paroxysmal nocturnal hemoglobinuria (pnh)
Showing 1 - 21 of 21
Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial (MY008211A tablets)
Not yet recruiting
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
- MY008211A tablets
- (no location specified)
Nov 17, 2023
Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Brisbane (ADX-038, Placebo)
Not yet recruiting
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
- ADX-038
- Placebo
-
Brisbane, Queensland, AustraliaNucleus Network Brisbane
May 17, 2023
Severe Aplastic Anemia (SAA), Hypo-Plastic Myelodysplastic Syndrome (MDS), Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial run
Recruiting
- Severe Aplastic Anemia (SAA)
- +2 more
- Cyclophosphamide
- Peripheral Blood Stem Cells
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 28, 2023
Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Worldwide (LNP023, Eculizumab, Ravulizumab)
Active, not recruiting
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
- LNP023
- +2 more
-
Duarte, California
- +39 more
Jan 13, 2023
Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Worldwide (BCX9930 monotherapy, Placebo)
Active, not recruiting
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
- BCX9930 monotherapy
- Placebo
-
Ampang, Malaysia
- +3 more
Dec 15, 2022
Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Worldwide (BCX9930, Eculizumab, Ravulizumab)
Active, not recruiting
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
- BCX9930
- +2 more
-
Paris, France
- +6 more
Dec 15, 2022
Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Worldwide (Iptacopan (LNP023))
Active, not recruiting
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
- Iptacopan (LNP023)
-
Tianjin, Tianjin, China
- +11 more
Nov 21, 2022
Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Italy, United Kingdom, United States (Danicopan, Eculizumab)
Active, not recruiting
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
-
Baltimore, Maryland
- +4 more
Aug 15, 2022
Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Worldwide (Ravulizumab, Eculizumab)
Completed
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
- Ravulizumab
- Eculizumab
-
Duarte, California
- +48 more
Jul 14, 2022
Paroxysmal Nocturnal Hemoglobinuria (PNH), Paroxysmal Hemoglobinuria Trial in Worldwide (Pegcetacoplan)
Recruiting
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
- Paroxysmal Hemoglobinuria
-
Atlanta, Georgia
- +9 more
Jul 18, 2022
Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Worldwide (Danicopan)
Completed
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
-
Florence, Italy
- +4 more
May 31, 2022
Paroxysmal Nocturnal Hemoglobinuria (PNH), CD55-deficient Protein-losing Enteropathy (PLE), CD59 Deficiency Trial (Pozelimab)
Available
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
- +2 more
- (no location specified)
Jan 28, 2022
Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Worldwide (REGN3918)
Completed
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
-
Sha Tin, Hong Kong
- +11 more
Jul 13, 2021
Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in United States (Pegcetacoplan)
No longer available
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
-
Jacksonville, Florida
- +3 more
Jun 2, 2021
Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in United States (Pegcetacoplan)
Completed
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
-
Los Angeles, California
- +6 more
Dec 14, 2020
Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Almaty, Vilnius, Colombo (rVA576, Standard of care (SOC))
Completed
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
- rVA576
- Standard of care (SOC)
-
Almaty, Microdistrict Kalkaman, Kazakhstan
- +2 more
Nov 3, 2020
Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Barcelona, Leeds, London (ALN-CC5, Sterile Normal Saline (0.9% NaCl))
Completed
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
- ALN-CC5
- Sterile Normal Saline (0.9% NaCl)
-
Barcelona, Spain
- +3 more
Mar 17, 2020
Allogeneic Stem Cell Transplant, Leukemia, Non-Hodgkins Trial in New York (cytoreductive regimen followed by a CD34+E- selected
Completed
- Allogeneic Stem Cell Transplant
- +5 more
- cytoreductive regimen followed by a CD34+E- selected allogeneic stem cell transplant
-
New York, New YorkMemorial Sloan-Kettering Cancer Center
Jan 20, 2017
Sickle Cell Anemia, Severe Aplastic Anemia, Paroxysmal Nocturnal Hemoglobinuria (PNH) Trial in Orlando, Durham (Campath, Chemo
Completed
- Sickle Cell Anemia
- +3 more
- Campath, Chemo and/or TBI Allo SCT
-
Orlando, Florida
- +1 more
Nov 19, 2014
Acute Lymphoblastic Leukemia (ALL), Acute Myeloid Leukemia (AML), Secondary AML Trial in Memphis (procedure, device, drug)
Completed
- Acute Lymphoblastic Leukemia (ALL)
- +9 more
- Stem Cell Transplantation
- +2 more
-
Memphis, TennesseeSt. Jude Children's Research Hospital
Feb 12, 2009