amyloid neuropathies, familial
Showing 1 - 4 of 4
Hereditary Transthyretin Amyloidosis
Recruiting
- Amyloidosis
- +6 more
-
Cleveland, OhioCleveland Clinic
Mar 11, 2022
TTR-mediated Amyloidosis, Amyloidosis, Hereditary, Amyloid Neuropathies, Familial Trial in Worldwide (patisiran (ALN-TTR02),
Completed
- TTR-mediated Amyloidosis
- +5 more
- patisiran (ALN-TTR02)
- Sterile Normal Saline (0.9% NaCl)
-
La Mesa, California
- +51 more
Nov 18, 2018
Amyloid Neuropathies, Familial Trial in Bordeaux (Systematic screening of TTR mutations)
Unknown status
- Amyloid Neuropathies, Familial
- Systematic screening of TTR mutations
-
Bordeaux, FranceReference center for neuromuscular diseases
Nov 29, 2018
Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC), Amyloidosis, Hereditary, Amyloid Neuropathies, Familial
Completed
- Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC)
- +5 more
- Revusiran (ALN-TTRSC)
- Sterile Normal Saline (0.9% NaCl)
-
Bakersfield, California
- +60 more
Jun 22, 2018