cln2 disease

Showing 1 - 4 of 4

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Jansky-Bielschowsky Disease, Batten Disease, Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 Trial in Worldwide (BMN 190,

Completed
  • Jansky-Bielschowsky Disease
  • +4 more
  • BMN 190
  • Intracerebroventricular (ICV) access device
  • Columbus, Ohio
  • +3 more
Jul 28, 2022

Neuronal Ceroid Lipofuscinosis, Batten Disease, CLN1 Disease Trial in Hamburg (Natural History)

Recruiting
  • Neuronal Ceroid Lipofuscinosis
  • +14 more
  • Natural History
  • Hamburg, Germany
    University Medical Center Hamburg-Eppendorf
Oct 22, 2021

Jansky-Bielschowsky Disease, Batten Disease, Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 Trial in Worldwide (BMN 190)

Completed
  • Jansky-Bielschowsky Disease
  • +3 more
  • BMN 190
  • Columbus, Ohio
  • +4 more
Mar 6, 2019

CLN2 Disease Trial in Worldwide (BMN190, recombinant human tripeptidyl peptidase-1 (rhTPP1))

Approved for marketing
  • CLN2 Disease
  • BMN190, recombinant human tripeptidyl peptidase-1 (rhTPP1)
  • Orange, California
  • +4 more
Jul 21, 2017