peroxisome biogenesis disorders

Showing 1 - 2 of 2

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Zellweger Syndrome, Peroxisome Biogenesis Disorders Trial in Toronto (Hydroxychloroquine, Placebo)

Completed
  • Zellweger Syndrome
  • Peroxisome Biogenesis Disorders
  • Toronto, Ontario, Canada
    The Hospital for Sick Children
Dec 15, 2020

Peroxisome Biogenesis Disorders Trial in Montreal (Betaine)

Completed
  • Peroxisome Biogenesis Disorders
  • Montreal, Quebec, Canada
    Montreal Children's Hospital
May 20, 2016