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Beta-Thalassaemia

Showing 1 - 25 of 3,059

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Transfusion Dependent Beta-Thalassaemia Trial in Nanning (ET-01)

Recruiting
  • Transfusion Dependent Beta-Thalassaemia
  • ET-01
  • Nanning, Guangxi, China
    PLA 923 Hospital
Mar 2, 2023

Beta Thalassaemia Trial in Milan (Safety and Efficacy assessments)

Active, not recruiting
  • Beta Thalassaemia
  • Safety and Efficacy assessments
  • Milan, Italy
    Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR
Nov 22, 2022

Transfusion Dependent Beta-Thalassaemia Trial in Guangzhou, Shenzhen, Tianjin (ET-01)

Active, not recruiting
  • Transfusion Dependent Beta-Thalassaemia
  • ET-01
  • Guangzhou, Guangdong, China
  • +3 more
May 9, 2022

Transfusion Dependent Beta-Thalassaemia Trial in Tianjin (ET-01)

Active, not recruiting
  • Transfusion Dependent Beta-Thalassaemia
  • ET-01
  • Tianjin, Tianjin, China
    Institute of Hematology & Blood Diseases Hospital
Dec 9, 2021

Beta-Thalassemia Trial in Bulgaria, Israel, United States (VIT-2763 60 mg QD, VIT-2763 60 mg BID, VIT-2763 120 mg BID)

Withdrawn
  • Beta-Thalassemia
  • VIT-2763 60 mg QD
  • +3 more
  • Whittier, California
  • +6 more
Nov 7, 2022

Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome, Very-Low Risk Myelodysplastic Syndrome Trial in

Recruiting
  • Non-transfusion-dependent Thalassemia
  • +2 more
  • Düsseldorf, Germany
  • +19 more
Mar 18, 2022

Thalassemia Major Trial in Ferrara (Blood component A, Blood component B)

Completed
  • Thalassemia Major
  • Blood component A
  • Blood component B
  • Ferrara, Italy
    Day Hospital Thalassaemia and Haemoglobinopathies (DHTE)
Nov 11, 2021

Beta-Thalassemia Trial in Ferrara, Firenze, Pisa (Sirolimus 0.5 mg)

Recruiting
  • Beta-Thalassemia
  • Sirolimus 0.5 mg
  • Ferrara, FE, Italy
  • +3 more
Nov 11, 2021

Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome Trial in Bulgaria, United Kingdom (SLN124 is a GalNAc

Withdrawn
  • Non-transfusion-dependent Thalassemia
  • Low Risk Myelodysplastic Syndrome
  • SLN124 is a GalNAc conjugated double stranded fully modified siRNA. Sodium chloride 0.9% w/v is used as Placebo
  • Kyustendil, Bulgaria
  • +4 more
Apr 23, 2020

Transfusion-dependent Beta-Thalassemia Trial in Tianjin (KL003 cell injection Drug Product)

Not yet recruiting
  • Transfusion-dependent Beta-Thalassemia
  • KL003 cell injection Drug Product
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
May 8, 2023

Transfusion-dependent Thalassemia Trial in Dhaka (Thalidomide Capsules, Placebo)

Recruiting
  • Transfusion-dependent Thalassemia
  • Thalidomide Capsules
  • Placebo
  • Dhaka, Bangladesh
    Bangabandhu Sheikh Mujib Medical University
Oct 18, 2023

Beta Thalassemia Major, Beta Thalassemia Intermedia Trial in Worldwide (SOTATERCEPT (ACE-011))

Completed
  • Beta Thalassemia Major
  • Beta Thalassemia Intermedia
  • SOTATERCEPT (ACE-011)
  • Créteil, France
  • +14 more
Aug 18, 2022

Sickle Cell Disease, Sickle Cell Trait, Beta-Thalassemia Trial (High performance liquid chromatography, Automated sickling test,

Not yet recruiting
  • Sickle Cell Disease
  • +4 more
  • High performance liquid chromatography
  • +5 more
  • (no location specified)
Aug 17, 2022

Atrial Fibrillation in Beta-Thalassemia

Not yet recruiting
  • Atrial Fibrillation
  • Thalassemia
    • Ferrara, Italy
      Matteo Bertini
    Aug 18, 2022

    Transfusion-dependent Beta-Thalassemia Trial in Peshawar (Thalidomide)

    Completed
    • Transfusion-dependent Beta-Thalassemia
    • Peshawar, Khyber Pakhtunkhwa, Pakistan
      Blood Care Clinic
    Nov 19, 2023

    Thalassemia Major, Transfusion-dependent Anemia Trial in Guangzhou (Luspatercept Injectable Product)

    Recruiting
    • Thalassemia Major
    • Transfusion-dependent Anemia
    • Luspatercept Injectable Product
    • Guangzhou, Guangdong, China
      The second affiliated hospital of Sun Yat-sen University
    Jul 15, 2022

    Thalassemia Trial in Peshawar (Thalidomide and Hydroxyurea)

    Completed
    • Thalassemia
    • Thalidomide and Hydroxyurea
    • Peshawar, Khyber Pakhtukhwa, Pakistan
      Blood Diseases Clinic
    Mar 10, 2022

    Transfusion-dependent ß-thalassemia Patients, Cardiac Iron Overload Trial in Athens, Patras (Deferasirox, Deferoxamine (DFO))

    Terminated
    • Transfusion-dependent β-thalassemia Patients
    • Cardiac Iron Overload
    • Athens, GR, Greece
    • +3 more
    Oct 21, 2019

    Nutritional Status in Thalassemia Major Assiut Children Hospital

    Completed
    • Thalassemia Major
      • Assiut, Egypt
        Asmaa Refaat Abdelmonem
      Jul 28, 2020

      ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)

      Recruiting
      • β-thalassemia
      • β-globin restored autologous hematopoietic stem cells
      • Shenzhen, Guangdong, China
        Shenzhen Children's Hospital
      Feb 24, 2023

      ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)

      Recruiting
      • β-thalassemia
      • β-globin restored autologous hematopoietic stem cells
      • Shenzhen, Guangdong, China
        Shenzhen University General Hospital
      May 8, 2023

      Insulin Secretion Trial in Vellore (Ferrous sulphate)

      Completed
      • Insulin Secretion
      • Ferrous sulphate
      • Vellore, Tamil Nadu, India
        Christian Medical College
      Feb 11, 2022

      Difficult Intubation Trial (fiberoptic intubation classic technique, fiberoptic intubation tube 1st technique)

      Not yet recruiting
      • Difficult Intubation
      • fiberoptic intubation classic technique
      • fiberoptic intubation tube 1st technique
      • (no location specified)
      May 28, 2022

      The Prevelence of HBB c.93-21 G-A in ß Thalassemia Patients

      Recruiting
      • Beta-Thalassemia
      • ARMS PCR
      • Assiut, Egypt
        Faculty of Medicine Assiut University
      Jan 30, 2023

      Beta Thalassemia Intermedia Trial in Worldwide (IONIS TMPRSS6-LRx)

      Active, not recruiting
      • Beta Thalassemia Intermedia
      • Camperdown, New South Wales, Australia
      • +18 more
      Sep 23, 2022