
  • Genetic Diseases, Inborn
  • Uterine Lavage Group
  • Istanbul, Turkey
    Istanbul University School of Medicine
May 27, 2016

Familial Cold Autoinflammatory Syndrome (FCAS), Familial Cold Urticaria, Muckle-Wells Syndrome (MWS) Trial in United States

Completed
  • Familial Cold Autoinflammatory Syndrome (FCAS)
  • +3 more
  • rilonacept 160 mg
  • Placebo
  • Little Rock, Arkansas
  • +23 more
Dec 1, 2011

Coronary Arteriosclerosis, Hypoalphalipoproteinemias, Genetic Diseases, Inborn Trial in Montreal (Atorvastatin; Fenofibrate;

Completed
  • Coronary Arteriosclerosis
  • +2 more
  • Atorvastatin; Fenofibrate; Niacin
  • Montreal, Quebec, Canada
    MUHC-Royal Victoria Hospital
Jun 2, 2008