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hurler syndrome

Showing 1 - 14 of 14
STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS
LAST UPDATED

Mucopolysaccharidosis Type I (MPS I), Hurler Syndrome, Hurler-Scheie Syndrome Trial in Orange, Philadelphia, Porto Alegre

Active, not recruiting
  • Mucopolysaccharidosis Type I (MPS I)
  • +2 more
  • RGX-111
  • Orange, California
  • +3 more
Jan 9, 2023

Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD

Recruiting
  • Mucopolysaccharidosis Disorders
  • +28 more
  • Stem Cell Transplantation
  • +7 more
  • Minneapolis, Minnesota
    Masonic Cancer Center, University of Minnesota
Nov 1, 2022

Bone Marrow Failure Syndrome, Thalassemia, Sickle Cell Disease Trial in Gainesville (Thiotepa--single daily dose,

Recruiting
  • Bone Marrow Failure Syndrome
  • +15 more
  • Thiotepa--single daily dose
  • Thiotepa--escalated dose
  • Gainesville, Florida
    UF Health Shands Children's Hospital
Jul 8, 2021

Hurler Syndrome, Inherited Metabolic Disorder, Lysosomal Storage Disorder Trial in Los Angeles, Palo Alto (rivogenlecleucel,

No longer available
  • Hurler Syndrome
  • +4 more
  • Los Angeles, California
  • +1 more
Oct 1, 2020

Hurler Syndrome Trial in Minneapolis (Laronidase)

Completed
Has Results
  • Hurler Syndrome
  • Minneapolis, Minnesota
    Masonic Cancer Center, University of Minnesota
Mar 6, 2020

Hurler Syndrome, Fanconi Anemia, Glanzmann Thrombasthenia Trial in Atlanta (Abatacept)

Completed
  • Hurler Syndrome
  • +14 more
  • Atlanta, Georgia
    Children's Healthcare of Atlanta
Dec 20, 2019

Neurobehavioral Phenotypes in MPS III

Completed
  • Sanfilippo Syndrome Type A
  • +2 more
    • Minneapolis, Minnesota
      University of Minnesota
    Oct 30, 2019

    Mucopolysaccharidosis I, Hurler Syndrome Trial in Minneapolis (Stem Cell Transplant, Laronidase ERT)

    Completed
    Has Results
    • Mucopolysaccharidosis I
    • Hurler Syndrome
    • Stem Cell Transplant
    • Laronidase ERT
    • Minneapolis, Minnesota
      Masonic Cancer Center, University of Minnesota
    Jul 10, 2019

    Hurler Syndrome, Cerebral Palsy, Juvenile Rheumatoid Arthritis Trial in Dallas (Growth Hormone, Whole body Protein turnover,

    Withdrawn
    • Hurler Syndrome
    • +4 more
    • Growth Hormone
    • +2 more
    • Dallas, Texas
      Children's Medical Center of Dallas
    Dec 12, 2018

    Hurler Syndrome Trial in Minneapolis (IRT Laronidase)

    Completed
    • Hurler Syndrome
    • IRT Laronidase
    • Minneapolis, Minnesota
      University of Minnesota, Fairview
    Nov 30, 2018

    Laronidase Enzyme Replacement Therapy With Hematopoietic Stem

    Terminated
    • Mucopolysaccharidosis Type IH
    • +2 more
    • Minneapolis, Minnesota
      Masonic Cancer Center, University of Minnesota
    Sep 25, 2018

    Mucopolysaccharidosis, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Campath-1H, Cyclophosphamide, Busulfan)

    Completed
    Has Results
    • Mucopolysaccharidosis
    • +12 more
    • Minneapolis, Minnesota
      Masonic Cancer Center, University of Minnesota
    Jan 9, 2018

    Mucopolysaccharidosis I, Hurler Syndrome, Hurler-Scheie Syndrome Trial in Worldwide (Aldurazyme (Recombinant Human

    Completed
    Has Results
    • Mucopolysaccharidosis I
    • +3 more
    • Aldurazyme (Recombinant Human Alpha-L-Iduronidase)
    • Lyon, France
    • +3 more
    Mar 17, 2015

    Mucopolysaccharidosis I, Hurler Syndrome, Hurler-Scheie Syndrome Trial in Osaka, Tokyo (Aldurazyme (Recombinant Human

    Completed
    Has Results
    • Mucopolysaccharidosis I
    • +3 more
    • Aldurazyme (Recombinant Human Alpha-L-Iduronidase)
    • Osaka, Japan
    • +1 more
    Feb 4, 2014