morquio a syndrome
Showing 1 - 11 of 11
Mucopolysaccharidosis IV Type A, Morquio A Syndrome, MPS IVA Trial in Worldwide (VimizimĀ® (elosulfase alfa))
Active, not recruiting
- Mucopolysaccharidosis IV Type A
- +2 more
- VimizimĀ® (elosulfase alfa)
-
Phoenix, Arizona
- +78 more
Dec 23, 2022
Non-invasive Functional Assessment and Pathogenesis of Morquio A
Recruiting
- Mucopolysaccharidosis IV Type A
- +2 more
- Imaging, gait analysis, growth, joint test, hearing test, questionnaire, etc.
-
Wilmington, DelawareNemours Children's Health, Delaware Valley
Mar 9, 2022
Mucopolysaccharidosis IV A, Morquio A Syndrome, MPS IVA Trial in Worldwide (BMN 110 - Weekly, BMN 110 - Every Other Week)
Completed
- Mucopolysaccharidosis IV A
- +2 more
- BMN 110 - Weekly
- BMN 110 - Every Other Week
-
Phoenix, Arizona
- +42 more
Jul 19, 2021
Mucopolysaccharidosis IV A, Mucopolysaccharidosis VI, Mucopolysaccharidoses Trial in Porto Alegre (Losartan, Placebo)
Recruiting
- Mucopolysaccharidosis IV A
- +8 more
- Losartan
- Placebo
-
Porto Alegre, Rio Grande Do Sul, BrazilHospital de Clinicas de Porto Alegre
Oct 2, 2020
Psychological Concomitants of Morquio A Syndrome - Longitudinal
Completed
- Morquio A Syndrome
- Mucopolysaccharidosis IV A
-
Decatur, GeorgiaEmory University
Apr 9, 2018
Mucopolysaccharidosis IVA, Morquio A Syndrome, MPS IVA Trial in Worldwide (BMN 110)
Completed
- Mucopolysaccharidosis IVA
- +2 more
- BMN 110
-
Oakland, California
- +4 more
Jul 12, 2017
Mucopolysaccharidosis IVA, Morquio A Syndrome, MPS IVA Trial in Worldwide (BMN 110)
Terminated
- Mucopolysaccharidosis IVA
- +2 more
- BMN 110
-
Oakland, California
- +10 more
Dec 24, 2015
Mucopolysaccharidosis IVA, Morquio A Syndrome, MPS IVA Trial in Germany, United Kingdom, United States (BMN 110)
Terminated
- Mucopolysaccharidosis IVA
- +2 more
- BMN 110
-
Oakland, California
- +6 more
Dec 8, 2015
Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)
Terminated
- MPS IV A
- +2 more
-
Oakland, California
- +14 more
Dec 5, 2014
Mucopolysaccharidosis IVA, Morquio A Syndrome, MPS IVA Trial in Puerto Rico, United States (BMN 110)
Approved for marketing
- Mucopolysaccharidosis IVA
- +2 more
- BMN 110
-
Birmingham, Alabama
- +24 more
Mar 31, 2014