Condition

OTC Deficiency (2)

Aminoacidopathy (1)

Inborn Errors of Metabolism (1)

Maple Syrup Urine Disease (1)

Methylmalonicacidemia (1)

Patient Reported Outcome Measurements (1)

Phenylketonurias (1)

Urea Cycle Disorder (1)

Overall Status

Completed (1)

Recruiting (1)

Phase

phase 3 (1)

Sponsor

Ultragenyx Pharmaceutical Inc (1)

University Children's Hospital, Zurich (1)

Collaborator

Intervention

dtx301 (1)

oral corticosteroids (1)

placebo (1)

placebo for oral corticosteroids (1)

sodium acetate (1)

survey (1)

Study Documents

Intervention Type

other (2)

drug (1)

genetic (1)

Funder Type

Industry (1)

Other (1)

Study Type

Interventional (1)

Observational (1)

otc deficiency

Showing 1 - 2 of 2

Trials per page:

STUDY

CONDITIONS

INTERVENTIONS

LOCATIONS

LAST UPDATED

OTC Deficiency Trial in Worldwide (genetic, other, drug)

Recruiting

OTC Deficiency

DTX301
+4 more

Aurora, Colorado
+19 more

Jul 29, 2022

Measurements in Inborn Errors of Metabolism

Completed

Inborn Errors of Metabolism
+7 more

Survey

Zurich, Switzerland

University Children's Hospital Zurich

Nov 3, 2020