DOCK8 Deficiency
Showing 26 - 50 of 8,470
Malnutrition, Child, Malnutrition Trial in Pittsburgh (SMOFlipid® (lipid injectable emulsion))
Not yet recruiting
- Malnutrition, Child
- Malnutrition
- SMOFlipid® (lipid injectable emulsion)
-
Pittsburgh, PennsylvaniaChildren's Hospital of Pittsburgh of UPMC
Sep 19, 2023
Advanced Colorectal Carcinoma, Advanced Lung Non-Small Cell Carcinoma, Lung Non-Small Cell Carcinoma Trial in Houston
Active, not recruiting
- Advanced Colorectal Carcinoma
- +24 more
- Danvatirsen
- Durvalumab
-
Houston, TexasM D Anderson Cancer Center
Oct 20, 2022
Heart Failure, Heart Failure With Reduced Ejection Fraction, Thiamine Deficiency Trial in Hamilton (Thiamine, Placebo)
Completed
- Heart Failure
- +3 more
- Thiamine
- Placebo
-
Hamilton, Ontario, CanadaMcMaster University
Aug 30, 2021
Asthma, COPD, Bronchiectasis Trial in Hamilton (Hyperpolarized 129Xe MRI)
Recruiting
- Asthma
- +7 more
- Hyperpolarized 129Xe MRI
-
Hamilton, Ontario, CanadaFirestone Institute for Respiratory Health, St. Joseph's Healthc
Sep 7, 2022
Pyruvate Kinase Deficiency, Anemia, Hemolytic Trial in Canada, Japan (Mitapivat)
Not yet recruiting
- Pyruvate Kinase Deficiency
- Anemia, Hemolytic
-
Hamilton, Ontario, Canada
- +3 more
Mar 9, 2023
Participation in a Research Registry for Immune Disorders
Recruiting
- Primary Immunodeficiencies
- +4 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center, 9000 Rockville Pi
Apr 7, 2022
Immunologic Deficiency Syndromes Trial in Canada, United States (GC5107)
Completed
- Immunologic Deficiency Syndromes
- GC5107
-
Centennial, Colorado
- +19 more
Nov 11, 2022
Preterm, Nutritional Deficiency, Immune System and Related Disorders Trial in Liverpool (Arginine)
Recruiting
- Preterm
- +2 more
- Arginine
-
Liverpool, Merseyside, United KingdomLiverpool Women's Hospital
Mar 17, 2022
Health, Subjective, Nutrition Disorders, Athletic Injuries Trial in Victoria (Treatment of REDS using a holistic treatment arm)
Recruiting
- Health, Subjective
- +11 more
- Treatment of REDS using a holistic treatment arm
-
Victoria, British Columbia, CanadaUniversity of Victoria
Jun 1, 2021
Pyruvate Kinase Deficiency, Anemia, Hemolytic Trial in Worldwide (Placebo, AG-348)
Completed
- Pyruvate Kinase Deficiency
- Anemia, Hemolytic
- Placebo
- AG-348
-
Little Rock, Arkansas
- +45 more
May 20, 2022
Fabry Disease, Alpha Galactosidase A Deficiency Trial in Austria, United Kingdom, United States (agalsidase beta)
Recruiting
- Fabry Disease
- Alpha Galactosidase A Deficiency
- agalsidase beta
-
Decatur, Georgia
- +4 more
May 4, 2022
Anemia of Chronic Kidney Disease Trial in Taiwan (Ferric citrate, Placebo)
Recruiting
- Anemia of Chronic Kidney Disease
- Ferric citrate
- Placebo
-
Kaohsiung, Taiwan
- +7 more
Mar 6, 2022
Biomarker for Mannosidosis Disease (BioMannosidosis)
Active, not recruiting
- Alpha-Mannosidase B Deficiency
- +2 more
-
Rostock, Germany
- +2 more
May 12, 2021
Pulmonary Emphysema in Alpha-1 PI Deficiency Trial in Worldwide (Alpha-1 MP, 0.9% Sodium Chloride for Injection, USP)
Recruiting
- Pulmonary Emphysema in Alpha-1 PI Deficiency
- Alpha-1 MP
- 0.9% Sodium Chloride for Injection, USP
-
Phoenix, Arizona
- +50 more
Dec 7, 2022
Monocarboxylate Transporter 8 Deficiency Trial in Rehovot (Glycerol Phenylbutyrate 1100 MG/ML)
Recruiting
- Monocarboxylate Transporter 8 Deficiency
- Glycerol Phenylbutyrate 1100 MG/ML
-
Rehovot, IsraelPediatric Endocrinology Unit, Kapan Medical Center
Aug 22, 2021
Hypocalcemia, Vitamin D Deficiency, Postoperative Complications Trial in Lódz (drug, diagnostic test, procedure, other)
Recruiting
- Hypocalcemia
- +6 more
- Dexamethasone oral tablet 8mg (Dexamethasone Krka tablets(8mg), Warsaw, Poland).
- +14 more
-
Łódź, Łódzkie, PolandDepartment of General and Oncological Surgery, Medical Universit
Feb 5, 2022
Anemia, Iron Deficiency, Anemia of Chronic Disease, Hip Arthropathy Trial in Toronto (Iron sucrose, Epoetin Alfa, Placebo)
Terminated
- Anemia, Iron Deficiency
- +3 more
- Iron sucrose
- +2 more
-
Toronto, Ontario, CanadaSt. Michael's Hosptial
Jun 14, 2021
Biomarker for Wolman Disease (BioWolman)
Active, not recruiting
- Acid Lipase Deficiency
- +2 more
-
Rostock, Germany
- +2 more
May 12, 2021
Skin Microbes in Healthy People and in People With Skin
Recruiting
- Atopic Dermatitis
- +2 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Feb 2, 2023
Refractory or Recurrent Hypermutated Malignancies, Biallelic Mismatch Repair Deficiency (bMMRD) Positive Patients Trial in
Active, not recruiting
- Refractory or Recurrent Hypermutated Malignancies
- Biallelic Mismatch Repair Deficiency (bMMRD) Positive Patients
-
Boston, Massachusetts
- +9 more
May 17, 2022
Pro-opiomelanocortin (POMC) Deficiency Obesity Trial in Worldwide (Setmelanotide, Placebo)
Completed
- Pro-opiomelanocortin (POMC) Deficiency Obesity
- Setmelanotide
- Placebo
-
Scottsdale, Arizona
- +6 more
Jan 26, 2021
Monitoring in Tyrosinemia Type 1 (BioTyrosin)
Active, not recruiting
- Tyrosinosis
- +4 more
-
Rostock, Germany
- +2 more
May 17, 2021