morquio a syndrome

Showing 1 - 11 of 11

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Mucopolysaccharidosis IV Type A, Morquio A Syndrome, MPS IVA Trial in Worldwide (VimizimĀ® (elosulfase alfa))

Active, not recruiting
  • Mucopolysaccharidosis IV Type A
  • +2 more
  • VimizimĀ® (elosulfase alfa)
  • Phoenix, Arizona
  • +78 more
Dec 23, 2022

Non-invasive Functional Assessment and Pathogenesis of Morquio A

Recruiting
  • Mucopolysaccharidosis IV Type A
  • +2 more
  • Imaging, gait analysis, growth, joint test, hearing test, questionnaire, etc.
  • Wilmington, Delaware
    Nemours Children's Health, Delaware Valley
Mar 9, 2022

Mucopolysaccharidosis IV A, Morquio A Syndrome, MPS IVA Trial in Worldwide (BMN 110 - Weekly, BMN 110 - Every Other Week)

Completed
  • Mucopolysaccharidosis IV A
  • +2 more
  • BMN 110 - Weekly
  • BMN 110 - Every Other Week
  • Phoenix, Arizona
  • +42 more
Jul 19, 2021

Mucopolysaccharidosis IV A, Mucopolysaccharidosis VI, Mucopolysaccharidoses Trial in Porto Alegre (Losartan, Placebo)

Recruiting
  • Mucopolysaccharidosis IV A
  • +8 more
  • Porto Alegre, Rio Grande Do Sul, Brazil
    Hospital de Clinicas de Porto Alegre
Oct 2, 2020

Psychological Concomitants of Morquio A Syndrome - Longitudinal

Completed
  • Morquio A Syndrome
  • Mucopolysaccharidosis IV A
    • Decatur, Georgia
      Emory University
    Apr 9, 2018

    Mucopolysaccharidosis IVA, Morquio A Syndrome, MPS IVA Trial in Worldwide (BMN 110)

    Completed
    • Mucopolysaccharidosis IVA
    • +2 more
    • BMN 110
    • Oakland, California
    • +4 more
    Jul 12, 2017

    Mucopolysaccharidosis IVA, Morquio A Syndrome, MPS IVA Trial in Worldwide (BMN 110)

    Terminated
    • Mucopolysaccharidosis IVA
    • +2 more
    • BMN 110
    • Oakland, California
    • +10 more
    Dec 24, 2015

    Mucopolysaccharidosis IVA, Morquio A Syndrome, MPS IVA Trial in Germany, United Kingdom, United States (BMN 110)

    Terminated
    • Mucopolysaccharidosis IVA
    • +2 more
    • BMN 110
    • Oakland, California
    • +6 more
    Dec 8, 2015

    MPS IV A, Mucopolysaccharidosis IVA, Morquio A Syndrome Trial in United Kingdom (BMN 110)

    Terminated
    • MPS IV A
    • +2 more
    • BMN 110
    • Birmingham, United Kingdom
    • +3 more
    Aug 28, 2015

    Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)

    Terminated
    • MPS IV A
    • +2 more
      • Oakland, California
      • +14 more
      Dec 5, 2014

      Mucopolysaccharidosis IVA, Morquio A Syndrome, MPS IVA Trial in Puerto Rico, United States (BMN 110)

      Approved for marketing
      • Mucopolysaccharidosis IVA
      • +2 more
      • BMN 110
      • Birmingham, Alabama
      • +24 more
      Mar 31, 2014