γ-globin
Showing 1 - 25 of 296
ß Thalassemia Major Trial in Shanghai (?-globin reactivated autologous hematopoietic stem cells)
Active, not recruiting
- β Thalassemia Major
- γ-globin reactivated autologous hematopoietic stem cells
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Shanghai, Shanghai, ChinaShanghai Bioray Laboratories Inc.
Oct 9, 2022
Thalassemia Major Trial in Shanghai (?-globin reactivated autologous hematopoietic stem cells)
Not yet recruiting
- Thalassemia Major
- γ-globin reactivated autologous hematopoietic stem cells
-
Shanghai, Shanghai, ChinaShanghai Bioray Laboratories Inc
Jul 1, 2022
Beta-Thalassemia Trial in Ferrara, Firenze, Pisa (Sirolimus 0.5 mg)
Recruiting
- Beta-Thalassemia
- Sirolimus 0.5 mg
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Ferrara, FE, Italy
- +3 more
Nov 11, 2021
Beta-Thalassemia Trial in Nanning (CS-101)
Recruiting
- Beta-Thalassemia
- CS-101
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Nanning, ChinaThe First Affiliated Hospital of Guangxi Medical University
Sep 9, 2023
Beta-Thalassemia Trial (CS-101 injection)
Not yet recruiting
- Beta-Thalassemia
- CS-101 injection
- (no location specified)
Sep 27, 2023
Pumilio1 Expression, Sickle Cell Anemia, ß-thalassemia
Not yet recruiting
- Sickle Cell Disease, Beta Thalassemia Intermedia
- RNA Binding Protein Pumilio1 (PUM1) Expression by reverse transcriptase quantatative PCR
- (no location specified)
May 30, 2023
Transfusion-dependent Beta-Thalassemia Trial in Peshawar (Thalidomide)
Completed
- Transfusion-dependent Beta-Thalassemia
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Peshawar, Khyber Pakhtunkhwa, PakistanBlood Care Clinic
Nov 19, 2023
Thalassemia Trait, Thalassemia; Mixed Trial in ChiangMai (blood draw)
Active, not recruiting
- Thalassemia Trait
- Thalassemia; Mixed
- blood draw
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ChiangMai, ThailandMaharaj Nakorn ChiangMai Hospital
Sep 22, 2022
Sickle Cell Disease Trial in Los Angeles, Boston (single infusion of autologous bone marrow derived CD34+ HSC cells transduced
Active, not recruiting
- Sickle Cell Disease
- single infusion of autologous bone marrow derived CD34+ HSC cells transduced with the lentiviral vector containing a short-hairpin RNA targeting BCL11a
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Los Angeles, California
- +1 more
Feb 8, 2022
ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)
Recruiting
- β-thalassemia
- β-globin restored autologous hematopoietic stem cells
-
Shenzhen, Guangdong, ChinaShenzhen University General Hospital
May 8, 2023
a-thalassemia Trial in Nanning (a-globin restored autologous hematopoietic stem cells)
Recruiting
- α-thalassemia
- α-globin restored autologous hematopoietic stem cells
-
Nanning, Guangxi, ChinaPLA Joint Logistic Support Force No. 923 Hospital
May 6, 2023
Quality of Life in Thalassemic Patients at Assiut University
Not yet recruiting
- Thalassemia
- Abdominal ultrasound
- (no location specified)
Mar 17, 2023
ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)
Recruiting
- β-thalassemia
- β-globin restored autologous hematopoietic stem cells
-
Shenzhen, Guangdong, ChinaShenzhen Children's Hospital
Feb 24, 2023
ß-thalassemia Trial in Shanghai (BD211)
Not yet recruiting
- β-thalassemia
- BD211
-
Shanghai, ChinaShanghai Ruijin Hospital
Mar 16, 2023
ß-thalassemia Trial (BD211)
Not yet recruiting
- β-thalassemia
- BD211
- (no location specified)
Mar 15, 2023
MDS, Myeloid Leukemia, Allogeneic Stem Cell Transplantation Trial in Pittsburgh (IFN-? (interferon gamma-1b) injection)
Recruiting
- Myelodysplastic Syndromes
- +2 more
- IFN-γ (interferon gamma-1b) injection
-
Pittsburgh, PennsylvaniaUPMC Hillman Cancer Center
Jan 5, 2023
Transfusion-dependent Beta-Thalassemia Trial in Tianjin (KL003 cell injection Drug Product)
Not yet recruiting
- Transfusion-dependent Beta-Thalassemia
- KL003 cell injection Drug Product
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
May 8, 2023
Advanced Solid Tumor, Locally Advanced Solid Tumor, Metastatic Solid Tumor Trial in Australia, United States (TransCon IL-2 ß/?,
Recruiting
- Advanced Solid Tumor
- +7 more
- TransCon IL-2 β/γ
- +4 more
-
Boston, Massachusetts
- +7 more
Nov 16, 2022
Transfusion-dependent a-Thalassemia Trial (GMCN-508A Drug Product)
Not yet recruiting
- Transfusion-dependent α-Thalassemia
- GMCN-508A Drug Product
- (no location specified)
Feb 24, 2023
Screening for Alpha Thalassemia in Healthy Volunteers
Recruiting
- Alpha Thalassemia
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 26, 2023
Effect of HBA or HBB Genetic Defects on Early Embryonic
Completed
- Thalassemia,Embryonic Development,Reproductive Sterility and Infertility
- Preimplantation genetic diagnosis
-
Changsha, Hunan, ChinaReproductive & Genetic Hospital of CITIC-XIANGYA
Jan 10, 2022
CD4/CD8+ Interferon Gamma Release Assay for Monitoring
Active, not recruiting
- Tuberculosis
- Interferon gamma release assay (IGRA)
-
Milano, ItalyIRCCS San Raffaele Scientific Institute
Feb 13, 2023
Sickle Cell Disease Trial in Paris (DREPAGLOBE drug product)
Active, not recruiting
- Sickle Cell Disease
- DREPAGLOBE drug product
-
Paris, FranceDepartment of Biotherapy, Necker-Enfants Malades Hospital
Sep 26, 2022
Head and Neck Tumors Trial (TransCon TLR7/8 Agonist, Pembrolizumab, TransCon IL-2 ß/?)
Not yet recruiting
- Head and Neck Neoplasms
- TransCon TLR7/8 Agonist
- +2 more
- (no location specified)
Aug 4, 2023
Inflammation, Platelets and Sickle Cell Disease
Not yet recruiting
- Platelet Activation
- +2 more
- Blood sampling
-
Toulouse, FranceIUCT-Oncopole University Hospital
Jan 6, 2023