mucopolysaccharidosis
Showing 1 - 7 of 7
Mucopolysaccharidosis Trial in Gaziantep (Enzyme Replacement Agent)
Completed
- Mucopolysaccharidosis
- Enzyme Replacement Agent
-
Gaziantep, None Selected, TurkeySerkan Usgu
Aug 7, 2021
Mucopolysaccharidosis, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Campath-1H, Cyclophosphamide, Busulfan)
Completed
- Mucopolysaccharidosis
- +12 more
- Campath-1H
- +5 more
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Jan 9, 2018
Inherited Metabolic Diseases, Lysosomal Storage Disorders, Peroxisomal Storage Diseases Trial in Los Angeles, New York, Durham
Terminated
- Inherited Metabolic Diseases
- +4 more
- ALD-101
-
Los Angeles, California
- +2 more
Jul 7, 2014
Intraocular Pressure in MPS by Use of Ocular Response Analyzer.
Unknown status
- Mucopolysaccharidosis
- Fabry Disease
-
Mainz, GermanyDepartment of Ophthalmology, University Medical Center, Johannes
Feb 28, 2013
Mucopolysaccharidosis Trial in Teharn (Conditioning regimen, Graft-versus-host disease (GVHD) prophylaxis, Stem Cell
Unknown status
- Mucopolysaccharidosis
- Conditioning regimen
- +2 more
-
Teharn, Tehran, Iran, Islamic Republic ofHematology-Oncology & SCT Research Center
May 31, 2012