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Beta Thalassemia Major

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Bone Denisty Change in Children With Beta Thalassemia Major

Not yet recruiting
  • Evaluate Bone Denisty Changes in Children With Beta Thalassemia Major
  • Dexa scan
  • (no location specified)
Sep 29, 2023

Beta Thalassemia Major Anemia Trial (SP-420)

Not yet recruiting
  • Beta Thalassemia Major Anemia
  • (no location specified)
Jan 20, 2023

Beta-Thalassemia Trial (CS-101 injection)

Not yet recruiting
  • Beta-Thalassemia
  • CS-101 injection
  • (no location specified)
Sep 27, 2023

Thalassemia Major Trial (n-acetylcystine)

Not yet recruiting
  • Thalassemia Major
  • (no location specified)
Mar 9, 2023

Beta Thalassemia Major Anemia Trial (blood sampling)

Not yet recruiting
  • Beta Thalassemia Major Anemia
  • blood sampling
  • (no location specified)
Jul 5, 2021

Beta Thalassemia Major Trial in Tirana (Emeramide)

Completed
  • Beta Thalassemia Major
  • Tirana, Albania
    University Hospital Center "Mother Theresa" Tirana
Aug 20, 2021

Thalassemia, Beta, Thalassemia Major Trial in Tianjin (VGB-Ex01)

Not yet recruiting
  • Thalassemia, Beta
  • Thalassemia Major
  • VGB-Ex01
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
Sep 11, 2023

"Iron Overload and Endocrinological Diseases"

Recruiting
  • Iron Overload
  • +4 more
    • Modena, Italy
      Unit of Endocrinology of Azienza Ospedaliero-Universitaria di Mo
    Nov 13, 2023

    Beta Thalassemia Major, Beta Thalassemia Intermedia Trial in Worldwide (SOTATERCEPT (ACE-011))

    Completed
    • Beta Thalassemia Major
    • Beta Thalassemia Intermedia
    • SOTATERCEPT (ACE-011)
    • Créteil, France
    • +14 more
    Aug 18, 2022

    ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)

    Recruiting
    • β-thalassemia
    • β-globin restored autologous hematopoietic stem cells
    • Shenzhen, Guangdong, China
      Shenzhen Children's Hospital
    Feb 24, 2023

    Alpha Thalassemia Major, Hemoglobinopathy; With Thalassemia, Hemoglobinopathies Trial in San Francisco (in utero hematopoietic

    Enrolling by invitation
    • Alpha Thalassemia Major
    • +8 more
    • in utero hematopoietic stem cell transplantation
    • San Francisco, California
      University of California
    Oct 28, 2022

    Transfusion Dependent Beta Thalassemia, Hemoglobinopathies, Thalassemia Major Trial in Nashville (EDIT-301)

    Recruiting
    • Transfusion Dependent Beta Thalassemia
    • +3 more
    • EDIT-301
    • Oakland, California
    • +3 more
    Jan 3, 2023

    Alpha-Thalassemia, Alpha Thalassemia Major, Alpha Thalassemia Minor Trial in San Francisco

    Recruiting
    • Alpha-Thalassemia
    • +2 more
      • San Francisco, California
        University of California San Francisco
      Oct 7, 2022

      Sickle Cell Anemia, Beta-thalassemia Major, Diamond-blackfan Anemia Trial in Pittsburgh (CD3/CD19 depleted leukocytes, CD45RA

      Recruiting
      • Sickle Cell Anemia
      • +2 more
      • CD3/CD19 depleted leukocytes
      • +6 more
      • Pittsburgh, Pennsylvania
        Children's Hospital of Pittsburgh of UPMC
      May 4, 2022

      ß Thalassemia Major Trial in Shanghai (?-globin reactivated autologous hematopoietic stem cells)

      Active, not recruiting
      • β Thalassemia Major
      • γ-globin reactivated autologous hematopoietic stem cells
      • Shanghai, Shanghai, China
        Shanghai Bioray Laboratories Inc.
      Oct 9, 2022

      QoL of Pediatric Patients After HSCT and Its Influencing Factors

      Not yet recruiting
      • Thalassemia Major
      • Acute Leukemia
      • Conventional nursing
      • Guangzhou, Guangdong, China
        Sun Yat-sen Memorial Hospital, Sun Yat-sen University
      Sep 4, 2023

      Thalassemia Major Trial in Shanghai (?-globin reactivated autologous hematopoietic stem cells)

      Not yet recruiting
      • Thalassemia Major
      • γ-globin reactivated autologous hematopoietic stem cells
      • Shanghai, Shanghai, China
        Shanghai Bioray Laboratories Inc
      Jul 1, 2022

      Sickle Cell Disease, Beta Thalassemia-Major Trial in New Hyde Park (alemtuzumab (Campath IH), Fludarabine, Melphalan)

      Completed
      • Sickle Cell Disease
      • Beta Thalassemia-Major
      • alemtuzumab (Campath IH)
      • +6 more
      • New Hyde Park, New York
        Cohen Children's Medical Center of New York
      Jul 30, 2021

      Thalassemia Major, Transfusion-dependent Anemia Trial in Guangzhou (Luspatercept Injectable Product)

      Recruiting
      • Thalassemia Major
      • Transfusion-dependent Anemia
      • Luspatercept Injectable Product
      • Guangzhou, Guangdong, China
        The second affiliated hospital of Sun Yat-sen University
      Jul 15, 2022

      Sickle Cell Disease, Thalassemia Major Trial in Philadelphia (CliniMACS)

      Recruiting
      • Sickle Cell Disease
      • Thalassemia Major
      • CliniMACS
      • Philadelphia, Pennsylvania
        Children's Hospital of Philadelphia
      Dec 22, 2021

      Pulmonary Hypertension (PAH) in Patients With Thalassemia

      Completed
      • Thalassemia Major
      • +2 more
      • Physician standard-of-care according to ESC/ERS Guidelines
      • Orbassano, Turin, Italy
      • +7 more
      Aug 3, 2022

      Different Risk Factors on Growth Parameters of Thalassemic

      Not yet recruiting
      • Thalassemia Major
      • serum ferritin and AST
      • (no location specified)
      Mar 29, 2022

      Thalassemia Major Trial in Ferrara (Blood component A, Blood component B)

      Completed
      • Thalassemia Major
      • Blood component A
      • Blood component B
      • Ferrara, Italy
        Day Hospital Thalassaemia and Haemoglobinopathies (DHTE)
      Nov 11, 2021

      Leukemia, Myeloid, Acute, Leukemia, B-cell, Leukemia, T Cell Trial in Monza (Sport Therapy)

      Recruiting
      • Leukemia, Myeloid, Acute
      • +7 more
      • Sport Therapy
      • Monza, MB, Italy
        Maria Letizia Verga Center, Pediatric Clinic, University of Mila
      Oct 24, 2022

      Beta Thalassemia Major Anemia, Iron Overload Trial in Cairo, Jakarta (Deferiprone oral solution, Placebo)

      Completed
      • Beta Thalassemia Major Anemia
      • Iron Overload
      • Deferiprone oral solution
      • Placebo
      • Cairo, Egypt
      • +3 more
      Feb 9, 2021