Leber Congenital Amaurosis

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CONDITIONS
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Leber Congenital Amaurosis Trial in Shanghai (HG004)

Recruiting
  • Leber Congenital Amaurosis
  • HG004
  • Shanghai, Shanghai, China
    Xinhua Hospital affiliated with Shanghai Jiao Tong UniversitySch
Oct 12, 2023

Leber Congenital Amaurosis Trial in Shanghai (HG004)

Recruiting
  • Leber Congenital Amaurosis
  • HG004
  • Shanghai, Shanghai, China
    Xinhua Hospital affiliated with Shanghai Jiao Tong University Sc
Sep 26, 2023

Leber Congenital Amaurosis Trial (HG004)

Not yet recruiting
  • Leber Congenital Amaurosis
  • (no location specified)
Jun 13, 2023

Rare Disorders, Undiagnosed Disorders, Disorders of Unknown Prevalence Trial in Sioux Falls, Sydney

Recruiting
  • Rare Disorders
  • +309 more
    • Sioux Falls, South Dakota
    • +1 more
    Jun 20, 2022

    Leber Congenital Amaurosis Associated With Mutations in RPE65

    Recruiting
    • Leber Congenital Amaurosis
      • Ann Arbor, Michigan
      • +1 more
      Apr 7, 2022

      Leber Congenital Amaurosis 10, Blindness, Leber Congenital Amaurosis Trial in Worldwide (sepofarsen)

      Recruiting
      • Leber Congenital Amaurosis 10
      • +10 more
      • Ghent, Belgium
      • +8 more
      Mar 24, 2022

      Leber Congenital Amaurosis 10, Blindness, Leber Congenital Amaurosis Trial in Worldwide (sepofarsen, Sham)

      Active, not recruiting
      • Leber Congenital Amaurosis 10
      • +9 more
      • Iowa City, Iowa
      • +13 more
      Mar 2, 2022

      Leber Congenital Amaurosis 10, Blindness, Leber Congenital Amaurosis Trial in Iowa City, Philadelphia, Ghent (QR-110)

      Active, not recruiting
      • Leber Congenital Amaurosis 10
      • +9 more
      • Iowa City, Iowa
      • +2 more
      Feb 8, 2022

      Inherited Retinal Dystrophy Due to RPE65 Mutations, Leber Congenital Amaurosis Trial in Iowa City, Philadelphia

      Active, not recruiting
      • Inherited Retinal Dystrophy Due to RPE65 Mutations
      • Leber Congenital Amaurosis
      • AAV2-hRPE65v2,voretigene neparvovec-rzyl
      • Iowa City, Iowa
      • +1 more
      Dec 9, 2021

      Leber Congenital Amaurosis Trial in Ann Arbor, London (AAV RPE65)

      Completed
      • Leber Congenital Amaurosis
      • AAV RPE65
      • Ann Arbor, Michigan
      • +1 more
      Jun 17, 2021

      Leber Congenital Amaurosis Trial in Philadelphia (voretigene neparvovec-rzyl)

      Completed
      • Leber Congenital Amaurosis
      • voretigene neparvovec-rzyl
      • Philadelphia, Pennsylvania
        The Children's Hospital of Philadelphia
      Oct 30, 2020

      Leber Congenital Amaurosis Trial in Jerusalem (rAAV2-hRPE65)

      Completed
      • Leber Congenital Amaurosis
      • rAAV2-hRPE65
      • Jerusalem, Israel
        Hadassah Medical Organization
      Apr 8, 2018

      Leber Congenital Amaurosis Trial in Worcester, Portland (rAAV2-CB-hRPE65)

      Completed
      • Leber Congenital Amaurosis
      • rAAV2-CB-hRPE65
      • Worcester, Massachusetts
      • +1 more
      Dec 1, 2017

      Genetic Decryption of Leber Congenital Amaurosis inLarge Cohort

      Completed
      • Leber Congenital Amaurosis
        • Paris, France
          Necker-Enfants Malades Hospital
        Nov 18, 2016

        Leber Congenital Amaurosis Trial in Nantes (rAAV2/4.hRPE65)

        Completed
        • Leber Congenital Amaurosis
        • Nantes, France
          CHU Nantes
        Oct 6, 2015