Leber Congenital Amaurosis
Showing 1 - 15 of 15
Leber Congenital Amaurosis Trial in Shanghai (HG004)
Recruiting
- Leber Congenital Amaurosis
- HG004
-
Shanghai, Shanghai, ChinaXinhua Hospital affiliated with Shanghai Jiao Tong UniversitySch
Oct 12, 2023
Leber Congenital Amaurosis Trial in Shanghai (HG004)
Recruiting
- Leber Congenital Amaurosis
- HG004
-
Shanghai, Shanghai, ChinaXinhua Hospital affiliated with Shanghai Jiao Tong University Sc
Sep 26, 2023
Rare Disorders, Undiagnosed Disorders, Disorders of Unknown Prevalence Trial in Sioux Falls, Sydney
Recruiting
- Rare Disorders
- +309 more
-
Sioux Falls, South Dakota
- +1 more
Jun 20, 2022
Leber Congenital Amaurosis Associated With Mutations in RPE65
Recruiting
- Leber Congenital Amaurosis
-
Ann Arbor, Michigan
- +1 more
Apr 7, 2022
Leber Congenital Amaurosis 10, Blindness, Leber Congenital Amaurosis Trial in Worldwide (sepofarsen, Sham)
Active, not recruiting
- Leber Congenital Amaurosis 10
- +9 more
- sepofarsen
- Sham
-
Iowa City, Iowa
- +13 more
Mar 2, 2022
Leber Congenital Amaurosis 10, Blindness, Leber Congenital Amaurosis Trial in Iowa City, Philadelphia, Ghent (QR-110)
Active, not recruiting
- Leber Congenital Amaurosis 10
- +9 more
-
Iowa City, Iowa
- +2 more
Feb 8, 2022
Inherited Retinal Dystrophy Due to RPE65 Mutations, Leber Congenital Amaurosis Trial in Iowa City, Philadelphia
Active, not recruiting
- Inherited Retinal Dystrophy Due to RPE65 Mutations
- Leber Congenital Amaurosis
- AAV2-hRPE65v2,voretigene neparvovec-rzyl
-
Iowa City, Iowa
- +1 more
Dec 9, 2021
Leber Congenital Amaurosis Trial in Philadelphia (voretigene neparvovec-rzyl)
Completed
- Leber Congenital Amaurosis
- voretigene neparvovec-rzyl
-
Philadelphia, PennsylvaniaThe Children's Hospital of Philadelphia
Oct 30, 2020
Leber Congenital Amaurosis Trial in Jerusalem (rAAV2-hRPE65)
Completed
- Leber Congenital Amaurosis
- rAAV2-hRPE65
-
Jerusalem, IsraelHadassah Medical Organization
Apr 8, 2018
Leber Congenital Amaurosis Trial in Worcester, Portland (rAAV2-CB-hRPE65)
Completed
- Leber Congenital Amaurosis
- rAAV2-CB-hRPE65
-
Worcester, Massachusetts
- +1 more
Dec 1, 2017
Genetic Decryption of Leber Congenital Amaurosis inLarge Cohort
Completed
- Leber Congenital Amaurosis
-
Paris, FranceNecker-Enfants Malades Hospital
Nov 18, 2016