rett syndrome

Showing 1 - 25 of 67

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Rett Syndrome Trial (TSHA-102)

Not yet recruiting
  • Rett Syndrome
  • TSHA-102
  • (no location specified)
Nov 21, 2023

Telomeric 22Q13 Monosomy Syndrome, Tuberous Sclerosis, Hamartoma Syndrome, Multiple Trial in Chicago (Functional Behavioral

Enrolling by invitation
  • Telomeric 22Q13 Monosomy Syndrome
  • +7 more
  • Functional Behavioral Training (FBT)
  • Positive Parenting Strategies-Treatment as Usual
  • Chicago, Illinois
    Autism Assessment Research Treatment and Services (AARTS) Center
Nov 14, 2023

Neurophysiologic Biomarkers in Rett Syndrome

Not yet recruiting
  • Rett Syndrome
  • +2 more
  • EEG and Auditory and Visual Evoked Potentials (AEP and VEP)
  • Los Angeles, California
  • +5 more
Jun 27, 2023

Rett Syndrome Trial in Aurora, Boston, Houston (NGN-401)

Recruiting
  • Rett Syndrome
  • NGN-401
  • Aurora, Colorado
  • +2 more
Jun 12, 2023

Gene Editing as a Therapeutic Approach for Rett Syndrome

Recruiting
  • Rett Syndrome
  • Gene editing in vitro
  • Siena, Italy
    University of Siena
Feb 13, 2023

Rett Syndrome Trial in Australia, Canada, United Kingdom (ANAVEX2-73 oral liquid, Placebo oral liquid)

Recruiting
  • Rett Syndrome
  • ANAVEX2-73 oral liquid
  • Placebo oral liquid
  • Sydney, New South Wales, Australia
  • +11 more
Jan 31, 2023

Rett Syndrome Trial in Verona (Osteopathic manipulative treatment)

Completed
  • Rett Syndrome
  • Osteopathic manipulative treatment
  • Verona, Italy
    Centro AIRETT Ricerca e Innovazione (CARI)
Jan 30, 2023

Rett Syndrome Trial in Bosisio Parini (GRAIL)

Completed
  • Rett Syndrome
  • GRAIL
  • Bosisio Parini, Lecco, Italy
    IRCCS E. Medea
Jan 19, 2023

Rett Syndrome Trial (VYNT-0126, Placebo)

Not yet recruiting
  • Rett Syndrome
  • (no location specified)
Nov 14, 2022

Rett Syndrome Trial in Montréal (TSHA-102)

Recruiting
  • Rett Syndrome
  • TSHA-102
  • MontrĂ©al, Canada
    Taysha Study Site
Nov 8, 2022

Rett Syndrome Trial in United States (Trofinetide, Placebo)

Completed
  • Rett Syndrome
  • Birmingham, Alabama
  • +20 more
Oct 28, 2022

Rett Syndrome, RTT Trial in Worldwide (GWP42003-P)

Terminated
  • Rett Syndrome
  • RTT
  • Birmingham, Alabama
  • +30 more
Jul 12, 2022

Rett Syndrome Trial in Verona (Rehabilitative Intervention)

Active, not recruiting
  • Rett Syndrome
  • Rehabilitative Intervention
  • Verona, Italy
    Centro AIRETT Ricerca e Innovazione (CARI)
Aug 3, 2022

Rett Syndrome, Rett Syndrome, Atypical, Genetic Disease Trial in United States

Recruiting
  • Rett Syndrome
  • +9 more
    • Birmingham, Alabama
    • +13 more
    Jul 12, 2022

    Rett Syndrome, Dysbiosis, Epilepsy Trial in Siena (ALAC, inulin, FOS, and sodium butyrate, Sodium butyrate and zinc oxide)

    Recruiting
    • Rett Syndrome
    • +3 more
    • ALAC, inulin, FOS, and sodium butyrate
    • Sodium butyrate and zinc oxide
    • Siena, Italy
      Policlinico "S. Maria alle Scotte" Azienda Ospedaliera Universit
    Jun 15, 2022

    Rett Syndrome Trial in United States (Trofinetide)

    Active, not recruiting
    • Rett Syndrome
    • Birmingham, Alabama
    • +6 more
    May 4, 2022

    Rett Syndrome Trial (calcium, )

    Completed
    • Rett Syndrome
    • calcium
    • placebo
    • (no location specified)
    Apr 27, 2022

    Rett Syndrome Trial in Trumbull

    Enrolling by invitation
    • Rett Syndrome
      • Trumbull, Connecticut
        Rett Syndrome Research Trust
      Apr 25, 2022

      Development of the ORCA Communication Measure for Rett Syndrome

      Completed
      • Rett Syndrome
        • Durham, North Carolina
          Duke University
        Apr 20, 2022

        Fragile X Syndrome, Angelman Syndrome, Prader-Willi Syndrome Trial in Research Triangle Park (Parent-Infant Inter(X)action

        Enrolling by invitation
        • Fragile X Syndrome
        • +13 more
        • Parent-Infant Inter(X)action Intervention (PIXI)
        • Research Triangle Park, North Carolina
          RTI International
        Feb 23, 2022

        Analysis of the Glutathione Cycle in Children With Rett Syndrome

        Withdrawn
        • Rett Syndrome
          • Birmingham, Alabama
            University of Alabama, Birmingham
          Jan 20, 2022

          Rett Syndrome Trial in Australia, United Kingdom (ANAVEX2-73, Placebo)

          Completed
          • Rett Syndrome
          • Greenwich, New South Wales, Australia
          • +6 more
          Jan 18, 2022

          Rett Syndrome, RTT Trial in Worldwide (GWP42003-P, Placebo)

          Terminated
          • Rett Syndrome
          • RTT
          • Birmingham, Alabama
          • +25 more
          Dec 1, 2021

          Rett Syndrome Trial in Worldwide (Sarizotan low dose, Sarizotan high dose, Placebo)

          Terminated
          • Rett Syndrome
          • Sarizotan low dose
          • +2 more
          • Birmingham, Alabama
          • +13 more
          Nov 22, 2021

          Rett Syndrome Trial in United States (Trofinetide)

          Active, not recruiting
          • Rett Syndrome
          • Birmingham, Alabama
          • +20 more
          Nov 29, 2021