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Hemophilia A, Hemophilia B Trial in Worldwide (Haemophilia Early Arthropathy Detection with Ultrasound (HEAD-US), Haemophilia

Not yet recruiting
  • Hemophilia A
  • Hemophilia B
  • Haemophilia Early Arthropathy Detection with Ultrasound (HEAD-US)
  • Haemophilia Joint Health Score (HJHS)
  • Sofia, Bulgaria
  • +55 more
May 3, 2023

Cystic Fibrosis Trial in Worldwide (VX-121, TEZ, VX-561)

Completed
  • Cystic Fibrosis
  • Los Angeles, California
  • +25 more
Dec 10, 2020

Systemic Juvenile Idiopathic Arthritis Trial in Worldwide (Baricitinib, Placebo)

Recruiting
  • Systemic Juvenile Idiopathic Arthritis
  • Rosario, Santa Fe, Argentina
  • +65 more
Jan 18, 2023

Multiple Myeloma (MM), DLBCL, Not Otherwise Specified, Double Hit Lymphoma Trial in Spain (IDP-121)

Recruiting
  • Multiple Myeloma (MM)
  • +5 more
  • Santander, Cantabria, Spain
  • +4 more
Jun 19, 2023

Juvenile Idiopathic Arthritis Trial in Worldwide (Baricitinib, Placebo)

Completed
  • Juvenile Idiopathic Arthritis
  • Rosario, Santa Fe, Argentina
  • +85 more
Sep 8, 2022

Mucopolysaccharidosis Type II (MPS II) Trial in Oakland, Montréal (RGX-121)

Recruiting
  • Mucopolysaccharidosis Type II (MPS II)
  • RGX-121
  • Oakland, California
  • +1 more
Oct 6, 2022

Juvenile Idiopathic Arthritis Trial in Worldwide (Baricitinib)

Recruiting
  • Juvenile Idiopathic Arthritis
  • Rosario, Santa Fe, Argentina
  • +95 more
Jan 18, 2023

Acne Trial in United States (IDP-121 Lotion, IDP-121 Vehicle Lotion)

Completed
  • Acne
  • IDP-121 Lotion
  • IDP-121 Vehicle Lotion
  • Guntersville, Alabama
  • +38 more
Dec 16, 2019

Acne Trial in United States (IDP 121 Lotion, IDP-121 Vehicle Lotion)

Completed
  • Acne
  • IDP 121 Lotion
  • IDP-121 Vehicle Lotion
  • Glendale, Arizona
  • +33 more
Dec 16, 2019

A Long-term Follow-up Study in Subjects Who Received CTX001

Enrolling by invitation
  • Beta-Thalassemia
  • +6 more
  • CTX001
  • New York, New York
  • +12 more
Nov 18, 2022

Cystic Fibrosis Trial (VX-121/TEZ/D-IVA)

Recruiting
  • Cystic Fibrosis
  • Aurora, Colorado
  • +16 more
Jan 19, 2023

Metastatic Breast Cancer Trial in Herlev, Vejle (PARP inhibitor 2X-121)

Active, not recruiting
  • Metastatic Breast Cancer
  • PARP inhibitor 2X-121
  • Herlev, Denmark
  • +1 more
Feb 1, 2023

NSCLC, NSCLC, Adenocarcinoma Trial in Worldwide (MM-121, Docetaxel)

Terminated
  • Non-Small Cell Lung Cancer
  • +3 more
  • Tucson, Arizona
  • +34 more
Oct 11, 2021

Cystic Fibrosis Trial (VX-121/TEZ/D-IVA)

Not yet recruiting
  • Cystic Fibrosis
  • (no location specified)
Sep 7, 2022

Mucopolysaccharidosis Type II (MPS II) Trial in Brazil, United States (RGX-121)

Recruiting
  • Mucopolysaccharidosis Type II (MPS II)
  • RGX-121
  • Oakland, California
  • +4 more
Dec 22, 2022

Pemphigus Vulgaris, Pemphigus Foliaceus Trial in Worldwide (biological, other, drug)

Recruiting
  • Pemphigus Vulgaris
  • Pemphigus Foliaceus
  • efgartigimod PH20 SC
  • +2 more
  • Birmingham, Alabama
  • +130 more
Dec 22, 2022

Cystic Fibrosis Trial in Miami, San Antonio (VX-121/TEZ/D-IVA)

Recruiting
  • Cystic Fibrosis
  • Miami, Florida
  • +1 more
Aug 4, 2022

Cystic Fibrosis Trial in Worldwide (VX-121/TEZ/D-IVA, ELX/TEZ/IVA, IVA)

Recruiting
  • Cystic Fibrosis
  • Birmingham, Alabama
  • +128 more
Aug 24, 2022

Cystic Fibrosis Trial in Worldwide (VX-121/TEZ/D-IVA, ELX/TEZ/IVA, IVA)

Active, not recruiting
  • Cystic Fibrosis
  • Birmingham, Alabama
  • +169 more
Dec 22, 2022

Advanced Solid Tumors Trial in Huntersville, Cleveland (2X-121 and dovitinib)

Recruiting
  • Advanced Solid Tumors
  • 2X-121 and dovitinib
  • Huntersville, North Carolina
  • +1 more
Feb 1, 2023

ADHD Trial in United States (Amphetamine Sulfate, Placebo)

Completed
  • Attention Deficit Hyperactivity Disorder
  • Amphetamine Sulfate
  • Placebo
  • Encino, California
  • +30 more
Oct 20, 2020

Cystic Fibrosis Trial in United States (VX-121/TEZ/D-IVA)

Recruiting
  • Cystic Fibrosis
  • Aurora, Colorado
  • +6 more
Jul 26, 2022

MPS I, MPS1-S, MPS1-HS Trial in Porto Alegre, London, Salford (SIG-005 (hIDUA Producing Spheres))

Withdrawn
  • MPS I
  • +2 more
  • SIG-005 (hIDUA Producing Spheres)
  • Porto Alegre, Brazil
  • +2 more
Dec 16, 2022

Oral HPV Infection in Patients Who Are Positive to the PAP-test

Recruiting
  • HPV Infection
    • Catania, Italy
      AOU Policlinico G. Rodolico
    Jul 13, 2023

    Biliary Tract Cancer Trial in Worldwide (NUC-1031, Gemcitabine, Cisplatin)

    Terminated
    • Biliary Tract Cancer
    • Tucson, Arizona
    • +124 more
    Mar 16, 2022