Leber Congenital Amaurosis
Showing 26 - 50 of 1,911
Acute LHON, Onset Within Three Months, Onset Between 3 to 6 Months Trial in Wuhan (rAAV2-ND4)
Unknown status
- Acute LHON
- +6 more
-
Wuhan, Hubei, ChinaDepartment of Ophthalmology ,Tongji Hospital, Tongji Medical Col
Jul 27, 2020
Blindness Trial in Pittsburgh (BrainPort V200 Device)
Active, not recruiting
- Blindness
- BrainPort V200 Device
-
Pittsburgh, PennsylvaniaUPMC Eye Center
Aug 15, 2021
Leber Congenital Amaurosis Trial in Worcester, Portland (rAAV2-CB-hRPE65)
Completed
- Leber Congenital Amaurosis
- rAAV2-CB-hRPE65
-
Worcester, Massachusetts
- +1 more
Dec 1, 2017
Retinitis Pigmentosa Trial in Amman (Stem Cell Transplantation)
Unknown status
- Retinitis Pigmentosa
- Stem Cell Transplantation
-
Amman, JordanStem Cells Arabia
Mar 15, 2020
Pattern of Congenital Hypothyroidism in Newborns.
Not yet recruiting
- Pattern of CH
- (no location specified)
Sep 26, 2023
SGLT2 for Heart Failure in CHD Patients
Not yet recruiting
- Heart Failure
-
Nice, FranceUniversity hospital of Nice
Jun 7, 2023
Congenital Syphilis in Switzerland
Completed
- Congenital Syphilis
- Epidemiological study
-
Geneva, SwitzerlandLaurence Toutous Trellu
Jul 27, 2023
Neonatal Duodenal Atresia
Recruiting
- Congenital Duodenal Atresia
-
Strasbourg, FranceService de Chirurgie pédiatrique - CHU de Strasbourg - France
Oct 30, 2023
Heart Defects, Congenital, Cardiovascular Disease Other Trial in Columbus (Physical Activity Monitoring, Tailored Exercise
Recruiting
- Heart Defects, Congenital
- Cardiovascular Disease Other
- Physical Activity Monitoring
- +3 more
-
Columbus, OhioNationwide Children's Hospital
Aug 23, 2023
Pyeloplasty Trial (pyeloplasty)
Not yet recruiting
- Pyeloplasty
- pyeloplasty
- (no location specified)
Nov 20, 2023
Mitochondrial Diseases, Pearson Syndrome Trial in Ramat Gan (MNV-201)
Recruiting
- Mitochondrial Diseases
- Pearson Syndrome
- MNV-201
-
Ramat Gan, IsraelSheba Medical Center
Aug 24, 2023
Visual Prognosis and Complications of Ectopia Lentis Lens
Recruiting
- Ectopia Lentis
- Dislocation, Lens
-
Guangzhou, Guangdong, ChinaGuangdong Provincial Clinical Research Center for Ocular Disease
Dec 23, 2022
Closed-loop Management System of Congenital Talipes Equinovarus
Recruiting
- Prenatal Diagnosis and Closed-loop Management System of Congenital Talipes Equinovarus
-
Nanjing, Jiangsu, ChinaDrum Tower hospital
Nov 27, 2022
Frailty and Non-Fragile Congenital Heart Disease
Not yet recruiting
- Congenital Heart Disease
- Frailty
- Observational
- (no location specified)
Apr 10, 2023
Congenital Heart Disease in Pregnancy, Prenatal Diagnosis, Fetal Echocardiography Trial (Improvement on Prenatal Screening and
Not yet recruiting
- Congenital Heart Disease in Pregnancy
- +2 more
- Improvement on Prenatal Screening and Treatment Capabilities for Congenital Heart Disease with a Comprehensive Diagnosis and Treatment Program Incorporating New Technologies
- (no location specified)
Jul 2, 2023
Genetic Diagnosis in Congenital Cataracts
Completed
- Congenital Cataract
- Ophthalmic examination
- Whole-exome sequencing
-
Guangzhou, Guangdong, ChinaZhongshan Ophthalmic Center, Sun Yat-sen University
Mar 12, 2023
Congenital Diaphragmatic Hernias Trial in Hartford (Fetoscopic Endoluminal Tracheal Occlusion (FETO))
Recruiting
- Congenital Diaphragmatic Hernias
- Fetoscopic Endoluminal Tracheal Occlusion (FETO)
-
Hartford, ConnecticutConnecticut Children's Medical Center
Sep 26, 2023
Exploring Patient Reported Outcomes in Inherited Ichthyosis
Recruiting
- Congenital Ichthyosis
- Questionnaires with patient reported outcome measures
-
Maastricht, NetherlandsMaastricht University Medical Centre +
Nov 6, 2023
Congenital Heart Defects
Not yet recruiting
- Congenital Heart Defects
- (no location specified)
Nov 5, 2023
Cleft Lip and Palate Trial in Alexandria (Feeding appliance)
Completed
- Cleft Lip and Palate
- Feeding appliance
-
Alexandria, EgyptFaculty of Dentistry, Alexandria University
Oct 4, 2023
Transcatheter Neonatal Cardiac Interventions Trial in Sohag (transcatheter cardiac intervention)
Recruiting
- Transcatheter Neonatal Cardiac Interventions
- transcatheter cardiac intervention
-
Sohag, EgyptSohag University
Nov 9, 2023
Evaluation of Risk Factors and Outcome of Thrombosis in Children
Not yet recruiting
- Thrombosis in Children
- complete blood count
-
Sohag, EgyptSohag University hospitals
Apr 30, 2023
A Study of Invasive Hemodynamic for MACHD Registry
Not yet recruiting
- Healthy
- Congenital Heart Disease
-
Rochester, MinnesotaMayo Clinic Rochester
Apr 27, 2023
Pulmonary Arterial Hypertension, Dilated Cardiomyopathy, Congenital Heart Disease Trial (IntelliStent)
Not yet recruiting
- Pulmonary Arterial Hypertension
- +2 more
- IntelliStent
- (no location specified)
Oct 6, 2023
Observatory of Pulmonary Arterial Hypertension of Congenital
Completed
- Pulmonary Arterial Hypertension of Congenital Heart Disease
-
Paris, FranceHopital Necker Enfants Malades
Sep 20, 2022