Autosomal dominant retinitis pigmentosa
Showing 1 - 25 of 1,191
Autosomal Dominant Retinitis Pigmentosa (adRP)
Terminated
- Retinitis Pigmentosa
- Observation
-
Dallas, TexasTexas Retina Associates,
Mar 15, 2021
Rare Disorders, Undiagnosed Disorders, Disorders of Unknown Prevalence Trial in Sioux Falls, Sydney
Recruiting
- Rare Disorders
- +309 more
-
Sioux Falls, South Dakota
- +1 more
Jun 20, 2022
Natural History of PRPF31 Mutation-Associated Retinal Dystrophy
Recruiting
- Retinitis Pigmentosa
- +4 more
-
San Francisco, California
- +4 more
Oct 5, 2022
Retinitis Pigmentosa Trial in Ankara (Wharton's jelly derived mesenchymal stemcells, Magnovision)
Completed
- Retinitis Pigmentosa
- Wharton's jelly derived mesenchymal stemcells
- Magnovision
-
Ankara, Gölbaşı, Turkey
- +2 more
Mar 23, 2023
Retinitis Pigmentosa Trial in Worldwide (N-acetylcysteine, Placebo)
Not yet recruiting
- Retinitis Pigmentosa
- N-acetylcysteine
- Placebo
-
Davis, California
- +30 more
Sep 8, 2022
PDE6A-related Retinitis Pigmentosa in Preparation toGene Therapy
Enrolling by invitation
- Retinitis Pigmentosa
-
Tübingen, Baden-Württemberg, GermanyInstitute for Ophthalmic Research, University Tübingen, Germany
Oct 25, 2022
Inherited Retinal Dystrophies Using Whole Genome Sequencing and
Recruiting
- Inherited Retinal Dystrophy
- +2 more
- whole genome sequencing
-
Rome, ItalyIstituto Superiore di Sanità-Dpt. Oncology and Molecular Medicin
Mar 30, 2023
Retinitis Pigmentosa Trial in Stockholm (CPK850)
Recruiting
- Retinitis Pigmentosa
- CPK850
-
Stockholm, SwedenNovartis Investigative Site
May 16, 2022
Retinitis Pigmentosa Trial in Shanghai (AuTNA I)
Recruiting
- Retinitis Pigmentosa
- AuTNA I
-
Shanghai, Shanghai, ChinaChunhui Jiang
May 2, 2023
Japanese Participants With X-linked Retinitis Pigmentosa
Recruiting
- X-Linked Retinitis Pigmentosa
-
Tokyo, JapanNational Hospital Organization Tokyo Medical Center
Jan 3, 2023
X-Linked Retinitis Pigmentosa Trial in Beijing, Shanghai (FT-002)
Recruiting
- X-Linked Retinitis Pigmentosa
- FT-002
-
Beijing, Beijing, China
- +1 more
May 23, 2023
Retinitis Pigmentosa Trial in Ann Arbor (Hydroxychloroquine lower dose, Hydroxychloroquine higher dose)
Recruiting
- Retinitis Pigmentosa
- Hydroxychloroquine lower dose
- Hydroxychloroquine higher dose
-
Ann Arbor, MichiganUniversity of Michigan
Feb 14, 2022
X-Linked Retinitis Pigmentosa Trial in United States (4D-125 IVT Injection, Observational)
Recruiting
- X-Linked Retinitis Pigmentosa
- 4D-125 IVT Injection
- Observational
-
Aurora, Colorado
- +7 more
Aug 18, 2022
X-Linked Retinitis Pigmentosa
Completed
- X-Linked Retinitis Pigmentosa
- Other: Assessments
-
Phoenix, Arizona
- +21 more
Jan 17, 2023
X-Linked Retinitis Pigmentosa Trial in Meguro-ku (AAV5-hRKp.RPGR)
Not yet recruiting
- X-Linked Retinitis Pigmentosa
- AAV5-hRKp.RPGR
-
Meguro-ku, JapanNational Hospital Organization Tokyo Medical Center
Jun 23, 2023
Retinitis Pigmentosa Trial (2C-QD, Sham 2C-QD)
Not yet recruiting
- Retinitis Pigmentosa
- 2C-QD
- (no location specified)
Apr 24, 2023
Retinitis Pigmentosa Trial (KIO-301)
Recruiting
- Retinitis Pigmentosa
-
Adelaide, South Australia, AustraliaRoyal Adeliade Hospital
Dec 22, 2022
X-Linked Retinitis Pigmentosa Trial in Worldwide (Genetic: AAV5-RPGR 4e11, Genetic: AAV5-RPGR 2e11)
Recruiting
- X-Linked Retinitis Pigmentosa
- Genetic: AAV5-RPGR 4e11
- Genetic: AAV5-RPGR 2e11
-
Los Angeles, California
- +9 more
Aug 16, 2022
Best Disease and Other Retinal Degenerative Diseases.
Active, not recruiting
- Retinal Disease
- +4 more
-
Rochester, MinnesotaMayo Clinic
Jan 4, 2022
Retinitis Pigmentosa Patients
Not yet recruiting
- Retinitis Pigmentosa
- (no location specified)
Apr 28, 2023
CLARIFY: ADH1 and ADH2 Disease Monitoring Study (DMS)
Recruiting
- Autosomal Dominant Hypocalcemia
-
Indianapolis, Indiana
- +14 more
Dec 6, 2022
Patients With X-linked Retinitis Pigmentosa (XLRP)
Completed
- X-Linked Retinitis Pigmentosa
-
Durham, North Carolina
- +2 more
Jan 10, 2023
Autosomal Dominant Optic Atrophy (ADOA), Caused by OPA1 Mutation
Not yet recruiting
- Autosomal Dominant Optic Atrophy
- +3 more
-
Sydney, AustraliaSydney Eye Hospital
Nov 15, 2023
The Polycystic Liver Disease Questionnaire (PLD-Q).
Recruiting
- Polycystic Liver Disease
- PLD-Q
-
Rochester, MinnesotaMayo Clinic
Nov 15, 2022
Assess the Reliability and Validity of the MLYMT
Recruiting
- Retinitis Pigmentosa
- Retinal Dystrophy
- Observational
-
Beverly Hills, California
- +6 more
Apr 18, 2023