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Sandhoff

Showing 26 - 31 of 31

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Cutaneous Atrophy Due to Corticosteroids Trial in Paris (Clobetasol + Spironolactone, Clobetasol + Placebo, Placebo +

Completed
  • Cutaneous Atrophy Due to Corticosteroids
  • Clobetasol + Spironolactone
  • +3 more
  • Paris, France
    Bichat Hospital
Jul 2, 2015

Inherited Metabolic Diseases, Lysosomal Storage Disorders, Peroxisomal Storage Diseases Trial in Los Angeles, New York, Durham

Terminated
  • Inherited Metabolic Diseases
  • +4 more
  • ALD-101
  • Los Angeles, California
  • +2 more
Jul 7, 2014

Gangliosidoses, GM2, Sandhoff Disease, Tay-Sachs Disease Trial in Toronto (Pyrimethamine, Leucovorin)

Completed
  • Gangliosidoses, GM2
  • +2 more
  • Toronto, Ontario, Canada
    The Hospital for Sick Children
Feb 22, 2012

Cystic Fibrosis, Pancreatic Insufficiency Trial in Philadelphia (Lym-X-Sorb powder, Placebo powder)

Completed
  • Cystic Fibrosis
  • Pancreatic Insufficiency
  • Lym-X-Sorb powder
  • Placebo powder
  • Philadelphia, Pennsylvania
    Children's Hospital of Philadelphia (CHOP)
Jan 11, 2013

GM2 Gangliosidoses, Tay-Sachs, Sandhoff Disease Trial in Washington (Zavesca (Miglustat))

Completed
  • GM2 Gangliosidoses
  • +2 more
  • Zavesca (Miglustat)
  • Washington, District of Columbia
    Children's National Medical Center
May 5, 2008