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γ-globin

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ß Thalassemia Major Trial in Shanghai (?-globin reactivated autologous hematopoietic stem cells)

Active, not recruiting
  • β Thalassemia Major
  • γ-globin reactivated autologous hematopoietic stem cells
  • Shanghai, Shanghai, China
    Shanghai Bioray Laboratories Inc.
Oct 9, 2022

Thalassemia Major Trial in Shanghai (?-globin reactivated autologous hematopoietic stem cells)

Not yet recruiting
  • Thalassemia Major
  • γ-globin reactivated autologous hematopoietic stem cells
  • Shanghai, Shanghai, China
    Shanghai Bioray Laboratories Inc
Jul 1, 2022

Beta-Thalassemia Trial in Ferrara, Firenze, Pisa (Sirolimus 0.5 mg)

Recruiting
  • Beta-Thalassemia
  • Sirolimus 0.5 mg
  • Ferrara, FE, Italy
  • +3 more
Nov 11, 2021

Beta-Thalassemia Trial in Nanning (CS-101)

Recruiting
  • Beta-Thalassemia
  • CS-101
  • Nanning, China
    The First Affiliated Hospital of Guangxi Medical University
Sep 9, 2023

Beta-Thalassemia Trial (CS-101 injection)

Not yet recruiting
  • Beta-Thalassemia
  • CS-101 injection
  • (no location specified)
Sep 27, 2023

Pumilio1 Expression, Sickle Cell Anemia, ß-thalassemia

Not yet recruiting
  • Sickle Cell Disease, Beta Thalassemia Intermedia
  • RNA Binding Protein Pumilio1 (PUM1) Expression by reverse transcriptase quantatative PCR
  • (no location specified)
May 30, 2023

Transfusion-dependent Beta-Thalassemia Trial in Peshawar (Thalidomide)

Completed
  • Transfusion-dependent Beta-Thalassemia
  • Peshawar, Khyber Pakhtunkhwa, Pakistan
    Blood Care Clinic
Nov 19, 2023

Thalassemia Trait, Thalassemia; Mixed Trial in ChiangMai (blood draw)

Active, not recruiting
  • Thalassemia Trait
  • Thalassemia; Mixed
  • blood draw
  • ChiangMai, Thailand
    Maharaj Nakorn ChiangMai Hospital
Sep 22, 2022

Sickle Cell Disease Trial in Los Angeles, Boston (single infusion of autologous bone marrow derived CD34+ HSC cells transduced

Active, not recruiting
  • Sickle Cell Disease
  • single infusion of autologous bone marrow derived CD34+ HSC cells transduced with the lentiviral vector containing a short-hairpin RNA targeting BCL11a
  • Los Angeles, California
  • +1 more
Feb 8, 2022

ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)

Recruiting
  • β-thalassemia
  • β-globin restored autologous hematopoietic stem cells
  • Shenzhen, Guangdong, China
    Shenzhen University General Hospital
May 8, 2023

a-thalassemia Trial in Nanning (a-globin restored autologous hematopoietic stem cells)

Recruiting
  • α-thalassemia
  • α-globin restored autologous hematopoietic stem cells
  • Nanning, Guangxi, China
    PLA Joint Logistic Support Force No. 923 Hospital
May 6, 2023

Quality of Life in Thalassemic Patients at Assiut University

Not yet recruiting
  • Thalassemia
  • Abdominal ultrasound
  • (no location specified)
Mar 17, 2023

ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)

Recruiting
  • β-thalassemia
  • β-globin restored autologous hematopoietic stem cells
  • Shenzhen, Guangdong, China
    Shenzhen Children's Hospital
Feb 24, 2023

ß-thalassemia Trial in Shanghai (BD211)

Not yet recruiting
  • β-thalassemia
  • BD211
  • Shanghai, China
    Shanghai Ruijin Hospital
Mar 16, 2023

ß-thalassemia Trial (BD211)

Not yet recruiting
  • β-thalassemia
  • BD211
  • (no location specified)
Mar 15, 2023

MDS, Myeloid Leukemia, Allogeneic Stem Cell Transplantation Trial in Pittsburgh (IFN-? (interferon gamma-1b) injection)

Recruiting
  • Myelodysplastic Syndromes
  • +2 more
  • IFN-γ (interferon gamma-1b) injection
  • Pittsburgh, Pennsylvania
    UPMC Hillman Cancer Center
Jan 5, 2023

Transfusion-dependent Beta-Thalassemia Trial in Tianjin (KL003 cell injection Drug Product)

Not yet recruiting
  • Transfusion-dependent Beta-Thalassemia
  • KL003 cell injection Drug Product
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
May 8, 2023

Advanced Solid Tumor, Locally Advanced Solid Tumor, Metastatic Solid Tumor Trial in Australia, United States (TransCon IL-2 ß/?,

Recruiting
  • Advanced Solid Tumor
  • +7 more
  • TransCon IL-2 β/γ
  • +4 more
  • Boston, Massachusetts
  • +7 more
Nov 16, 2022

Transfusion-dependent a-Thalassemia Trial (GMCN-508A Drug Product)

Not yet recruiting
  • Transfusion-dependent α-Thalassemia
  • GMCN-508A Drug Product
  • (no location specified)
Feb 24, 2023

Screening for Alpha Thalassemia in Healthy Volunteers

Recruiting
  • Alpha Thalassemia
    • Bethesda, Maryland
      National Institutes of Health Clinical Center
    Jan 26, 2023

    Effect of HBA or HBB Genetic Defects on Early Embryonic

    Completed
    • Thalassemia,Embryonic Development,Reproductive Sterility and Infertility
    • Preimplantation genetic diagnosis
    • Changsha, Hunan, China
      Reproductive & Genetic Hospital of CITIC-XIANGYA
    Jan 10, 2022

    CD4/CD8+ Interferon Gamma Release Assay for Monitoring

    Active, not recruiting
    • Tuberculosis
    • Interferon gamma release assay (IGRA)
    • Milano, Italy
      IRCCS San Raffaele Scientific Institute
    Feb 13, 2023

    Sickle Cell Disease Trial in Paris (DREPAGLOBE drug product)

    Active, not recruiting
    • Sickle Cell Disease
    • DREPAGLOBE drug product
    • Paris, France
      Department of Biotherapy, Necker-Enfants Malades Hospital
    Sep 26, 2022

    Head and Neck Tumors Trial (TransCon TLR7/8 Agonist, Pembrolizumab, TransCon IL-2 ß/?)

    Not yet recruiting
    • Head and Neck Neoplasms
    • TransCon TLR7/8 Agonist
    • +2 more
    • (no location specified)
    Aug 4, 2023

    Inflammation, Platelets and Sickle Cell Disease

    Not yet recruiting
    • Platelet Activation
    • +2 more
    • Blood sampling
    • Toulouse, France
      IUCT-Oncopole University Hospital
    Jan 6, 2023