Mucopolysaccharidosis VII
Showing 26 - 50 of 245
Head and Neck Tumors, Congenital Abnormalities Trial in Paris (Tractography MRI)
Not yet recruiting
- Head and Neck Neoplasms
- Congenital Abnormalities
- Tractography MRI
-
Paris, FranceHôpital Necker-Enfants Malades
Mar 15, 2023
Mucopolysaccharidosis Type 3 B Trial in Worldwide (rAAV9.CMV.hNAGLU)
Terminated
- Mucopolysaccharidosis Type 3 B
- rAAV9.CMV.hNAGLU
-
Columbus, Ohio
- +3 more
Apr 29, 2022
Mucopolysaccharidosis Type VI Trial in Naples, Ankara (AAV2/8.TBG.hARSB)
Active, not recruiting
- Mucopolysaccharidosis Type VI
- AAV2/8.TBG.hARSB
-
Naples, Italy
- +1 more
Nov 22, 2021
Recombinant Factor VII for Intractable Postpartum Haemorrhage
Completed
- Post Partum Hemorrhage
- recombinant factor VIIa
-
Cairo, EgyptDoaaa Alaa
Mar 18, 2022
Sanfilippo Syndrome A Trial (assessment)
Not yet recruiting
- Sanfilippo Syndrome A
- assessment
- (no location specified)
Jun 6, 2021
Mucopolysaccharidosis (MPS), Hunter Syndrome Trial (ELAPRASE, Rituximab, Methotrexate)
Not yet recruiting
- Mucopolysaccharidosis (MPS)
- Hunter Syndrome
- ELAPRASE
- +3 more
- (no location specified)
Aug 8, 2022
Respiratory Cathepsins, Proteases Inhibitors and
Completed
- Mucopolysaccharidoses
- Sputum
- Tracheal aspiration
-
Angers, France
- +6 more
Jan 3, 2022
Mucopolysaccharidosis IV A, Morquio A Syndrome, MPS IVA Trial in Worldwide (BMN 110 - Weekly, BMN 110 - Every Other Week)
Completed
- Mucopolysaccharidosis IV A
- +2 more
- BMN 110 - Weekly
- BMN 110 - Every Other Week
-
Phoenix, Arizona
- +42 more
Jul 19, 2021
Mucopolysaccharidosis IH Trial in Milano (Frozen autologous CD34+ hematopoietic stem and progenitor cells genetically modified
Active, not recruiting
- Mucopolysaccharidosis IH
- Frozen autologous CD34+ hematopoietic stem and progenitor cells genetically modified with the lentiviral vector IDUA LV, encoding for the α-L-iduronidase cDNA, in their final formulation medium.
-
Milano, ItalyOspedale San Raffaele
Aug 6, 2021
Epidermolysis Bullosa Dystrophica, Recessive Trial in Stanford, Aurora (FCX-007)
Active, not recruiting
- Epidermolysis Bullosa Dystrophica, Recessive
- FCX-007
-
Stanford, California
- +1 more
Sep 30, 2021
Mucopolysaccharidosis, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Campath-1H, Cyclophosphamide, Busulfan)
Completed
- Mucopolysaccharidosis
- +12 more
- Campath-1H
- +5 more
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Jan 9, 2018
Mucopolysaccharidosis IV Type A, Morquio A Syndrome, MPS IVA Trial in Worldwide (Vimizim® (elosulfase alfa))
Active, not recruiting
- Mucopolysaccharidosis IV Type A
- +2 more
- Vimizim® (elosulfase alfa)
-
Phoenix, Arizona
- +78 more
Dec 23, 2022
Hunter Syndrome Trial in India (Elaprase)
Recruiting
- Hunter Syndrome
- Elaprase
-
Thiruvananthapuram, Kerala, India
- +4 more
May 5, 2022
Mucopolysaccharidosis Trial in Gaziantep (Enzyme Replacement Agent)
Completed
- Mucopolysaccharidosis
- Enzyme Replacement Agent
-
Gaziantep, None Selected, TurkeySerkan Usgu
Aug 7, 2021
Mucopolysaccharidosis II Trial in Oakland (JR-141)
Not yet recruiting
- Mucopolysaccharidosis II
-
Oakland, CaliforniaUCSF Benioff Children's Hospital Oakland
Oct 21, 2022
Mucopolysaccharidosis II Trial in Cincinnati (DNL310)
Enrolling by invitation
- Mucopolysaccharidosis II
-
Cincinnati, OhioCincinnati Children's Hospital Medical Center
Oct 10, 2023
Striae Distensae Trial in Xi'an (Polylevolactic Acid Injection, 1565nm Non-ablative Fractional Laser, Polylevolactic Acid
Recruiting
- Striae Distensae
- Polylevolactic Acid Injection
- +2 more
-
Xi'an, Shaanxi, ChinaDermatology Derpartment of Xijing Hospital
Apr 24, 2023
Mucopolysaccharidosis VI Clinical Surveillance Program
Completed
- Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome)
-
Irvine, California
- +49 more
Apr 2, 2021
Coagulation Testing in Patients Undergoing Cardiac Surgery
Active, not recruiting
- Congenital Heart Disease
- Discarded blood samples
- Discarded Urine Sample
-
Boston, MassachusettsBoston Children's Hospital
Jan 7, 2023