cln2 disease
Showing 1 - 4 of 4
Jansky-Bielschowsky Disease, Batten Disease, Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 Trial in Worldwide (BMN 190,
Completed
- Jansky-Bielschowsky Disease
- +4 more
- BMN 190
- Intracerebroventricular (ICV) access device
-
Columbus, Ohio
- +3 more
Jul 28, 2022
Neuronal Ceroid Lipofuscinosis, Batten Disease, CLN1 Disease Trial in Hamburg (Natural History)
Recruiting
- Neuronal Ceroid Lipofuscinosis
- +14 more
- Natural History
-
Hamburg, GermanyUniversity Medical Center Hamburg-Eppendorf
Oct 22, 2021
Jansky-Bielschowsky Disease, Batten Disease, Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 Trial in Worldwide (BMN 190)
Completed
- Jansky-Bielschowsky Disease
- +3 more
- BMN 190
-
Columbus, Ohio
- +4 more
Mar 6, 2019
CLN2 Disease Trial in Worldwide (BMN190, recombinant human tripeptidyl peptidase-1 (rhTPP1))
Approved for marketing
- CLN2 Disease
- BMN190, recombinant human tripeptidyl peptidase-1 (rhTPP1)
-
Orange, California
- +4 more
Jul 21, 2017