Amyloid neuropathies
Showing 1 - 25 of 759
Amyloid Neuropathies, Transthyretin Amyloidosis Trial in Marseille (Electrophysiological biomarkers, MRI biomarkers)
Completed
- Amyloid Neuropathies
- Transthyretin Amyloidosis
- Electrophysiological biomarkers
- MRI biomarkers
-
Marseille, Paca, FranceAssistance Publique Des Hopitaux de Marseille
Oct 2, 2022
Long-Term Follow-Up (LTFU) of Subjects Dosed With NTLA-2001
Not yet recruiting
- Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy
- +2 more
-
Auckland, New Zealand
- +2 more
Jan 24, 2023
Hereditary Transthyretin Amyloidosis
Recruiting
- Amyloidosis
- +6 more
-
Cleveland, OhioCleveland Clinic
Mar 11, 2022
Hereditary Transthyretin Amyloidosis Trial in Roma (Assessment of disease biomarkers)
Recruiting
- Hereditary Transthyretin Amyloidosis
- Assessment of disease biomarkers
-
Roma, ID, ItalyFondazione Policlinico Universitario Agostino Gemelli IRCCS
Jun 26, 2023
Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy Trial (Acoramidis)
Withdrawn
- Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy
- (no location specified)
Jan 26, 2022
Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy, Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy,
Recruiting
- Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy
- +2 more
- NTLA-2001
-
Paris, France
- +3 more
Nov 29, 2022
The Regional Scintigraphic DPD Uptake in Cardiac Transthyretin
Recruiting
- Transthyretin Amyloidosis
- 99mTc-DPD scintigraphy
- Collection of blood samples and echocardiography
-
Krakow, Lesser Poland, PolandDepartment of Cardiac and Vascular Diseases, John Paul II Hospit
Apr 14, 2023
Transthyretin Amyloidosis (ATTR) With Cardiomyopathy Trial (NTLA-2001, Placebo)
Not yet recruiting
- Transthyretin Amyloidosis (ATTR) With Cardiomyopathy
- NTLA-2001
- Placebo
- (no location specified)
Nov 8, 2023
Transthyretin Amyloidosis Trial in New York (I 124-Evuzamitide)
Recruiting
- Transthyretin Amyloidosis
- I 124-Evuzamitide
-
New York, New YorkColumbia University Irving Medical Center
Nov 23, 2022
Mixed Phenotype Hereditary Transthyretin Amyloidosis
Not yet recruiting
- Hereditary Transthyretin Amyloidosis (ATTRv) Cardiomyopathy (CM), Mixed Phenotype
- (no location specified)
Dec 8, 2022
Cerebral MRI Anomalies in Mutated Transthyretin Amyloidosis
Completed
- Transthyretin Amyloidosis
- No intervention,
-
Nîmes, FranceCHU de Nîmes
Sep 1, 2022
Systemic Transthyretin Amyloidosis: Carpal Tunnel Syndrome
Recruiting
- Transthyretin Amyloidosis
- Carpal Tunnel Syndrome
- Synovial biopsy and Cardiac scintigraphy with [99mTc]Tc-DPD
-
Porto, PortugalCentro Hospitalar Universitário São João
Jan 12, 2023
Transthyretin Amyloid Polyneuropathy (ATTR-PN) Trial in China (tafamidis meglumine)
Active, not recruiting
- Transthyretin Amyloid Polyneuropathy (ATTR-PN)
- tafamidis meglumine
-
Beijing, Beijing, China
- +7 more
Nov 21, 2022
Hereditary Transthyretin Amyloidosis Patients Included in
Completed
- Hereditary Transthyretin Amyloidosis (ATTRv)
- Polyneuropathy
-
Barcelona, Spain
- +2 more
Dec 23, 2022
Transthyretin Amyloidosis, Heart Failure, Heart Failure, Diastolic Trial in Boston (99mTc-pyrophosphate Scintigraphy)
Recruiting
- Transthyretin Amyloidosis
- +3 more
- 99mTc-pyrophosphate Scintigraphy
-
Boston, MassachusettsMassachusetts General Hospital
Oct 11, 2022
Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy Trial in San Francisco (AG10, Placebo)
Withdrawn
- Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy
- AG10
- Placebo
-
San Francisco, CaliforniaEidos Therapeutics
Jun 11, 2021
Hereditary Transthyretin Amyloidosis With Polyneuropthy Trial in Canada, United States (Blood samples for immunoglobulins, Blood
Recruiting
- Hereditary Transthyretin Amyloidosis With Polyneuropthy
- Blood samples for immunoglobulins
- +2 more
-
Rosedale, New York
- +3 more
Dec 19, 2022
Transthyretin Amyloidosis Trial in Beijin (Tafamidis Pill)
Recruiting
- Transthyretin Amyloidosis
- Tafamidis Pill
-
Beijin, ChinaPeking University Third Hospital
Jul 7, 2021
Hereditary Transthyretin-Mediated Amyloid Polyneuropathy Trial in Indianapolis, Boston (Eplontersen)
Recruiting
- Hereditary Transthyretin-Mediated Amyloid Polyneuropathy
-
Indianapolis, Indiana
- +19 more
Jan 31, 2023
Hereditary Amyloidotic Cardiomyopathy: Hereditary Amyloidotic
Not yet recruiting
- Autonomic Nervous System Disease
- Amyloid Neuropathies
- Head-Up Tilt table test
- Heart Rate Variability
-
São Paulo, Sao Paulo, Brazil
- +2 more
Oct 20, 2021
Familial Amyloidotic Polyneuropathy (BioTRAP)
Completed
- Transthyretin Amyloidosis
- +2 more
-
Rostock, Germany
- +1 more
May 4, 2021
Amyloidosis Cardiac, Amyloid Polyneuropathy, Amyloidosis Trial in Edegem (Specific diagnostic work-up for ATTR-CM patients)
Not yet recruiting
- Amyloidosis Cardiac
- +5 more
- Specific diagnostic work-up for ATTR-CM patients
-
Edegem, Antwerp, BelgiumEmeline van Craenenbroek
Jul 29, 2021
Study of Patients With hATTR-PN
Recruiting
- Hereditary Transthyretin Amyloidosis With Polyneuropthy
- Data Collection
-
Anchorage, Alaska
- +22 more
Feb 1, 2023
Transthyretin Amyloidosis in Left Ventricular Hypertrophy of
Completed
- Transthyretin Amyloidosis Cardiomyopathy (ATTR-CM)
- Diagnosis of TTR amyloidosis cardiomyopathy
-
Chermside, Australia
- +17 more
Nov 3, 2022
FAP, Familial Amyloid Polyneuropathy, TTR Trial in Worldwide (IONIS-TTR Rx)
Completed
- FAP
- +4 more
- IONIS-TTR Rx
-
Orange, California
- +21 more
Feb 10, 2021