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fabry disease

Showing 26 - 50 of 164
STUDY
CONDITIONS
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Fabry Disease Trial in Worldwide (PRX-102 (pegunigalsidase alfa), agalsidase beta)

Completed
  • Fabry Disease
  • PRX-102 (pegunigalsidase alfa)
  • agalsidase beta
  • Birmingham, Alabama
  • +28 more
Oct 12, 2022

Fabry Disease Who Received Lentiviral Gene Therapy in Study

Enrolling by invitation
  • Fabry Disease
  • Safety and Efficacy Assessments
  • Melbourne, Parkville VIC, Australia
  • +2 more
Oct 5, 2022

Early Detection of Fabry Disease

Not yet recruiting
  • Fabry Disease
  • No intervention
  • Erlangen, Germany
  • +2 more
Sep 30, 2022

Fabry Renal Disease Treatment Outcomes(Changes)in Fabry Renal

Recruiting
  • Fabry Disease
    • Minneapolis, Minnesota
    • +1 more
    Sep 16, 2022

    Fabry Disease Trial in Toronto (Cardiac MRI, ECG/Holter and Blood Biomarkers)

    Recruiting
    • Fabry Disease
    • Cardiac MRI, ECG/Holter and Blood Biomarkers
    • Toronto, Ontario, Canada
      University Health Network
    Aug 19, 2022

    Fabry Disease Trial in Worldwide (REPLAGAL)

    Recruiting
    • Fabry Disease
    • Calgary, Canada
    • +27 more
    Aug 8, 2022

    Study of Patients With Fabry Disease Treated With Migalastat

    Active, not recruiting
    • Fabry Disease
      • Angers, France
      • +14 more
      Jul 26, 2022

      related Benefit and Satisfaction in Fabry Patients. Insight in

      Active, not recruiting
      • Fabry Disease
      • Anderson Fabry Disease
      • Characterization of patients expectations and preferences regarding their treatment
      • Angers, France
      • +14 more
      Jul 26, 2022

      Cerebral Small Vessel Diseases, Cadasil, HTRA1-Related Autosomal Dominant Cerebral Angiopathy Trial in Taipei (MRI)

      Recruiting
      • Cerebral Small Vessel Diseases
      • +7 more
      • MRI
      • Taipei, Taiwan
        Department of Neurology, National Taiwan University Hospital
      Jul 24, 2022

      Fabry Disease and Their Infants During Pregnancy and

      Recruiting
      • Fabry Disease
      • Philadelphia, Pennsylvania
        Amicus Therapeutics, Inc. Pregnancy Registry
      Jul 18, 2022

      Trajectiories in Italian Patients With Fabry Disease

      Completed
      • Fabry Disease
      • FD patients
      • Arezzo, Italy
      • +6 more
      Jul 15, 2022

      Evaluation of HEArt invoLvement in Patients With FABRY Disease

      Recruiting
      • Rare Diseases
      • +3 more
        • Würzburg, Bayern, Germany
          Wuerzburg University Hospital
        Jul 6, 2022

        Fabry Disease Trial in Fairfax, La Rioja, Pergamino (Venglustat (GZ402671), Placebo)

        Recruiting
        • Fabry Disease
        • Venglustat (GZ402671)
        • Placebo
        • Fairfax, Virginia
        • +2 more
        Jun 14, 2022

        Fabry Exercise Intolerance Study

        Recruiting
        • Fabry Disease
        • Fabry Disease, Cardiac Variant
        • Intermittent cardiopulmonary exercise test
        • Incremental cardiopulmonary exercise test
        • Amsterdam, Netherlands
          Amsterdam UMC, location AMC
        Jun 9, 2022

        A Study of Migalastat in Fabry Disease

        Active, not recruiting
        • Fabry Disease
        • Manchester, United Kingdom
        • +1 more
        May 26, 2022

        ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn

        Enrolling by invitation
        • Acid Sphingomyelinase Deficiency
        • +13 more
        • Confirmatory Testing
        • Bronx, New York
        • +9 more
        May 9, 2022

        Fabry Disease, Alpha Galactosidase A Deficiency Trial in Austria, United Kingdom, United States (agalsidase beta)

        Recruiting
        • Fabry Disease
        • Alpha Galactosidase A Deficiency
        • agalsidase beta
        • Decatur, Georgia
        • +4 more
        May 4, 2022

        Fabry Disease Trial in Ciudadela (Agalsidase beta from Biosidus 1 mg/kg, Fabrazyme (agalsidase beta) 1 mg/kg)

        Active, not recruiting
        • Fabry Disease
        • Agalsidase beta from Biosidus 1 mg/kg
        • Fabrazyme (agalsidase beta) 1 mg/kg
        • Ciudadela, Buenos Aires, Argentina
          Sanatorio Nuestra Señora del Pilar
        Apr 22, 2022

        Fabry Disease Trial in Worldwide (Pegunigalsidase alfa)

        Completed
        • Fabry Disease
        • Pegunigalsidase alfa
        • Birmingham, Alabama
        • +20 more
        Mar 29, 2022

        Fabry Disease Trial in United States (4D-310)

        Recruiting
        • Fabry Disease
        • 4D-310
        • Birmingham, Alabama
        • +5 more
        Mar 24, 2022

        Fabry Disease Trial in Canada (No intervention)

        Recruiting
        • Fabry Disease
        • No intervention
        • Calgary, Alberta, Canada
        • +4 more
        Mar 9, 2022

        Fabry Patient's Experience Of PegunigaLsidasE Alfa Monthly

        Enrolling by invitation
        • Fabry Disease
        • Interview
        • Birmingham, Alabama
        • +11 more
        Mar 8, 2022

        Fabry Disease Trial in Worldwide (pegunigalsidase alfa)

        Enrolling by invitation
        • Fabry Disease
        • pegunigalsidase alfa
        • Birmingham, Alabama
        • +14 more
        Feb 14, 2022

        Fabry Disease Trial in Worldwide (pegunigalsidase alfa)

        Enrolling by invitation
        • Fabry Disease
        • pegunigalsidase alfa
        • Birmingham, Alabama
        • +28 more
        Feb 14, 2022

        Fabry Disease Trial in Worldwide (PRX-102 (pegunigalsidase alfa))

        Completed
        • Fabry Disease
        • PRX-102 (pegunigalsidase alfa)
        • Gainesville, Florida
        • +6 more
        Jan 20, 2022