Factor IX
Showing 51 - 75 of >10,000
Hemophilia A, Hemophilia B Trial in Worldwide (fitusiran, factor concentrates)
Completed
- Hemophilia A
- Hemophilia B
- fitusiran
- factor concentrates
-
Little Rock, Arkansas
- +63 more
Mar 15, 2022
Mutation p.Ile112Thr : Discrepancy Between Factor IX Level and
Unknown status
- Hemophilia B
- data collection
-
Dijon, FranceCHU Dijon Bourgogne
May 9, 2019
Hemophilia A, Hemophilia B Trial in Worldwide (Fitusiran (SAR439774))
Active, not recruiting
- Hemophilia A
- Hemophilia B
- Fitusiran (SAR439774)
-
Ann Arbor, Michigan
- +11 more
Aug 4, 2022
Patterns of Hemophilia Care in Assiut Children Patients
Not yet recruiting
- Hemophilia A
- Hemophilia B
- (no location specified)
Jul 29, 2023
Hemophilia B, Hemophilia A Trial in Worldwide (Standard of Care FIX Replacement therapy, Standard of Care FVIII Replacement
Recruiting
- Hemophilia B
- Hemophilia A
- Standard of Care FIX Replacement therapy
- Standard of Care FVIII Replacement therapy
-
Palo Alto, California
- +77 more
Dec 29, 2022
Hemophilia A Trial in Worldwide (SPK-8011)
Recruiting
- Hemophilia A
- SPK-8011
-
Sacramento, California
- +18 more
Jul 15, 2022
Hemophilia B Without Inhibitor Trial (Low dose KL001, Middle dose KL001, High dose KL001)
Not yet recruiting
- Hemophilia B Without Inhibitor
- Low dose KL001
- +2 more
- (no location specified)
Nov 5, 2023
Hemophilia B Without Inhibitor Trial (Low dose KL001, Middle dose KL001, High dose KL001)
Not yet recruiting
- Hemophilia B Without Inhibitor
- Low dose KL001
- +2 more
- (no location specified)
Nov 5, 2023
Hemophilia B, Blood Coagulation Disorders, Inherited, Blood Coagulation Disorder Trial in Worldwide
Recruiting
- Hemophilia B
- +3 more
-
Phoenix, Arizona
- +55 more
Dec 6, 2021
Hemophilia B Trial in Tianjin (Single dose intravenous injection of BBM-H901)
Active, not recruiting
- Hemophilia B
- Single dose intravenous injection of BBM-H901
-
Tianjin, Tianjin, ChinaInstitute of Hematology & Blood Diseases Hospital
Dec 12, 2021
Coagulation, Inflammation and Vessels in Chronic Liver Disease
Not yet recruiting
- Chronic Liver Diseases
- Coagulation
- biomarker assay
- (no location specified)
May 9, 2023
Factor Product Utilization and Health Outcomes in Hemophilia
Completed
- Hemophilia A, Congenital
- Hemophilia B, Congenital
-
Vancouver, British Columbia, CanadaBC Hemophilia Adult Program
Apr 26, 2021
Hemophilia B Trial in Tianjin (ZS801)
Not yet recruiting
- Hemophilia B
- ZS801
-
Tianjin, Tianjin, ChinaInstitute of Hematology & Blood Diseases Hospital
Nov 24, 2022
Hemophilia B Trial in Tianjin (ZS801)
Not yet recruiting
- Hemophilia B
- ZS801
-
Tianjin, Tianjin, ChinaInstitute of Hematology & Blood Diseases Hospital
Dec 5, 2022
Hemophilia A, Hemophilia B Trial in Worldwide (fitusiran, Bypassing agents)
Completed
- Hemophilia A
- Hemophilia B
- fitusiran
- Bypassing agents
-
Phoenix, Arizona
- +57 more
Mar 15, 2022
Duchenne Muscular Dystrophy Trial in Chengdu (JWK007 Single intravenous infusion administration)
Recruiting
- Duchenne Muscular Dystrophy
- JWK007 Single intravenous infusion administration
-
Chengdu, Sichuan, ChinaWest China Hospital, Sichuan University
Oct 29, 2023
Reliability and Validity of the Turkish Version of the PedHAL
Not yet recruiting
- Hemophilia
- +2 more
-
Gaziantep, Şahinbey, TurkeyHasan Kalyoncu University
Jun 2, 2023
Hemophilia B Trial in Philadelphia, Pittsburgh, Camperdown (AAV8-hFIX19)
Terminated
- Hemophilia B
- AAV8-hFIX19
-
Philadelphia, Pennsylvania
- +2 more
Mar 11, 2019
Observatory of Patients With Haemophilia B Treated by IdElvion®
Recruiting
- Haemophilia B
-
Annecy, France
- +23 more
Oct 4, 2022
Trauma Trial (4 factor Prothrombin Complex Concentrates)
Not yet recruiting
- Trauma
- 4 factor Prothrombin Complex Concentrates
- (no location specified)
Feb 21, 2023
Severe Hemophilia A, Osteoporosis Trial in Bron (radiation, biological, other)
Recruiting
- Severe Hemophilia A
- Osteoporosis
- HR-pQCT
- +3 more
-
Bron, FranceHôpital Cardio-Vasculaire et Pneumologique
Feb 22, 2022
Study Medicines Called Giroctocogene Fitelparvovec and
Recruiting
- Hemophilia A
- Hemophilia B
- Testing of hepatic AAV Vector integration
-
Madison, MississippiMississippi Center For Advanced Medicine
Dec 1, 2022