CLN
Showing 1 - 25 of 334
Advanced Solid Tumor Trial in United States (CLN-617, Pembrolizumab)
Not yet recruiting
- Advanced Solid Tumor
-
Los Angeles, California
- +5 more
Sep 12, 2023
Neuronal Ceroid Lipofuscinosis, Batten's CLN6 Diseae
Recruiting
- Batten Disease
- CLN6
- Natural history
-
Columbus, OhioNationwide Children's Hospital
Oct 20, 2022
Neuronal Ceroid Lipofuscinosis CLN5 Trial in Rochester (NGN-101)
Recruiting
- Neuronal Ceroid Lipofuscinosis CLN5
- NGN-101
-
Rochester, New York
- +1 more
Jan 19, 2023
Investigations of Juvenile Neuronal Ceroid Lipofuscinosis
Recruiting
- Juvenile Neuronal Ceroid Lipofuscinosis (CLN3)
- Batten Disease
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 31, 2023
CLN7 Trial in Dallas (AAV9/CLN7)
Recruiting
- CLN7
- AAV9/CLN7
-
Dallas, TexasChildren' Health
May 16, 2022
CLN3, Batten Disease Trial in Columbus (AT-GTX-502)
Active, not recruiting
- CLN3
- Batten Disease
- AT-GTX-502
-
Columbus, OhioNationwide Children's Hospital
Jul 18, 2022
Neuronal Ceroid Lipofuscinosis Type 2 Trial in London (RGX-381)
Not yet recruiting
- Neuronal Ceroid Lipofuscinosis Type 2
- RGX-381
-
London, United KingdomGreater Ormond Street Hospital
Mar 17, 2023
Jansky-Bielschowsky Disease, Batten Disease, Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 Trial in Worldwide (BMN 190,
Completed
- Jansky-Bielschowsky Disease
- +4 more
- BMN 190
- Intracerebroventricular (ICV) access device
-
Columbus, Ohio
- +3 more
Jul 28, 2022
Late Infantile Variant CLN5 And CLN7 Disease
Recruiting
- Ceroid Lipofuscinosis, Neuronal 5
- Ceroid Lipofuscinosis, Neuronal 7
-
Rochester, New YorkUniversity of Rochester Medical Center
Mar 1, 2022
Neuronal Ceroid Lipofuscinosis, Batten Disease, CLN1 Disease Trial in Hamburg (Natural History)
Recruiting
- Neuronal Ceroid Lipofuscinosis
- +14 more
- Natural History
-
Hamburg, GermanyUniversity Medical Center Hamburg-Eppendorf
Oct 22, 2021
Non Small Cell Lung Cancer, EGFR Exon 20 Mutation Trial in Worldwide (CLN-081)
Recruiting
- Non Small Cell Lung Cancer
- EGFR Exon 20 Mutation
-
Duarte, California
- +18 more
Nov 11, 2022
Natural History Study of Batten Disease
Terminated
- Batten Disease
- +2 more
-
Rochester, New YorkUniversity of Rochester Medical Center
Apr 1, 2022
Juvenile Neuronal Ceroid Lipofuscinosis Trial (PLX-200, Placebo)
Not yet recruiting
- Juvenile Neuronal Ceroid Lipofuscinosis
- PLX-200
- Placebo
- (no location specified)
Mar 31, 2022
Batten Disease Trial in Houston (Miglustat 100Mg Oral Capsule)
Recruiting
- Batten Disease
- Miglustat 100Mg Oral Capsule
-
Houston, TexasTexas Children Hospital
May 17, 2022
CLN6 Batten Disease Subjects Following Gene Transfer
Active, not recruiting
- CLN6
- Batten Disease
- AT-GTX-501
-
Columbus, OhioNationwide Children's Hosptial
Dec 17, 2021
A Retrospective, Natural History Study in Children With CLN2
Withdrawn
- Late-infantile Neuronal Ceroid Lipofuscinosis Type 2 (CLN2)
- (no location specified)
Oct 25, 2021
Children Diagnosed With CLN2 Disease
Recruiting
- Batten Disease
- +2 more
- CLN2 Treatment
-
Columbus, OhioNationwide Children's Hospital
Aug 2, 2021
Variant Late-Infantile Neuronal Ceroid Lipofuscinosis Trial in Columbus (AT-GTX-501)
Completed
- Variant Late-Infantile Neuronal Ceroid Lipofuscinosis
- AT-GTX-501
-
Columbus, OhioNationwide Children's Hosptial
Jan 21, 2022
Neuronal Ceroid Lipofuscinosis Type 2 Trial in Columbus (Cerliponase Alfa)
Enrolling by invitation
- Neuronal Ceroid Lipofuscinosis Type 2
- Cerliponase Alfa
-
Columbus, OhioNationwide Children's Hospital
Nov 29, 2021
Investigate Frequency of Neuronal Ceroid Lipofuxinosis Type 2
Recruiting
- Neuronal Ceroid Lipofuxinosis Type2 (CLN2)
- Blood Sampling
-
Adana, Turkey
- +33 more
Nov 7, 2023
Atypical Tripeptidyl Peptidase 1 Enzyme Deficiency Patients
Active, not recruiting
- Neuronal Ceroid-Lipofuscinoses
- +2 more
-
Orange, CaliforniaChildren's Hospital of Orange County
Jul 18, 2022
Acute Myeloid Leukemia, Acute Myeloid Leukemia Recurrent, Leukemia Trial in Boston (Cytokine-Induced Memory-like Natural Killer
Not yet recruiting
- Acute Myeloid Leukemia
- +3 more
- Cytokine-Induced Memory-like Natural Killer Cells
- +2 more
-
Boston, Massachusetts
- +1 more
Nov 22, 2023