acute intermittent porphyria

Showing 1 - 10 of 10

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Acute Hepatic Porphyria, Acute Intermittent Porphyria, Porphyria, Acute Intermittent Trial in Worldwide (Givosiran, Placebo)

Completed
  • Acute Hepatic Porphyria
  • +6 more
  • Little Rock, Arkansas
  • +35 more
May 31, 2022

Acute Intermittent Porphyria, Hereditary Coproporphyria, Variegate Porphyria Trial in Galveston (Hemin for injection, Placebo)

Recruiting
  • Acute Intermittent Porphyria
  • +2 more
  • Hemin for injection
  • Placebo
  • Galveston, Texas
    University of Texas Medical Branch
Nov 23, 2021

Acute Intermittent Porphyria Trial in Sweden, United Kingdom, United States (givosiran (ALN-AS1))

Completed
  • Acute Intermittent Porphyria
  • givosiran (ALN-AS1)
  • San Francisco, California
  • +4 more
Nov 9, 2021

Acute Porphyria Biomarkers for Disease Activity

Active, not recruiting
  • Acute Intermittent Porphyria
  • +2 more
  • Galveston, Texas
    University of Texas Medical Branch
Jul 27, 2021

Dental Health, Diet, Inflammation and Biomarkers in Acute

Active, not recruiting
  • Acute Intermittent Porphyria
    • Bodø, Nordland, Norway
      Nordlandssykehuset HF
    Dec 3, 2020

    Acute Intermittent Porphyria Trial in Sweden, United Kingdom, United States (givosiran (ALN-AS1), Sterile Normal Saline (0.9%

    Completed
    • Acute Intermittent Porphyria
    • givosiran (ALN-AS1)
    • Sterile Normal Saline (0.9% NaCl)
    • Birmingham, Alabama
    • +5 more
    Jun 13, 2018

    Acute Intermittent Porphyria Trial in Galveston (recombinant human porphobilinogen deaminase (Porphozym))

    Completed
    • Acute Intermittent Porphyria
    • recombinant human porphobilinogen deaminase (Porphozym)
    • Galveston, Texas
      Univercity Texas Medical Branch
    Mar 7, 2018

    Anti-Psychotic, Management of Manifestations of Psychotic Disorders, Treatment of Schizophrenia Trial in Bloemfontein

    Completed
    • Anti-Psychotic
    • +8 more
    • Chlorpromazine Hydrochloride
    • Bloemfontein, Kampuslaan Suid, South Africa
      Farmovs Parexel
    Oct 12, 2017

    Acute Intermittent Porphyria Trial in Pamplona, Madrid (rAAV2/5-PBGD vector dosage 1, rAAV2/5-PBGD vector dosage 2, rAAV2/5-PBGD

    Completed
    • Acute Intermittent Porphyria
    • rAAV2/5-PBGD vector dosage 1
    • +3 more
    • Pamplona, Navarra, Spain
    • +1 more
    Dec 17, 2014

    Observational Study of Acute Intermittent Porphyria Patients

    Completed
    • Acute Intermittent Porphyria
      • Pamplona, Navarra, Spain
      • +1 more
      Mar 11, 2014