Sandhoff
Showing 26 - 31 of 31
Cutaneous Atrophy Due to Corticosteroids Trial in Paris (Clobetasol + Spironolactone, Clobetasol + Placebo, Placebo +
Completed
- Cutaneous Atrophy Due to Corticosteroids
- Clobetasol + Spironolactone
- +3 more
-
Paris, FranceBichat Hospital
Jul 2, 2015
Inherited Metabolic Diseases, Lysosomal Storage Disorders, Peroxisomal Storage Diseases Trial in Los Angeles, New York, Durham
Terminated
- Inherited Metabolic Diseases
- +4 more
- ALD-101
-
Los Angeles, California
- +2 more
Jul 7, 2014
Gangliosidoses, GM2, Sandhoff Disease, Tay-Sachs Disease Trial in Toronto (Pyrimethamine, Leucovorin)
Completed
- Gangliosidoses, GM2
- +2 more
-
Toronto, Ontario, CanadaThe Hospital for Sick Children
Feb 22, 2012
Cystic Fibrosis, Pancreatic Insufficiency Trial in Philadelphia (Lym-X-Sorb powder, Placebo powder)
Completed
- Cystic Fibrosis
- Pancreatic Insufficiency
- Lym-X-Sorb powder
- Placebo powder
-
Philadelphia, PennsylvaniaChildren's Hospital of Philadelphia (CHOP)
Jan 11, 2013
GM2 Gangliosidoses, Tay-Sachs, Sandhoff Disease Trial in Washington (Zavesca (Miglustat))
Completed
- GM2 Gangliosidoses
- +2 more
- Zavesca (Miglustat)
-
Washington, District of ColumbiaChildren's National Medical Center
May 5, 2008