acute intermittent porphyria
Showing 1 - 10 of 10
Acute Hepatic Porphyria, Acute Intermittent Porphyria, Porphyria, Acute Intermittent Trial in Worldwide (Givosiran, Placebo)
Completed
- Acute Hepatic Porphyria
- +6 more
- Givosiran
- Placebo
-
Little Rock, Arkansas
- +35 more
May 31, 2022
Acute Intermittent Porphyria, Hereditary Coproporphyria, Variegate Porphyria Trial in Galveston (Hemin for injection, Placebo)
Recruiting
- Acute Intermittent Porphyria
- +2 more
- Hemin for injection
- Placebo
-
Galveston, TexasUniversity of Texas Medical Branch
Nov 23, 2021
Acute Intermittent Porphyria Trial in Sweden, United Kingdom, United States (givosiran (ALN-AS1))
Completed
- Acute Intermittent Porphyria
- givosiran (ALN-AS1)
-
San Francisco, California
- +4 more
Nov 9, 2021
Acute Porphyria Biomarkers for Disease Activity
Active, not recruiting
- Acute Intermittent Porphyria
- +2 more
-
Galveston, TexasUniversity of Texas Medical Branch
Jul 27, 2021
Dental Health, Diet, Inflammation and Biomarkers in Acute
Active, not recruiting
- Acute Intermittent Porphyria
-
Bodø, Nordland, NorwayNordlandssykehuset HF
Dec 3, 2020
Acute Intermittent Porphyria Trial in Sweden, United Kingdom, United States (givosiran (ALN-AS1), Sterile Normal Saline (0.9%
Completed
- Acute Intermittent Porphyria
- givosiran (ALN-AS1)
- Sterile Normal Saline (0.9% NaCl)
-
Birmingham, Alabama
- +5 more
Jun 13, 2018
Acute Intermittent Porphyria Trial in Galveston (recombinant human porphobilinogen deaminase (Porphozym))
Completed
- Acute Intermittent Porphyria
- recombinant human porphobilinogen deaminase (Porphozym)
-
Galveston, TexasUnivercity Texas Medical Branch
Mar 7, 2018
Anti-Psychotic, Management of Manifestations of Psychotic Disorders, Treatment of Schizophrenia Trial in Bloemfontein
Completed
- Anti-Psychotic
- +8 more
- Chlorpromazine Hydrochloride
-
Bloemfontein, Kampuslaan Suid, South AfricaFarmovs Parexel
Oct 12, 2017
Acute Intermittent Porphyria Trial in Pamplona, Madrid (rAAV2/5-PBGD vector dosage 1, rAAV2/5-PBGD vector dosage 2, rAAV2/5-PBGD
Completed
- Acute Intermittent Porphyria
- rAAV2/5-PBGD vector dosage 1
- +3 more
-
Pamplona, Navarra, Spain
- +1 more
Dec 17, 2014
Observational Study of Acute Intermittent Porphyria Patients
Completed
- Acute Intermittent Porphyria
-
Pamplona, Navarra, Spain
- +1 more
Mar 11, 2014