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mucopolysaccharidosis i

Showing 1 - 25 of 32
STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS
LAST UPDATED

Long Term Follow-Up for RGX-111

Enrolling by invitation
  • Mucopolysaccharidosis I
  • No Intervention
  • Orange, California
  • +2 more
Oct 25, 2023

MPS (RaDiCo Cohort) (RaDiCo-MPS)

Recruiting
  • Mucopolysaccharidosis I
  • +7 more
    • Angers, France
    • +22 more
    Sep 12, 2023

    (LTFU) of Subjects Who Received SB-318, SB-913, or SB-FIX

    Active, not recruiting
    • Hemophilia B
    • +2 more
    • SB-318
    • +2 more
    • Oakland, California
    • +4 more
    Jan 30, 2023

    Baby Detect : Genomic Newborn Screening

    Recruiting
    • Congenital Adrenal Hyperplasia
    • +126 more
      • Liege, Wallonia, Belgium
        CRMN, Hôpital La Citadelle
      Jan 24, 2023

      Mucopolysaccharidosis I Trial in Wuhan (Laronidase)

      Recruiting
      • Mucopolysaccharidosis I
      • Wuhan, China
        Investigational Site Number :1560001
      Jan 15, 2023

      Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis IV A Trial in San Francisco (There is no intervention)

      Recruiting
      • Mucopolysaccharidosis I
      • +7 more
      • There is no intervention
      • San Francisco, California
        University of California San Francisco
      Nov 9, 2022

      Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Adrenoleukodystrophy Trial in Denver, Valhalla, Salt Lake City (Human

      Completed
      • Mucopolysaccharidosis I
      • +15 more
      • Human Placental Derived Stem Cell
      • Denver, Colorado
      • +2 more
      Oct 24, 2022

      Mucopolysaccharidosis I Trial in Brazil, Japan, United States (JR-171)

      Active, not recruiting
      • Mucopolysaccharidosis I
      • Oakland, California
      • +4 more
      Aug 16, 2022

      Mucopolysaccharidosis I Trial in Brazil, Japan, United States (JR-171)

      Completed
      • Mucopolysaccharidosis I
      • Oakland, California
      • +5 more
      Aug 16, 2022

      Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis VI Trial in Torrance (Adalimumab Injection [Humira],

      Recruiting
      • Mucopolysaccharidosis I
      • +2 more
      • Adalimumab Injection [Humira]
      • Saline Solution for Injection
      • Torrance, California
        The Lundquist Institute at Harbor-UCLA Medical Center
      Aug 9, 2022

      Mucopolysaccharidosis I, Hurler's Syndrome, Hurler-Scheie Syndrome Trial in Rome (Aldurazyme (laronidase))

      Recruiting
      • Mucopolysaccharidosis I
      • +3 more
      • Aldurazyme (laronidase)
      • Rome, Italy
        Dipartimento di Scienze Pediatriche Medico - Chirurgiche e Neuro
      Mar 28, 2022

      Patients Who Have Received Gene Therapy Or Gene Marked Products

      Recruiting
      • Severe Combined Immunodeficiency
      • +4 more
      • Venipuncture
      • Memphis, Tennessee
        St. Jude Children's Research Hospital
      Dec 10, 2021

      Mucopolysaccharidosis I, Cognitive Decline Trial in Torrance (Intrathecal recombinant human alpha iduronidase)

      Terminated
      • Mucopolysaccharidosis I
      • Cognitive Decline
      • Intrathecal recombinant human alpha iduronidase
      • Torrance, California
        Los Angeles Biomedical Research Institute at Harbor-UCLA Medical
      Oct 5, 2020

      Mucopolysaccharidosis I, Hurler Syndrome Trial in Minneapolis (Stem Cell Transplant, Laronidase ERT)

      Completed
      Has Results
      • Mucopolysaccharidosis I
      • Hurler Syndrome
      • Stem Cell Transplant
      • Laronidase ERT
      • Minneapolis, Minnesota
        Masonic Cancer Center, University of Minnesota
      Jul 10, 2019

      Mucopolysaccharidosis I Trial (AGT-181)

      Completed
      • Mucopolysaccharidosis I
      • (no location specified)
      Sep 21, 2018

      Mucopolysaccharidosis I Trial in Porto Alegre (AGT-181)

      Completed
      • Mucopolysaccharidosis I
      • Porto Alegre, RS, Brazil
        HCPA - Hospital das Clinicas de Porto Alegre
      Sep 16, 2018

      Mucopolysaccharidosis I Trial in Porto Alegre (AGT-181)

      Completed
      • Mucopolysaccharidosis I
      • Porto Alegre, RS, Brazil
        HCPA - Hospital das Clinicas de Porto Alegre
      Sep 16, 2018

      Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis VI Trial in Minneapolis (Somatropin (DNA origin))

      Terminated
      Has Results
      • Mucopolysaccharidosis I
      • +2 more
      • Somatropin (DNA origin)
      • Minneapolis, Minnesota
        University of Minnesota
      Aug 6, 2018

      Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Mannosidosis Trial in Minneapolis (Stem Cell Transplant, Busulfan,

      Completed
      Has Results
      • Mucopolysaccharidosis I
      • +3 more
      • Stem Cell Transplant
      • Busulfan, Cyclophosphamide, ATG
      • Minneapolis, Minnesota
        Masonic Cancer Center, University of Minnesota
      Dec 3, 2017

      Mucopolysaccharidosis I Trial in United States (AGT-181 (HIRMAb-IDUA))

      Unknown status
      • Mucopolysaccharidosis I
      • AGT-181 (HIRMAb-IDUA)
      • Oakland, California
      • +5 more
      Mar 3, 2017

      Cognitive Decline, Mucopolysaccharidosis I, Hurler-Scheie Syndrome Trial in Oakland, Torrance, Minneapolis (laronidase)

      Completed
      • Cognitive Decline
      • +4 more
      • Oakland, California
      • +2 more
      Jan 22, 2016

      Mucopolysaccharidosis I, Hurlers Syndrome, Hurler-Scheie Syndrome Trial in Canada, Germany, United States (rhIDU (recombinant

      Completed
      Has Results
      • Mucopolysaccharidosis I
      • +2 more
      • rhIDU (recombinant human-Alpha-L-Iduronidase)
      • Placebo
      • New York, New York
      • +3 more
      Mar 19, 2015

      Mucopolysaccharidosis I, Hurler's Syndrome, Hurler-Scheie Syndrome Trial in Worldwide (Aldurazyme, )

      Completed
      Has Results
      • Mucopolysaccharidosis I
      • +3 more
      • Aldurazyme
      • placebo
      • Mobile, Alabama
      • +24 more
      Mar 17, 2015

      Mucopolysaccharidosis I, Hurler's Syndrome, Hurler-Scheie Syndrome Trial in Brazil, Canada (Aldurazyme (Recombinant Human

      Completed
      Has Results
      • Mucopolysaccharidosis I
      • +3 more
      • Aldurazyme (Recombinant Human Alpha-L-Iduronidase)
      • Florianopolis, Santa Catarina, Brazil
      • +4 more
      Mar 17, 2015

      Mucopolysaccharidosis I, Hurler Syndrome, Hurler-Scheie Syndrome Trial in Worldwide (Aldurazyme (Recombinant Human

      Completed
      Has Results
      • Mucopolysaccharidosis I
      • +3 more
      • Aldurazyme (Recombinant Human Alpha-L-Iduronidase)
      • Lyon, France
      • +3 more
      Mar 17, 2015