hemophilia b

Showing 1 - 25 of 145

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Development of Non-Invasive Prenatal Diagnosis for Single Gene

Not yet recruiting
  • Invasive PreNatal Diagnosis in a Context of Family History of Single-gene Disorders, Including
  • +14 more
  • Blood sample
  • Paris, France
    Hôpital Cochin, Maternité Port-Royal, service de Gynécologie obs
Nov 24, 2023

Hemophilia B Trial in Russian Federation (ANB-002, dose 1, ANB-002, dose 2)

Recruiting
  • Hemophilia B
  • ANB-002, dose 1
  • ANB-002, dose 2
  • Chelyabinsk, Russian Federation
  • +14 more
Nov 4, 2023

Hemophilia A, Hemophilia B, Blood Coagulation Disorders Trial in Seoul (TU7710, Normal saline)

Recruiting
  • Hemophilia A
  • +2 more
  • Seoul, Korea, Republic of
    Seoul National University Hospital
Sep 8, 2023

Patients With End Stage Liver Disease

Not yet recruiting
  • Liver Cirrhosis
  • +6 more
    • Palo Alto, California
      Stanford Hospital
    Aug 23, 2023

    Characterize Effectiveness and Safety of HEMGENIX® in Hemophilia

    Not yet recruiting
    • Hemophilia B
    • HEMGENIX
    • Factor IX (FIX)
    • (no location specified)
    Aug 23, 2023

    Hemophilia B Trial (CSL222 (AAV5-hFIXco-Padua))

    Not yet recruiting
    • Hemophilia B
    • CSL222 (AAV5-hFIXco-Padua)
    • (no location specified)
    Aug 14, 2023

    Patterns of Hemophilia Care in Assiut Children Patients

    Not yet recruiting
    • Hemophilia A
    • Hemophilia B
      • (no location specified)
      Jul 29, 2023

      Lower Extremity Muscles in Patients With Hemophilia

      Not yet recruiting
      • Hemophilia
      • +2 more
        • Gaziantep, Şahinbey, Turkey
          Hasan Kalyoncu University
        Jul 31, 2023

        Male Hemophilia B Previously Treated With Etranacogene

        Not yet recruiting
        • Hemophilia B
        • AAV5-hFIXco-Padua
        • (no location specified)
        Jul 31, 2023

        Liver Biopsy Following Gene Therapy For Hemophilia

        Not yet recruiting
        • Hemophilia A
        • Hemophilia B
        • Liver Biopsy
        • Memphis, Tennessee
          St. Jude Children's Research Hospital
        Jun 27, 2023

        Hemophilia B Trial in Beijing (Sodium valproate extended-release tablets)

        Recruiting
        • Hemophilia B
        • Sodium valproate extended-release tablets
        • Beijing, China
          PLA General Hospital
        Jun 17, 2023

        Reliability and Validity of the Turkish Version of the PedHAL

        Not yet recruiting
        • Hemophilia
        • +2 more
          • Gaziantep, Şahinbey, Turkey
            Hasan Kalyoncu University
          Jun 2, 2023

          Hemophilia A, Hemophilia B Trial in Istanbul (Closed Chain Exercise Group, Proprioceptive Exercise Group)

          Not yet recruiting
          • Hemophilia A
          • Hemophilia B
          • Closed Chain Exercise Group
          • Proprioceptive Exercise Group
          • Istanbul, Turkey
            İstanbul University-Cerrahpaşa
          May 18, 2023

          Hemophilia A, Hemophilia B Trial in Worldwide (Haemophilia Early Arthropathy Detection with Ultrasound (HEAD-US), Haemophilia

          Not yet recruiting
          • Hemophilia A
          • Hemophilia B
          • Haemophilia Early Arthropathy Detection with Ultrasound (HEAD-US)
          • Haemophilia Joint Health Score (HJHS)
          • Sofia, Bulgaria
          • +55 more
          May 3, 2023

          Vitamin K Antagonist Versus Direct Oral Anticoagulant Treatments

          Completed
          • Hemophilia A
          • +2 more
          • Vitamin K Antagonist - Drug
          • Brest, France
          • +5 more
          Apr 6, 2023

          Hemophilia B With Inhibitor, Hemophilia B Trial (SerpinPC)

          Not yet recruiting
          • Hemophilia B With Inhibitor
          • Hemophilia B
          • (no location specified)
          Mar 16, 2023

          Hemophilia A, Hemophilia B Trial (SerpinPC)

          Not yet recruiting
          • Hemophilia A
          • Hemophilia B
          • (no location specified)
          Mar 16, 2023

          Hemophilia B Trial (BBM-H901)

          Not yet recruiting
          • Hemophilia B
          • (no location specified)
          Feb 6, 2023

          Hemophilia B Trial in Worldwide (PF-06838435 (formerly SPK-9001))

          Recruiting
          • Hemophilia B
          • PF-06838435 (formerly SPK-9001)
          • Sacramento, California
          • +24 more
          Feb 2, 2023

          ATHN 8: Previously Untreated Patients (PUPs) Matter Study

          Completed
          • Hemophilia
          • +7 more
            • Phoenix, Arizona
            • +26 more
            Jan 30, 2023

            (LTFU) of Subjects Who Received SB-318, SB-913, or SB-FIX

            Active, not recruiting
            • Hemophilia B
            • +2 more
            • SB-318
            • +2 more
            • Oakland, California
            • +4 more
            Jan 30, 2023

            Baby Detect : Genomic Newborn Screening

            Recruiting
            • Congenital Adrenal Hyperplasia
            • +126 more
              • Liege, Wallonia, Belgium
                CRMN, Hôpital La Citadelle
              Jan 24, 2023

              Hemophilia A, Hemophilia B Trial in Korea, Republic of, South Africa, Taiwan (marstacimab)

              Recruiting
              • Hemophilia A
              • Hemophilia B
              • Seoul, Seoul-teukbyeolsi [seoul], Korea, Republic of
              • +3 more
              Jan 18, 2023

              Study of AAV5-hFIX in Severe or Moderately Severe Haemophilia B

              Active, not recruiting
              • Hemophilia B
              • AAV5-hFIX
              • Berlin, Germany
              • +5 more
              Jan 17, 2023

              Hemophilia B, Hemophilia A Trial in Worldwide (Standard of Care FIX Replacement therapy, Standard of Care FVIII Replacement

              Recruiting
              • Hemophilia B
              • Hemophilia A
              • Standard of Care FIX Replacement therapy
              • Standard of Care FVIII Replacement therapy
              • Palo Alto, California
              • +77 more
              Dec 29, 2022