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CLN

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STUDY
CONDITIONS
INTERVENTIONS
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Advanced Solid Tumor Trial in United States (CLN-617, Pembrolizumab)

Not yet recruiting
  • Advanced Solid Tumor
  • Los Angeles, California
  • +5 more
Sep 12, 2023

NHL, NHL, Relapsed, Adult Trial in United States (CLN-978)

Recruiting
  • NHL
  • NHL, Relapsed, Adult
  • Birmingham, Alabama
  • +4 more
May 31, 2023

Neuronal Ceroid Lipofuscinosis, Batten's CLN6 Diseae

Recruiting
  • Batten Disease
  • CLN6
  • Natural history
  • Columbus, Ohio
    Nationwide Children's Hospital
Oct 20, 2022

Neuronal Ceroid Lipofuscinosis CLN5 Trial in Rochester (NGN-101)

Recruiting
  • Neuronal Ceroid Lipofuscinosis CLN5
  • NGN-101
  • Rochester, New York
  • +1 more
Jan 19, 2023

Investigations of Juvenile Neuronal Ceroid Lipofuscinosis

Recruiting
  • Juvenile Neuronal Ceroid Lipofuscinosis (CLN3)
  • Batten Disease
    • Bethesda, Maryland
      National Institutes of Health Clinical Center
    Jan 31, 2023

    CLN7 Trial in Dallas (AAV9/CLN7)

    Recruiting
    • CLN7
    • AAV9/CLN7
    • Dallas, Texas
      Children' Health
    May 16, 2022

    Advanced Solid Tumor Trial in Australia, United States (CLN-619, Pembrolizumab)

    Recruiting
    • Advanced Solid Tumor
    • Duarte, California
    • +15 more
    Nov 30, 2022

    CLN3, Batten Disease Trial in Columbus (AT-GTX-502)

    Active, not recruiting
    • CLN3
    • Batten Disease
    • AT-GTX-502
    • Columbus, Ohio
      Nationwide Children's Hospital
    Jul 18, 2022

    Neuronal Ceroid Lipofuscinosis Type 2 Trial in London (RGX-381)

    Not yet recruiting
    • Neuronal Ceroid Lipofuscinosis Type 2
    • RGX-381
    • London, United Kingdom
      Greater Ormond Street Hospital
    Mar 17, 2023

    Jansky-Bielschowsky Disease, Batten Disease, Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 Trial in Worldwide (BMN 190,

    Completed
    • Jansky-Bielschowsky Disease
    • +4 more
    • BMN 190
    • Intracerebroventricular (ICV) access device
    • Columbus, Ohio
    • +3 more
    Jul 28, 2022

    Late Infantile Variant CLN5 And CLN7 Disease

    Recruiting
    • Ceroid Lipofuscinosis, Neuronal 5
    • Ceroid Lipofuscinosis, Neuronal 7
      • Rochester, New York
        University of Rochester Medical Center
      Mar 1, 2022

      Neuronal Ceroid Lipofuscinosis, Batten Disease, CLN1 Disease Trial in Hamburg (Natural History)

      Recruiting
      • Neuronal Ceroid Lipofuscinosis
      • +14 more
      • Natural History
      • Hamburg, Germany
        University Medical Center Hamburg-Eppendorf
      Oct 22, 2021

      Non Small Cell Lung Cancer, EGFR Exon 20 Mutation Trial in Worldwide (CLN-081)

      Recruiting
      • Non Small Cell Lung Cancer
      • EGFR Exon 20 Mutation
      • Duarte, California
      • +18 more
      Nov 11, 2022

      Natural History Study of Batten Disease

      Terminated
      • Batten Disease
      • +2 more
        • Rochester, New York
          University of Rochester Medical Center
        Apr 1, 2022

        Relapsed/Refractory AML Trial in United States (CLN-049)

        Recruiting
        • Relapsed/Refractory AML
        • Tampa, Florida
        • +3 more
        Dec 2, 2021

        Juvenile Neuronal Ceroid Lipofuscinosis Trial (PLX-200, Placebo)

        Not yet recruiting
        • Juvenile Neuronal Ceroid Lipofuscinosis
        • (no location specified)
        Mar 31, 2022

        Batten Disease Trial in Houston (Miglustat 100Mg Oral Capsule)

        Recruiting
        • Batten Disease
        • Miglustat 100Mg Oral Capsule
        • Houston, Texas
          Texas Children Hospital
        May 17, 2022

        CLN6 Batten Disease Subjects Following Gene Transfer

        Active, not recruiting
        • CLN6
        • Batten Disease
        • AT-GTX-501
        • Columbus, Ohio
          Nationwide Children's Hosptial
        Dec 17, 2021

        A Retrospective, Natural History Study in Children With CLN2

        Withdrawn
        • Late-infantile Neuronal Ceroid Lipofuscinosis Type 2 (CLN2)
          • (no location specified)
          Oct 25, 2021

          Children Diagnosed With CLN2 Disease

          Recruiting
          • Batten Disease
          • +2 more
          • CLN2 Treatment
          • Columbus, Ohio
            Nationwide Children's Hospital
          Aug 2, 2021

          Variant Late-Infantile Neuronal Ceroid Lipofuscinosis Trial in Columbus (AT-GTX-501)

          Completed
          • Variant Late-Infantile Neuronal Ceroid Lipofuscinosis
          • AT-GTX-501
          • Columbus, Ohio
            Nationwide Children's Hosptial
          Jan 21, 2022

          Neuronal Ceroid Lipofuscinosis Type 2 Trial in Columbus (Cerliponase Alfa)

          Enrolling by invitation
          • Neuronal Ceroid Lipofuscinosis Type 2
          • Cerliponase Alfa
          • Columbus, Ohio
            Nationwide Children's Hospital
          Nov 29, 2021

          Investigate Frequency of Neuronal Ceroid Lipofuxinosis Type 2

          Recruiting
          • Neuronal Ceroid Lipofuxinosis Type2 (CLN2)
          • Blood Sampling
          • Adana, Turkey
          • +33 more
          Nov 7, 2023

          Atypical Tripeptidyl Peptidase 1 Enzyme Deficiency Patients

          Active, not recruiting
          • Neuronal Ceroid-Lipofuscinoses
          • +2 more
            • Orange, California
              Children's Hospital of Orange County
            Jul 18, 2022

            Acute Myeloid Leukemia, Acute Myeloid Leukemia Recurrent, Leukemia Trial in Boston (Cytokine-Induced Memory-like Natural Killer

            Not yet recruiting
            • Acute Myeloid Leukemia
            • +3 more
            • Cytokine-Induced Memory-like Natural Killer Cells
            • +2 more
            • Boston, Massachusetts
            • +1 more
            Nov 22, 2023