paroxysmal nocturnal hemoglobinuria (pnh)

Showing 1 - 21 of 21

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial (MY008211A tablets)

Not yet recruiting
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • MY008211A tablets
  • (no location specified)
Nov 17, 2023

Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Brisbane (ADX-038, Placebo)

Not yet recruiting
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • Brisbane, Queensland, Australia
    Nucleus Network Brisbane
May 17, 2023

Severe Aplastic Anemia (SAA), Hypo-Plastic Myelodysplastic Syndrome (MDS), Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial run

Recruiting
  • Severe Aplastic Anemia (SAA)
  • +2 more
  • Bethesda, Maryland
    National Institutes of Health Clinical Center
Jan 28, 2023

Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Worldwide (LNP023, Eculizumab, Ravulizumab)

Active, not recruiting
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • Duarte, California
  • +39 more
Jan 13, 2023

Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Worldwide (BCX9930 monotherapy, Placebo)

Active, not recruiting
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • BCX9930 monotherapy
  • Placebo
  • Ampang, Malaysia
  • +3 more
Dec 15, 2022

Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Worldwide (BCX9930, Eculizumab, Ravulizumab)

Active, not recruiting
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • Paris, France
  • +6 more
Dec 15, 2022

Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Worldwide (Iptacopan (LNP023))

Active, not recruiting
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • Iptacopan (LNP023)
  • Tianjin, Tianjin, China
  • +11 more
Nov 21, 2022

Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Italy, United Kingdom, United States (Danicopan, Eculizumab)

Active, not recruiting
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • Baltimore, Maryland
  • +4 more
Aug 15, 2022

Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Worldwide (Ravulizumab, Eculizumab)

Completed
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • Ravulizumab
  • Eculizumab
  • Duarte, California
  • +48 more
Jul 14, 2022

Paroxysmal Nocturnal Hemoglobinuria (PNH), Paroxysmal Hemoglobinuria Trial in Worldwide (Pegcetacoplan)

Recruiting
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • Paroxysmal Hemoglobinuria
  • Atlanta, Georgia
  • +9 more
Jul 18, 2022

Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Worldwide (Danicopan)

Completed
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • Florence, Italy
  • +4 more
May 31, 2022

Paroxysmal Nocturnal Hemoglobinuria (PNH), CD55-deficient Protein-losing Enteropathy (PLE), CD59 Deficiency Trial (Pozelimab)

Available
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • +2 more
  • (no location specified)
Jan 28, 2022

Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Worldwide (REGN3918)

Completed
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • Sha Tin, Hong Kong
  • +11 more
Jul 13, 2021

Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in United States (Pegcetacoplan)

No longer available
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • Jacksonville, Florida
  • +3 more
Jun 2, 2021

Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in United States (Pegcetacoplan)

Completed
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • Los Angeles, California
  • +6 more
Dec 14, 2020

Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Almaty, Vilnius, Colombo (rVA576, Standard of care (SOC))

Completed
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • Almaty, Microdistrict Kalkaman, Kazakhstan
  • +2 more
Nov 3, 2020

Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Barcelona, Leeds, London (ALN-CC5, Sterile Normal Saline (0.9% NaCl))

Completed
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • ALN-CC5
  • Sterile Normal Saline (0.9% NaCl)
  • Barcelona, Spain
  • +3 more
Mar 17, 2020

Allogeneic Stem Cell Transplant, Leukemia, Non-Hodgkins Trial in New York (cytoreductive regimen followed by a CD34+E- selected

Completed
  • Allogeneic Stem Cell Transplant
  • +5 more
  • cytoreductive regimen followed by a CD34+E- selected allogeneic stem cell transplant
  • New York, New York
    Memorial Sloan-Kettering Cancer Center
Jan 20, 2017

Sickle Cell Anemia, Severe Aplastic Anemia, Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Orlando, Durham (Campath, Chemo

Completed
  • Sickle Cell Anemia
  • +3 more
  • Campath, Chemo and/or TBI Allo SCT
  • Orlando, Florida
  • +1 more
Nov 19, 2014

Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Worldwide (ALXN1102, ALXN1103)

Terminated
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • Los Angeles, California
  • +4 more
May 21, 2014

Acute Lymphoblastic Leukemia (ALL), Acute Myeloid Leukemia (AML), Secondary AML Trial in Memphis (procedure, device, drug)

Completed
  • Acute Lymphoblastic Leukemia (ALL)
  • +9 more
  • Stem Cell Transplantation
  • +2 more
  • Memphis, Tennessee
    St. Jude Children's Research Hospital
Feb 12, 2009