hemophilia b
Showing 1 - 25 of 145
Development of Non-Invasive Prenatal Diagnosis for Single Gene
Not yet recruiting
- Invasive PreNatal Diagnosis in a Context of Family History of Single-gene Disorders, Including
- +14 more
- Blood sample
-
Paris, FranceHôpital Cochin, Maternité Port-Royal, service de Gynécologie obs
Nov 24, 2023
Hemophilia B Trial in Russian Federation (ANB-002, dose 1, ANB-002, dose 2)
Recruiting
- Hemophilia B
- ANB-002, dose 1
- ANB-002, dose 2
-
Chelyabinsk, Russian Federation
- +14 more
Nov 4, 2023
Hemophilia A, Hemophilia B, Blood Coagulation Disorders Trial in Seoul (TU7710, Normal saline)
Recruiting
- Hemophilia A
- +2 more
- TU7710
- Normal saline
-
Seoul, Korea, Republic ofSeoul National University Hospital
Sep 8, 2023
Patients With End Stage Liver Disease
Not yet recruiting
- Liver Cirrhosis
- +6 more
-
Palo Alto, CaliforniaStanford Hospital
Aug 23, 2023
Characterize Effectiveness and Safety of HEMGENIX® in Hemophilia
Not yet recruiting
- Hemophilia B
- HEMGENIX
- Factor IX (FIX)
- (no location specified)
Aug 23, 2023
Hemophilia B Trial (CSL222 (AAV5-hFIXco-Padua))
Not yet recruiting
- Hemophilia B
- CSL222 (AAV5-hFIXco-Padua)
- (no location specified)
Aug 14, 2023
Patterns of Hemophilia Care in Assiut Children Patients
Not yet recruiting
- Hemophilia A
- Hemophilia B
- (no location specified)
Jul 29, 2023
Lower Extremity Muscles in Patients With Hemophilia
Not yet recruiting
- Hemophilia
- +2 more
-
Gaziantep, Şahinbey, TurkeyHasan Kalyoncu University
Jul 31, 2023
Male Hemophilia B Previously Treated With Etranacogene
Not yet recruiting
- Hemophilia B
- AAV5-hFIXco-Padua
- (no location specified)
Jul 31, 2023
Liver Biopsy Following Gene Therapy For Hemophilia
Not yet recruiting
- Hemophilia A
- Hemophilia B
- Liver Biopsy
-
Memphis, TennesseeSt. Jude Children's Research Hospital
Jun 27, 2023
Hemophilia B Trial in Beijing (Sodium valproate extended-release tablets)
Recruiting
- Hemophilia B
- Sodium valproate extended-release tablets
-
Beijing, ChinaPLA General Hospital
Jun 17, 2023
Reliability and Validity of the Turkish Version of the PedHAL
Not yet recruiting
- Hemophilia
- +2 more
-
Gaziantep, Şahinbey, TurkeyHasan Kalyoncu University
Jun 2, 2023
Hemophilia A, Hemophilia B Trial in Istanbul (Closed Chain Exercise Group, Proprioceptive Exercise Group)
Not yet recruiting
- Hemophilia A
- Hemophilia B
- Closed Chain Exercise Group
- Proprioceptive Exercise Group
-
Istanbul, Turkeyİstanbul University-Cerrahpaşa
May 18, 2023
Hemophilia A, Hemophilia B Trial in Worldwide (Haemophilia Early Arthropathy Detection with Ultrasound (HEAD-US), Haemophilia
Not yet recruiting
- Hemophilia A
- Hemophilia B
- Haemophilia Early Arthropathy Detection with Ultrasound (HEAD-US)
- Haemophilia Joint Health Score (HJHS)
-
Sofia, Bulgaria
- +55 more
May 3, 2023
Vitamin K Antagonist Versus Direct Oral Anticoagulant Treatments
Completed
- Hemophilia A
- +2 more
- Vitamin K Antagonist - Drug
-
Brest, France
- +5 more
Apr 6, 2023
Hemophilia B With Inhibitor, Hemophilia B Trial (SerpinPC)
Not yet recruiting
- Hemophilia B With Inhibitor
- Hemophilia B
- (no location specified)
Mar 16, 2023
Hemophilia B Trial in Worldwide (PF-06838435 (formerly SPK-9001))
Recruiting
- Hemophilia B
- PF-06838435 (formerly SPK-9001)
-
Sacramento, California
- +24 more
Feb 2, 2023
ATHN 8: Previously Untreated Patients (PUPs) Matter Study
Completed
- Hemophilia
- +7 more
-
Phoenix, Arizona
- +26 more
Jan 30, 2023
(LTFU) of Subjects Who Received SB-318, SB-913, or SB-FIX
Active, not recruiting
- Hemophilia B
- +2 more
- SB-318
- +2 more
-
Oakland, California
- +4 more
Jan 30, 2023
Baby Detect : Genomic Newborn Screening
Recruiting
- Congenital Adrenal Hyperplasia
- +126 more
-
Liege, Wallonia, BelgiumCRMN, Hôpital La Citadelle
Jan 24, 2023
Hemophilia A, Hemophilia B Trial in Korea, Republic of, South Africa, Taiwan (marstacimab)
Recruiting
- Hemophilia A
- Hemophilia B
-
Seoul, Seoul-teukbyeolsi [seoul], Korea, Republic of
- +3 more
Jan 18, 2023
Study of AAV5-hFIX in Severe or Moderately Severe Haemophilia B
Active, not recruiting
- Hemophilia B
- AAV5-hFIX
-
Berlin, Germany
- +5 more
Jan 17, 2023
Hemophilia B, Hemophilia A Trial in Worldwide (Standard of Care FIX Replacement therapy, Standard of Care FVIII Replacement
Recruiting
- Hemophilia B
- Hemophilia A
- Standard of Care FIX Replacement therapy
- Standard of Care FVIII Replacement therapy
-
Palo Alto, California
- +77 more
Dec 29, 2022