Diamond Blackfan Anemia (DBA)
Showing 1 - 25 of 2,238
Steroid-refractory Diamond-Blackfan Anemia (DBA) Trial run by the National Heart, Lung, and Blood Institute (NHLBI) (Bitopertin)
Not yet recruiting
- Steroid-refractory Diamond-Blackfan Anemia (DBA)
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Bethesda, MarylandNational Institutes of Health Clinical Center
Apr 28, 2023
Diamond Blackfan Anemia, Pure Red Cell Aplasia Trial in Boston, Manhasset (Trifluoperazine)
Terminated
- Diamond Blackfan Anemia
- Pure Red Cell Aplasia
-
Boston, Massachusetts
- +1 more
Nov 18, 2022
Cancer in Inherited Bone Marrow Failure Syndromes
Recruiting
- Diamond Blackfan Anemia
- +4 more
-
Bethesda, Maryland
- +1 more
Jan 24, 2023
Diamond Blackfan Anemia Trial in Manhasset (Sotatercept, Sotatercept with prednisone boost)
Terminated
- Diamond Blackfan Anemia
- Sotatercept
- Sotatercept with prednisone boost
-
Manhasset, New YorkNorth Shore- LIJ campus of The Feinstein Institute for Medical R
Nov 22, 2021
Aplastic Anemia, Pure Red Cell Aplasia, Diamond Blackfan Anemia Trial run by the NHLBI (Daclizumab)
Terminated
- Aplastic Anemia
- +2 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center, 9000 Rockville Pi
Jun 15, 2021
Sickle Cell Anemia, Beta-thalassemia Major, Diamond-blackfan Anemia Trial in Pittsburgh (CD3/CD19 depleted leukocytes, CD45RA
Recruiting
- Sickle Cell Anemia
- +2 more
- CD3/CD19 depleted leukocytes
- +6 more
-
Pittsburgh, PennsylvaniaChildren's Hospital of Pittsburgh of UPMC
May 4, 2022
Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Adrenoleukodystrophy Trial in Denver, Valhalla, Salt Lake City (Human
Completed
- Mucopolysaccharidosis I
- +15 more
- Human Placental Derived Stem Cell
-
Denver, Colorado
- +2 more
Oct 24, 2022
Multi-Center Study of Iron Overload: Survey Study (MCSIO)
Completed
- Sickle Cell Disease
- +2 more
-
Oakland, California
- +7 more
Sep 22, 2020
Multi-Center Study of Iron Overload: Pilot Study
Completed
- Sickle Cell Disease
- +2 more
-
Oakland, California
- +2 more
Sep 22, 2020
Familial Investigations of Childhood Cancer Predisposition
Recruiting
- Acute Leukemia
- +45 more
-
Memphis, TennesseeSt. Jude Children's Research Hospital
May 11, 2022
Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive, Acute Leukemia in Remission, Acute Lymphoblastic Leukemia
Active, not recruiting
- Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive
- +36 more
- Cyclophosphamide
- +4 more
-
Buffalo, New YorkRoswell Park Cancer Institute
Jan 23, 2023
Bone Marrow Failure Syndrome, Thalassemia, Sickle Cell Disease Trial in Gainesville (Thiotepa--single daily dose,
Recruiting
- Bone Marrow Failure Syndrome
- +15 more
- Thiotepa--single daily dose
- Thiotepa--escalated dose
-
Gainesville, FloridaUF Health Shands Children's Hospital
Jul 8, 2021
Baby Detect : Genomic Newborn Screening
Recruiting
- Congenital Adrenal Hyperplasia
- +126 more
-
Liege, Wallonia, BelgiumCRMN, Hôpital La Citadelle
Jan 24, 2023
Bone Marrow Failure Syndrome, Congenital Amegakaryocytic Thrombocytopenia, Congenital Pure Red Cell Aplasia Trial in United
Recruiting
- Bone Marrow Failure Syndrome
- +6 more
- Treosulfan
- +7 more
-
Los Angeles, California
- +23 more
Aug 15, 2022
Congenital Hemolytic Anemia, Sickle Cell Disease Trial run by the National Heart, Lung, and Blood Institute (NHLBI) (Peripheral
Recruiting
- Congenital Hemolytic Anemia
- Sickle Cell Disease
- Peripheral blood hematopoietic progenitor cell (PBPC) transplant
- +3 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 25, 2023
Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
Recruiting
- Primary Immunodeficiency (PID)
- +4 more
- data collection
-
Pittsburgh, PennsylvaniaUPMC Children's Hospital of Pittsburgh
Feb 9, 2022
Bone Marrow Failure Syndrome, Severe Aplastic Anemia, Severe Congenital Neutropenia Trial in New York (CD34 Stem Cell Selection
Active, not recruiting
- Bone Marrow Failure Syndrome
- +15 more
- CD34 Stem Cell Selection Therapy
-
New York, New YorkMorgan Stanley Children's Hospital, New York-Presbyterian, Colum
Jun 17, 2020
Hurler Syndrome, Fanconi Anemia, Glanzmann Thrombasthenia Trial in Atlanta (Abatacept)
Completed
- Hurler Syndrome
- +14 more
-
Atlanta, GeorgiaChildren's Healthcare of Atlanta
Dec 20, 2019
Sickle Cell Disease, Thalassemia, Diamond-Blackfan Anemia Trial in Birmingham, Minneapolis (Bone marrow transplantation,
Completed
- Sickle Cell Disease
- +2 more
- Bone marrow transplantation
- Mesenchymal Stromal Cells
-
Birmingham, Alabama
- +1 more
Jul 9, 2018
Bone Marrow Failure Syndromes Trial in Philadelphia (MRD-BMT with Fludarabine-based RIC for Acquired AA, MRD-BMT with
Recruiting
- Bone Marrow Failure Syndromes
- MRD-BMT with Fludarabine-based RIC for Acquired AA
- +2 more
-
Philadelphia, PennsylvaniaChildren's Hospital of Philadelphia
May 6, 2022
Hemoglobinopathies and Rare Inherited Anemia and Covid 19
Recruiting
- Haemoglobinopathies
-
Genova, Italy
- +1 more
May 4, 2022
Anemia, Aplastic, Red-Cell Aplasia, Pure, Anemia, Diamond-Blackfan Trial run by the NHLBI (Rituximab)
Completed
- Anemia, Aplastic
- +2 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center, 9000 Rockville Pi
Aug 20, 2018
Hearing Screener Trial in Wake Forest
Recruiting
- Hearing Screener
-
Wake Forest, North CarolinaCrossover Mangement
Apr 28, 2023
DIAMOND AF Post-Approval Study
Recruiting
- Paroxysmal Atrial Fibrillation
- DiamondTemp™ Ablation System
-
Winter Park, Florida
- +1 more
Jan 19, 2023