amyloid neuropathies, familial

Showing 1 - 4 of 4

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Hereditary Transthyretin Amyloidosis

Recruiting
  • Amyloidosis
  • +6 more
    • Cleveland, Ohio
      Cleveland Clinic
    Mar 11, 2022

    TTR-mediated Amyloidosis, Amyloidosis, Hereditary, Amyloid Neuropathies, Familial Trial in Worldwide (patisiran (ALN-TTR02),

    Completed
    • TTR-mediated Amyloidosis
    • +5 more
    • patisiran (ALN-TTR02)
    • Sterile Normal Saline (0.9% NaCl)
    • La Mesa, California
    • +51 more
    Nov 18, 2018

    Amyloid Neuropathies, Familial Trial in Bordeaux (Systematic screening of TTR mutations)

    Unknown status
    • Amyloid Neuropathies, Familial
    • Systematic screening of TTR mutations
    • Bordeaux, France
      Reference center for neuromuscular diseases
    Nov 29, 2018

    Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC), Amyloidosis, Hereditary, Amyloid Neuropathies, Familial

    Completed
    • Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC)
    • +5 more
    • Revusiran (ALN-TTRSC)
    • Sterile Normal Saline (0.9% NaCl)
    • Bakersfield, California
    • +60 more
    Jun 22, 2018