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batten disease

Showing 1 - 20 of 20
STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS
LAST UPDATED

Investigations of Juvenile Neuronal Ceroid Lipofuscinosis

Recruiting
  • Juvenile Neuronal Ceroid Lipofuscinosis (CLN3)
  • Batten Disease
    • Bethesda, Maryland
      National Institutes of Health Clinical Center
    Jan 31, 2023

    Adrenoleukodystrophy, Batten Disease, Mucopolysaccharidosis II Trial in Durham (DUOC-01)

    Recruiting
    • Adrenoleukodystrophy
    • +11 more
    • DUOC-01
    • Durham, North Carolina
      Duke University Medical Center
    Oct 24, 2022

    Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Adrenoleukodystrophy Trial in Denver, Valhalla, Salt Lake City (Human

    Completed
    • Mucopolysaccharidosis I
    • +15 more
    • Human Placental Derived Stem Cell
    • Denver, Colorado
    • +2 more
    Oct 24, 2022

    Neuronal Ceroid Lipofuscinosis, Batten's CLN6 Diseae

    Recruiting
    • Batten Disease
    • CLN6
    • Natural history
    • Columbus, Ohio
      Nationwide Children's Hospital
    Oct 20, 2022

    Jansky-Bielschowsky Disease, Batten Disease, Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 Trial in Worldwide (BMN 190,

    Completed
    Has Results
    • Jansky-Bielschowsky Disease
    • +4 more
    • BMN 190
    • Intracerebroventricular (ICV) access device
    • Columbus, Ohio
    • +3 more
    Jul 28, 2022

    CLN3, Batten Disease Trial in Columbus (AT-GTX-502)

    Active, not recruiting
    • CLN3
    • Batten Disease
    • AT-GTX-502
    • Columbus, Ohio
      Nationwide Children's Hospital
    Jul 18, 2022

    Batten Disease Trial in Houston (Miglustat 100Mg Oral Capsule)

    Recruiting
    • Batten Disease
    • Miglustat 100Mg Oral Capsule
    • Houston, Texas
      Texas Children Hospital
    May 17, 2022

    Natural History Study of Batten Disease

    Terminated
    • Batten Disease
    • +2 more
      • Rochester, New York
        University of Rochester Medical Center
      Apr 1, 2022

      CLN6 Batten Disease Subjects Following Gene Transfer

      Active, not recruiting
      • CLN6
      • Batten Disease
      • AT-GTX-501
      • Columbus, Ohio
        Nationwide Children's Hosptial
      Dec 17, 2021

      The Natural History of Metachromatic Leukodystrophy

      Recruiting
      • MLD
      • +26 more
      • Palliative Care
      • Hematopoetic Stem Cell Transplantation
      • Pittsburgh, Pennsylvania
        The Program for the Study of Neurodevelopment in Rare Disorders,
      Nov 2, 2021

      Neuronal Ceroid Lipofuscinosis, Batten Disease, CLN1 Disease Trial in Hamburg (Natural History)

      Recruiting
      • Neuronal Ceroid Lipofuscinosis
      • +14 more
      • Natural History
      • Hamburg, Germany
        University Medical Center Hamburg-Eppendorf
      Oct 22, 2021

      Children Diagnosed With CLN2 Disease

      Recruiting
      • Batten Disease
      • +2 more
      • CLN2 Treatment
      • Columbus, Ohio
        Nationwide Children's Hospital
      Aug 2, 2021

      Batten Disease, Late-Infantile Neuronal Ceroid Lipofuscinosis Trial in New York (AAVrh.10CUhCLN2 vector 9.0x10^11 genome copies,

      Completed
      • Batten Disease
      • Late-Infantile Neuronal Ceroid Lipofuscinosis
      • AAVrh.10CUhCLN2 vector 9.0x10^11 genome copies
      • AAVrh.10CUhCLN2 vector 2.85x10^11 genome copies
      • New York, New York
        Weill Cornell Medical College
      Jan 31, 2021

      Late Infantile Neuronal Ceroid Lipofuscinosis, Batten Disease Trial in New York (AAVrh.10CUCLN2)

      Completed
      • Late Infantile Neuronal Ceroid Lipofuscinosis
      • Batten Disease
      • AAVrh.10CUCLN2
      • New York, New York
        Weill Cornell Medical College
      Aug 28, 2020

      Late Infantile Neuronal Ceroid Lipofuscinosis

      Completed
      • Batten Disease
      • Late Infantile Neuronal Ceroid Lipofuscinosis
        • New York, New York
          Weill Cornell Medicine
        Jul 28, 2020

        Batten Disease, Late Infantile Neuronal Ceroid Lipofuscinosis Trial in New York (AAV2CUhCLN2 (3x10^12 particle units))

        Completed
        • Batten Disease
        • Late Infantile Neuronal Ceroid Lipofuscinosis
        • AAV2CUhCLN2 (3x10^12 particle units)
        • New York, New York
          New York Presbyterian Hospital - Weill Medical College of Cornel
        Jul 22, 2020

        Jansky-Bielschowsky Disease, Batten Disease, Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 Trial in Worldwide (BMN 190)

        Completed
        Has Results
        • Jansky-Bielschowsky Disease
        • +3 more
        • BMN 190
        • Columbus, Ohio
        • +4 more
        Mar 6, 2019

        Adrenoleukodystrophy, Metachromatic Leukodystrophy, Globoid Cell Leukodystrophy Trial in Minneapolis (Stem Cell Transplant,

        Completed
        Has Results
        • Adrenoleukodystrophy
        • +10 more
        • Stem Cell Transplant
        • Busulfan, Cyclophosphamide, Antithymocyte Globulin
        • Minneapolis, Minnesota
          Masonic Cancer Center, University of Minnesota
        Dec 3, 2017

        Genotype - Phenotype Correlations of LINCL

        Completed
        • Batten Disease
        • Late-Infantile Neuronal Ceroid Lipfuscinosis
          • (no location specified)
          Jul 28, 2016

          Collection of Cerebrospinal Fluid in Healthy Children

          Terminated
          • Late Infantile Neuronal Ceroid Lipofuscinosis
          • Batten Disease
          • Group 1
          • New York, New York
            Weill Cornell Medical College / New York Presbyterian Hospital
          May 3, 2016