acid maltase deficiency disease

Showing 1 - 6 of 6

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Pompe Disease, Glycogen Storage Disease Type II (GSD-II), Acid Maltase Deficiency Disease Trial in Gainesville, Decatur, Detroit

Completed
  • Pompe Disease
  • +2 more
  • alglucosidase alfa
  • Gainesville, Florida
  • +2 more
Jul 29, 2022

Pompe Disease, Glycogen Storage Disease Type II, Acid Maltase Deficiency Disease Trial in Durham (recombinant human acid

Completed
  • Pompe Disease
  • +3 more
  • recombinant human acid alpha-glucosidase (rhGAA)
  • Durham, North Carolina
    Duke University Medical Center
Nov 12, 2014

Glycogen Storage Disease Type II (GSD-II), Pompe Disease (Late-Onset), Acid Maltase Deficiency Disease Trial in United States

Approved for marketing
  • Glycogen Storage Disease Type II (GSD-II)
  • +3 more
  • alglucosidase alfa (recombinant human acid alpha-glucosidase [rhGAA])
  • Sheffield, Alabama
  • +73 more
Feb 4, 2014

Pompe Disease (Late-onset), Glycogen Storage Disease Type II (GSD-II), Acid Maltase Deficiency Disease Trial in Rotterdam

Completed
  • Pompe Disease (Late-onset)
  • +3 more
  • Myozyme
  • Rotterdam, Netherlands
    Sophia Kinderziekenhuis, Erasmus MC
Feb 4, 2014

Glycogen Storage Disease Type II, Pompe Disease, Acid Maltase Deficiency Disease Trial in New Brunswick (Alglucosidase alfa)

Completed
  • Glycogen Storage Disease Type II
  • +3 more
  • Alglucosidase alfa
  • New Brunswick, New Jersey
    Saint Peter's University Hospital
Feb 4, 2014

Glycogen Storage Disease Type II, Pompe Disease, Acid Maltase Deficiency Disease Trial in Worldwide (Myozyme)

Completed
  • Glycogen Storage Disease Type II
  • +3 more
  • Myozyme
  • Gainesville, Florida
  • +5 more
Feb 4, 2014