peroxisomal disorders

Showing 1 - 5 of 5

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD

Recruiting
  • Mucopolysaccharidosis Disorders
  • +28 more
  • Stem Cell Transplantation
  • +7 more
  • Minneapolis, Minnesota
    Masonic Cancer Center, University of Minnesota
Nov 1, 2022

Protein Translocation in Patients With Beta-Oxidation Disorders

Completed
  • Beta-Oxidation Disorder
  • Peroxisomal Disorders
    • (no location specified)
    Sep 21, 2021

    Infantile Refsum's Disease, Zellweger Syndrome, Adrenoleukodystrophy Trial in Cincinnati (Cholic Acids)

    Completed
    • Infantile Refsum's Disease
    • +4 more
    • Cholic Acids
    • Cincinnati, Ohio
      Cincinnati Children's Hospital Medical Center
    Sep 28, 2020

    New Strategy for the Diagnosis of Peroxisomal Diseases

    Recruiting
    • Peroxisomal Disorders
    • Diagnoses Disease
      • Amiens, France
      • +3 more
      Aug 24, 2020

      Mucopolysaccharidosis, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Campath-1H, Cyclophosphamide, Busulfan)

      Completed
      • Mucopolysaccharidosis
      • +12 more
      • Minneapolis, Minnesota
        Masonic Cancer Center, University of Minnesota
      Jan 9, 2018