Clincosm LogoSign in Get a demo

pompe disease

Showing 1 - 25 of 68
STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS
LAST UPDATED

Pompe Disease, Muscle Loss, Obesity Trial (Multi-ingredient supplement (PDT-MIS), Placebo (PLA))

Not yet recruiting
  • Pompe Disease
  • +7 more
  • Multi-ingredient supplement (PDT-MIS)
  • Placebo (PLA)
  • (no location specified)
Nov 8, 2023

Pompe Disease Trial in New York, Fairfax (biological, drug, other)

Not yet recruiting
  • Pompe Disease
  • Cipaglucosidase alfa
  • +3 more
  • New York, New York
  • +1 more
Nov 2, 2023

Pompe Disease -Non-invasive Magnetic Resonance Exploratory Pilot

Not yet recruiting
  • Pompe Disease
  • McArdle Disease
  • Siemens Magnetom 7T Plus
  • Vienna, Austria
    Medical University of Vienna
Jul 5, 2023

Avalglucosidase Alfa Pregnancy Study

Recruiting
  • Pompe Disease
  • Pregnancy
  • avalglucosidase alfa-NGPT (GZ402666) IV
  • avalglucosidase alfa-NGPT (GZ402666)
  • Bridgewater, New Jersey
    Investigational site worldwide
Feb 15, 2023

Baby Detect : Genomic Newborn Screening

Recruiting
  • Congenital Adrenal Hyperplasia
  • +126 more
    • Liege, Wallonia, Belgium
      CRMN, Hôpital La Citadelle
    Jan 24, 2023

    Glycogen Storage Disease Type II, Pompe Disease Trial in Worldwide

    Recruiting
    • Glycogen Storage Disease Type II
    • Pompe Disease
      • Birmingham, Alabama
      • +274 more
      Jan 12, 2023

      Patients With "Late-Onset" Pompe Disease

      Active, not recruiting
      • Pompe Disease
      • +2 more
      • Observational
      • Durham, North Carolina
        Duke University
      Oct 7, 2022

      Pompe Disease, Glycogen Storage Disease Type II (GSD-II), Acid Maltase Deficiency Disease Trial in Gainesville, Decatur, Detroit

      Completed
      Has Results
      • Pompe Disease
      • +2 more
      • alglucosidase alfa
      • Gainesville, Florida
      • +2 more
      Jul 29, 2022

      Pompe Disease, Pompe Disease (Late-onset), Glycogen Storage Disease Type 2 Trial in Worldwide (SPK-3006)

      Active, not recruiting
      • Pompe Disease
      • +6 more
      • SPK-3006
      • Phoenix, Arizona
      • +28 more
      Jul 22, 2022

      Cognitive and Neurological Pathologies in Pompe Disease

      Recruiting
      • Pompe Disease
        • Durham, North Carolina
          Duke University Medical Center
        Jun 30, 2022

        Pompe Disease, Pompe Disease (Late-onset), Pompe's Disease Juvenile Onset Trial in Erlangen (Multispectral Optoacoustic

        Recruiting
        • Pompe Disease
        • +3 more
        • Multispectral Optoacoustic Tomography
        • Erlangen, Bavaria, Germany
          University Hospital Erlangen
        Jun 2, 2022

        Pompe Disease Trial in Zürich (Testing of reliability / validity of new questionnaire)

        Recruiting
        • Pompe Disease
        • Testing of reliability / validity of new questionnaire
        • Zürich, Switzerland
          University Childrens Hospital Zürich
        May 25, 2022

        Pompe Disease Trial in Saint Louis, New York, Durham (ACTUS-101)

        Recruiting
        • Pompe Disease
        • ACTUS-101
        • Saint Louis, Missouri
        • +2 more
        May 25, 2022

        Clinical Specimen Collection From Pompe Disease Patients

        Recruiting
        • Pompe Disease
        • Toluca Lake, California
          Seraph Research Institute
        May 17, 2022

        Myozyme® and of Aldurazyme® in Male and Female Participants of

        Recruiting
        • Pompe Disease
        • Mucopolysaccharidosis Type I (MPS I)
          • Italy, Italy
            Investigational site Italy
          May 3, 2022

          Pompe Disease, Glycogen Storage Disease Type II (GSD-II), Glycogenesis 2 Acid Maltase Deficiency Trial in Israel, United States

          Terminated
          Has Results
          • Pompe Disease
          • +2 more
          • Myozyme® (alglucosidase alfa)
          • Louisville, Kentucky
          • +4 more
          Mar 24, 2022

          Pompe Disease Trial in Gainesville (genetic, drug, other)

          Completed
          • Pompe Disease
          • Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase
          • +7 more
          • Gainesville, Florida
            Clinical and Translational Research Building (CTRB), University
          Mar 24, 2022

          Pompe Disease, Glycogen Storage Disease Type II (GSD II) Trial in Worldwide (alglucosidase alfa)

          Completed
          Has Results
          • Pompe Disease
          • Glycogen Storage Disease Type II (GSD II)
          • alglucosidase alfa
          • Valhalla, New York
          • +11 more
          Mar 15, 2022

          Frequency of Pompe Disease in Myalgia With or Without Hyper

          Recruiting
          • Pompe Disease
            • Fort-de-France, Martinique
              CHU de Martinique
            Oct 28, 2021

            Pompe Telemedicine Developmental Study

            Completed
            • Pompe Disease
            • Glycogen Storage Disease II
              • Durham, North Carolina
                Duke University Medical Center
              Oct 27, 2021

              Pompe Disease Trial in Worldwide (ATB200, AT2221)

              Active, not recruiting
              • Pompe Disease
              • Phoenix, Arizona
              • +18 more
              Oct 19, 2021

              CRIM Status and Longitudinal Follow-up of Individuals With Pompe

              Recruiting
              • Pompe Disease
              • Observational
              • Durham, North Carolina
                Duke University Medical Center
              Sep 16, 2021

              Screen of Childhood Late-onset Pompe Disease in Pediatric

              Not yet recruiting
              • Pompe Disease
                • Taipei, Taiwan
                  Wen-Chin Weng
                Jul 21, 2021

                Pompe Disease, Pompe Disease (Late-onset), Glycogen Storage Disease Type 2 Trial in Worldwide (Neutralizing Antibody to SPK-3006

                Completed
                • Pompe Disease
                • +5 more
                • Neutralizing Antibody to SPK-3006 capsid
                • Phoenix, Arizona
                • +17 more
                Jul 14, 2021

                Pompe Disease Trial in Worldwide (alglucosidase alfa)

                Completed
                • Pompe Disease
                • alglucosidase alfa
                • Phoenix, Arizona
                • +17 more
                Jul 12, 2021